CClinicalTrials.gg
RecruitingNCT05076175Updated Sep 24, 2026

A Study Investigating Oral Ozanimod (RPC1063) in Pediatric Participants With Moderate to Severe Active Ulcerative Colitis

A Phase 2/3 interventional study of Ozanimod in Colitis, Ulcerative, sponsored by Bristol-Myers Squibb. Recruiting at 91 sites in 13 countries. Open to participants aged 2 Years to 17 Years. Per ClinicalTrials.gov, last updated 2026-09-24.

Sponsored by Bristol-Myers Squibb · Phase 2/3, Interventional, and Treatment

Phase
Phase 2/3
Study type
Interventional
Enrollment
120
Allocation
Randomized
Ages
2 Years to 17 Years
Sex
All
01

Study summary

The purpose of this study is to evaluate the effectiveness and safety of ozanimod (RPC1063) in achieving and maintaining clinical remission. Ozanimod will be administered orally to pediatric participants with moderate to severe active ulcerative colitis (UC) who have had an inadequate response to conventional therapy.

02

Conditions studied

  • Colitis, Ulcerative

Browse trials for

Keywords

  • Ulcerative Colitis
  • Ozanimod
  • Pediatric
03

Who can participate

Ages eligible
2 Years to 17 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Moderately to severely active Ulcerative Colitis (UC) diagnosed prior to the Screening Visit
  • Evidence of UC extending beyond the rectum, as determined by baseline endoscopy
  • Has had an inadequate response, loss of response to, or is intolerant to at least 1 of the following treatments for UC: oral aminosalicylates, systemic corticosteroids, immunomodulators, biologic therapy

Exclusion criteria

Exclusion Criteria

  • Diagnosis of Crohn's disease or indeterminate colitis
  • Has documentation of positive test for toxin producing Clostridium difficile, or polymerase chain reaction examination of the stool
  • Apheresis within 2 weeks of randomization
  • History of or currently active primary or secondary immunodeficiency, or participants with known genetic disorders as a cause for colitis
  • Other protocol-defined inclusion/exclusion criteria apply
04

Study design

Phase
Phase 2 / Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
120 participants (estimated)

Study arms

  • Experimental
    Ozanimod High Dose

    Drug: Ozanimod

  • Experimental
    Ozanimod Low Dose

    Drug: Ozanimod

Interventions

  • DrugOzanimod

    Specified dose on specified days

    Also known as: RPC1063

05

What researchers measure

Primary outcomes

  1. Proportion of participants who achieve clinical remission

    Time frame: At Week 52

Secondary outcomes

  1. Proportion of participants who achieve clinical remission

    Time frame: At Week 10

  2. Proportion of participants who achieve clinical response

    Time frame: At Week 52

  3. Proportion of participants who achieve clinical response

    Time frame: At Week 10

  4. Proportion of participants who achieve symptomatic remission

    Time frame: At Week 10 and Week 52

  5. Time to achievement of symptomatic remission

    Time frame: Up to 6 years

  6. Proportion of participants who achieve endoscopic improvement

    Time frame: At Week 10 and Week 52

  7. Proportion of participants who achieve corticosteroid free remission

    Time frame: At Week 52

  8. Incidence of Adverse Events (AEs)

    Time frame: Up to 6 years

  9. Incidence of Serious Adverse Events

    Time frame: Up to 6 years

  10. Incidence of AEs leading to discontinuation from treatment

    Time frame: Up to 6 years

  11. Incidence of AEs of special interest (AESIs)

    Time frame: Up to 6 years

  12. Steady state systemic exposure of ozanimod and CC112273

    Time frame: At Week 18 and throughout the study, up to 70 weeks

  13. Absolute change from baseline in Absolute Lymphocyte Count (ALC)

    Time frame: Up to 6 years

  14. Percent change from baseline in ALC

    Time frame: Up to 6 years

06

Study locations

40 of 91 sites recruiting
  • Local Institution - 0041
    Phoenix, Arizona 85016-7710, United States
    Withdrawn
  • University of Arizona
    Tucson, Arizona 85724, United States
    Withdrawn
  • Local Institution - 0052
    Garden Grove, California 92845, United States
    Completed
  • Loma Linda University Health System
    Loma Linda, California 92354, United States
    • Kalyan Ray Parashette, Site 0087 · Contact · 505-274-0704
    Recruiting
  • Cedars-Sinai Medical Center
    Los Angeles, California 90048, United States
    • Shervin Rabizadeh, Site 0074 · Contact · 310-423-7100
    Recruiting
  • Lucile Packard Children's Hospital
    Palo Alto, California 94304, United States
    • Jonathan Moses, Site 0080 · Contact · 650-721-2250
    Not yet recruiting
  • University of California Davis Health
    Sacramento, California 95817, United States
    • Trinh Truong, Site 0096 · Contact · 310-597-1251
    Recruiting
  • Local Institution - 0007
    Hartford, Connecticut 06106, United States
    Completed
  • Local Institution - 0064
    Washington D.C., District of Columbia 20010, United States
    Completed
  • Local Institution - 0075
    Orlando, Florida 32803, United States
    Completed
  • Local Institution - 0016
    Atlanta, Georgia 30342, United States
    Completed
  • Local Institution - 0101
    Park Ridge, Illinois 60068, United States
    • Site 0101 · Contact
    Not yet recruiting
  • Local Institution - 0100
    Indianapolis, Indiana 46202, United States
    • Site 0100 · Contact
    Not yet recruiting
  • Local Institution - 0049
    Iowa City, Iowa 52242, United States
    Completed
  • Maine Medical Partners
    Portland, Maine 04102, United States
    • Noah Hoffman, Site 0090 · Contact · 207-662-5522
    Not yet recruiting
  • Boston Children's Hospital
    Boston, Massachusetts 02115, United States
    • Athos Bousvaros, Site 0005 · Contact · 617-699-1021
    Recruiting
  • Local Institution - 0042
    Springfield, Massachusetts 01199, United States
    Completed
  • University of Massachusetts Chan Medical School
    Worcester, Massachusetts 01655, United States
    • Basavaraj Kerur, Site 0095 · Contact · 774-441-8082
    Recruiting
  • Local Institution - 0093
    Detroit, Michigan 48201, United States
    Completed
  • Mayo Clinic in Rochester, Minnesota
    Rochester, Minnesota 55905, United States
    • Michael Stephens, Site 0070 · Contact · 111111
    Recruiting
  • Washington University
    St Louis, Missouri 63110, United States
    • Charles Samson, Site 0053 · Contact · 513-518-8949
    Recruiting
  • Local Institution - 0028
    New York, New York 10029, United States
    Completed
  • Columbia University Medical Center
    New York, New York 10032, United States
    • JOSEPH PICORARO, Site 0040 · Contact · 212-305-5903
    Recruiting
  • Local Institution - 0023
    New York, New York 10065, United States
    Withdrawn
  • University of North Carolina Medical Center
    Chapel Hill, North Carolina 27599, United States
    Withdrawn
  • Local Institution - 0047
    Charlotte, North Carolina 28203, United States
    Completed
  • Cleveland Clinic
    Cleveland, Ohio 44124, United States
    • Jessica Barry, Site 0036 · Contact · 216444231
    Recruiting
  • Local Institution - 0062
    Oklahoma City, Oklahoma 73112, United States
    Withdrawn
  • Local Institution - 0045
    Hershey, Pennsylvania 17033, United States
    Completed
  • Local Institution - 0099
    Charleston, South Carolina 29425, United States
    • Site 0099 · Contact
    Not yet recruiting
  • Local Institution - 0103
    Fort Worth, Texas 76104, United States
    • Site 0103 · Contact
    Not yet recruiting
  • Texas Children's Hospital
    Houston, Texas 77030, United States
    • Lina Karam, Site 0067 · Contact · 832-822-3612
    Recruiting
  • Seattle Children's Hospital
    Seattle, Washington 98105, United States
    • Ghassan Wahbeh, Site 0060 · Contact · 111111
    Recruiting
  • Local Institution - 0091
    Seattle, Washington 98122, United States
    Completed
  • MultiCare Health System
    Tacoma, Washington 98405, United States
    • Raghu Varier, Site 0046 · Contact · 503-847-4748
    Recruiting
  • Local Institution - 0037
    Milwaukee, Wisconsin 53226, United States
    Completed
  • The Children's Hospital at Westmead
    Westmead, New South Wales 2145, Australia
    • Shoma Dutt, Site 0094 · Contact · 0298453999
    Recruiting
  • Monash Health
    Clayton, Victoria 3168, Australia
    • Edward Giles, Site 0085 · Contact · +61395943577
    Recruiting
  • Local Institution - 0086
    Murdoch, Western Australia 6150, Australia
    Withdrawn
  • Local Institution - 0106
    Nedlands, Western Australia 6009, Australia
    • Site 0106 · Contact
    Not yet recruiting
  • Local Institution - 0076
    Brussels, Bruxelles-Capitale, Région de 1090, Belgium
    Withdrawn
  • UZ Leuven
    Leuven, Vlaams-Brabant 3000, Belgium
    • Ilse Hoffman, Site 0059 · Contact · 003216343343
    Recruiting
  • Local Institution - 0056
    Brussels, 1090, Belgium
    Completed
  • Local Institution - 0063
    Edegem, 2650, Belgium
    • Site 0063 · Contact
    Not yet recruiting
  • Centre Hospitalier Régional de la Citadelle
    Liège, 4000, Belgium
    • Emeline Bequet, Site 0061 · Contact · 32 4321 54 67
    Recruiting
  • Local Institution - 0071
    Liège, 4000, Belgium
    Withdrawn
  • Local Institution - 0083
    Hamilton, Ontario L8N 3Z5, Canada
    Withdrawn
  • Local Institution - 0104
    Toronto, Ontario M3M 0B2, Canada
    Withdrawn
  • Local Institution - 0082
    Toronto, Ontario M5G 1X8, Canada
    • Site 0082 · Contact
    Not yet recruiting
  • CHU de Toulouse - Hôpital des Enfants
    Toulouse, Haute-Garonne 31059, France
    • EMMANUEL MAS, Site 0058 · Contact · 0685946782
    Recruiting
  • Local Institution - 0022
    Bron, 69500, France
    Completed
  • Centre Hospitalier Universitaire de Caen - Hôpital Côte de Nacre
    Caen, 14033, France
    • Claire Dupont-Lucas, Site 0030 · Contact · 33668354806
    Recruiting
  • Local Institution - 0017
    Paris, 75015, France
    Completed
  • Local Institution - 0073
    Paris, 75571, France
    Withdrawn
  • Local Institution - 0032
    München, Bavaria 80337, Germany
    Completed
  • Universitätsklinikum Leipzig
    Leipzig, Saxony 04103, Germany
    • Gunter Flemming, Site 0097 · Contact · +49-341-9726111
    Recruiting
  • Local Institution - 0031
    Dresden, 01307, Germany
    Completed
  • Schneider Children's Medical Center
    Petah Tikva, Central District 49202, Israel
    • Dror Shouval, Site 0020 · Contact · 03-9253673
    Recruiting
  • Shaare Zedek Medical Center
    Jerusalem, Jerusalem 9013102, Israel
    • Dan Turner, Site 0019 · Contact · 02-6666482
    Recruiting
  • Rambam Health Care Campus
    Haifa, Northern District 3109601, Israel
    • Ron Shaoul, Site 0018 · Contact · 04-7774381
    Recruiting
  • Aichi Children's Health and Medical Center
    Ōbu, Aichi-ken 474-8710, Japan
    • Naomi Iwata, Site 0025 · Contact · 81562430500
    Recruiting
  • Kurume University Hospital
    Kurume-shi, Fukuoka 8300011, Japan
    • Tatsuki Mizuochi, Site 0011 · Contact · +81-942-35-3311
    Recruiting
  • Komatsu Municipal Hospital
    Komatsu, Ishikawa-ken 923-8560, Japan
    • HISASHI KANEDA, Site 0068 · Contact · 81-761-22-7111
    Recruiting
  • Saiseikai Yokohamashi Tobu Hospital
    Yokohama, Kanagawa 2300012, Japan
    • shuichiro umetsu, Site 0038 · Contact · +81455763000
    Recruiting
  • Osaka Medical and Pharmaceutical University Hospital
    Takatsuki, Osaka 569-8686, Japan
    • Emiri Kaji, Site 0021 · Contact · 81-726-83-1221
    Recruiting
  • Institute of Science Tokyo Hospital
    Bunkyo-Ku, Tokyo 113-8519, Japan
    • Toshimitsu Fujii, Site 0024 · Contact · +81-3-5803-5877
    Recruiting
  • National Center for Child Health and Development
    Setagaya-ku, Tokyo 1578535, Japan
    • Katsuhiro Arai, Site 0009 · Contact · +81-3-3416-0181
    Recruiting
  • Tokyo Medical University Hospital
    Shinjuku-ku, Tokyo 160-0023, Japan
    • Shigeo Nishimata, Site 0033 · Contact · 81333426111
    Recruiting
  • Hiroshima University Hospital
    Hiroshima, 734-8551, Japan
    • Shiro Oka, Site 0069 · Contact
    Recruiting
  • Juntendo University Hospital
    Tokyo, 113-8431, Japan
    • Takahiro Kudo, Site 0010 · Contact · +81-3-3813-3111
    Recruiting
  • Local Institution - 0084
    Krakow, Lesser Poland Voivodeship 30-663, Poland
    Withdrawn
  • Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu
    Wroclaw, Lower Silesian Voivodeship 50-369, Poland
    • Tomasz Pytrus, Site 0012 · Contact · +48 71 7703045
    Recruiting
  • WIP Warsaw IBD Point Profesor Kierkuś
    Warsaw, Masovian Voivodeship 00-728, Poland
    • Monika Meglicka, Site 0043 · Contact · +48603508908
    Recruiting
  • Centrum Zdrowia Dziecka w Warszawie
    Warsaw, Masovian Voivodeship 04-746, Poland
    • Jaroslaw Kierkus, Site 0014 · Contact · +48500111648
    Recruiting
  • Local Institution - 0015
    Rzeszów, Podkarpackie Voivodeship 35-302, Poland
    Withdrawn
  • Local Institution - 0013
    Gdansk, Pomeranian Voivodeship 80-803, Poland
    Withdrawn
  • Local Institution - 0079
    Gdansk, Pomeranian Voivodeship 80-803, Poland
    Withdrawn
  • Twoja Przychodnia SCM
    Szczecin, West Pomeranian Voivodeship 71-434, Poland
    • Beata Gawdis-Wojnarska, Site 0088 · Contact · +48664929399
    Recruiting
  • Local Institution - 0092
    Lodz, Łódź Voivodeship 91-738, Poland
    Completed
  • Clinical Research Puerto Rico
    San Juan, 00909-1711, Puerto Rico
    • Antonio Del Valle-Segarra, Site 0098 · Contact · 787-723-5945
    Recruiting
  • Local Institution
    Moscow, 119991, Russia
    Withdrawn
  • Local Institution
    Moskva, 119571, Russia
    Withdrawn
  • Local Institution - 0048
    Badalona, Barcelona [Barcelona] 08916, Spain
    Completed
  • Local Institution - 0051
    Esplugues de Llobregat, Barcelona [Barcelona] 08950, Spain
    Completed
  • Local Institution - 0044
    Madrid, Madrid, Comunidad de 28009, Spain
    Completed
  • Local Institution - 0057
    Madrid, 28007, Spain
    Completed
  • Local Institution - 0050
    Madrid, 28046, Spain
    Withdrawn
  • Birmingham Children's Hospital
    Birmingham, England B4 6NH, United Kingdom
    • Rafeeq Muhammed, Site 0054 · Contact · +44 121 333 9999
    Recruiting
  • King's College Hospital
    London, Greater London SE5 9RS, United Kingdom
    • Babu Vadamalayan, Site 0026 · Contact · +44 20 3299 9000
    Recruiting
  • Local Institution - 0105
    London, Greater London SW10 9NH, United Kingdom
    • Site 0105 · Contact
    Not yet recruiting
  • Barts Health NHS Trust
    London, London, City of E1 1BB, United Kingdom
    • Protima Deb, Site 0066 · Contact · 02035941551
    Recruiting
07

References and documents

Individual participant data

Plan to share: Yes — BMS will provide access to individual anonymized participant data upon request from qualified researchers, and subject to certain criteria. Additional information regarding Bristol Myer Squibb's data sharing policy and process can be found at https://www.bms.com/researchers-and-partners/clinical-trials-and-research.html

Supporting information: Study protocol, Sap, Csr

08

Registry details

Key details

Study ID
NCT05076175
Lead sponsor
Bristol-Myers Squibb
Responsible party
Sponsor
First posted
Oct 13, 2021
Start date
May 30, 2022
Primary completion
Jul 12, 2032 (estimated)
Completion
Jul 12, 2032 (estimated)
Last update
Sep 24, 2026

Study contacts

BMS Clinical Trials Contact Center www.BMSClinicalTrials.com
Contact
Clinical.Trials@bms.com
855-907-3286
First line of the email MUST contain NCT # and Site #.
Contact
Bristol-Myers Squibb
study director · Bristol-Myers Squibb

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Interested in this study?

Eligibility is decided by the study team. Share this record with your doctor or contact the team directly.

Contact study team

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion