CClinicalTrials.gg
CompletedNCT04598451ADDRESSUpdated Oct 1, 2024Results posted

A Study to Assess the Efficacy and Safety of a Subcutaneous Formulation of Efgartigimod PH20 SC in Adults With Pemphigus (Vulgaris or Foliaceus)

A Phase 3 interventional study of efgartigimod PH20 SC and Placebo in Pemphigus Vulgaris and Pemphigus Foliaceus, sponsored by argenx. Completed at 134 sites in 21 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2024-10-01.

Sponsored by argenx · Phase 3, Interventional, and Treatment

Phase
Phase 3
Study type
Interventional
Enrollment
222
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

This is a prospective, multicenter, randomized, double-blinded, placebo-controlled trial to investigate the efficacy, safety, patient outcome measures, tolerability, immunogenicity, PK, and PD of efgartigimod PH20 SC in adult participants aged from 18 years with PV or PF. The trial comprises a screening period of up to 3 weeks, a treatment period of up to 30 weeks, and an 8-week follow-up period for participants who do not enroll into the open-label extension (OLE) trial ARGX-113-1905. The primary objective of the ARGX-113-1904 trial is to demonstrate the efficacy of subcutaneous administration of efgartigimod co-formulated with recombinant human hyaluronidase PH20 (Efgartigimod PH20 SC) compared to placebo in the treatment of participants with Pemphigus Vulgaris (PV). Secondary objectives are to also demonstrate the efficacy of efgartigimod PH20 SC in the treatment of participants with Pemphigus Foliaceus (PF), and to demonstrate early onset of action and a prednisone-sparing effect. After confirmation of eligibility, participants will be randomized in a 2: 1 ratio to receive efgartigimod PH20 SC or placebo

02

Conditions studied

  • Pemphigus Vulgaris
  • Pemphigus Foliaceus

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03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Ability to understand the requirements of the trial, to provide written informed consent (including consent for the use and disclosure of research-related health information), willingness and ability to comply with the trial protocol procedures (including required trial visits).
  2. The participant is male or female, and aged from 18 years at the time of signing the informed consent form (ICF).
  3. The participant has a clinical diagnosis of PV (mucosal, cutaneous, mucocutaneous) or PF which has been confirmed by cutaneous histology, positive direct immunofluorescence (IF), and positive indirect IF and/or enzyme-linked immunosorbent assay (ELISA).
  4. The participant meets one of the following profiles:

    1. Newly diagnosed disease with PDAI ≥15 at baseline and naïve to treatment
    2. Newly diagnosed disease with PDAI ≥15 while receiving a first course of oral prednisone (or equivalent). According to clinical judgment, the participant has shown no significant improvement of PV or PF signs for at least 2 weeks before baseline and is considered fit to start prednisone treatment at 0.5 mg/kg qd at baseline.
    3. Experiencing flare with PDAI ≥15, a maximum of 4 years since diagnosis, and off prednisone therapy ± a conventional immunosuppressant (e.g., azathioprine, cyclophosphamide, methotrexate, mycophenolate mofetil) or dapsone. Note: conventional immunosuppressants and dapsone must be discontinued before baseline.
    4. Experiencing flare with PDAI ≥15, a maximum of 4 years since diagnosis, and receiving a tapered dose of oral prednisone (or the equivalent), provided that prednisone has been given at stable dose ± a conventional immunosuppressant for at least 2 weeks and patients are fit to start prednisone treatment at 0.5 mg/kg qd at baseline.
  5. Contraceptive use by men and women should be consistent with local regulations regarding the methods of contraception for those participating clinical trials and:

    1. Male participants: Male participants must agree to use acceptable method of contraception, and not donate sperm from signing the ICF until the end of the study.
    2. Female participants: Women of childbearing potential must:

      • have a negative serum pregnancy test at screening and negative urine pregnancy test at baseline before the IMP can be administered.
      • agree to use a highly effective or acceptable contraception method, which should be maintained at minimum until after the last dose of IMP
  6. For Japanese participants enrolled in sites in Japan only: A Japanese participant is defined as a participant whose parents and 4 grandparents are Japanese, and who has Japanese nationality, was born in Japan, has not lived outside of Japan for a total of >10 years, and currently lives in Japan.

Exclusion criteria

Exclusion Criteria:

  1. Participant has a confirmed diagnosis of paraneoplastic pemphigus, drug-induced pemphigus, pemphigus vegetans, pemphigus erythematosus, or any other non-PV/non-PF autoimmune blistering disease.
  2. Participants with mild disease severity as defined by PDAI \<15 at baseline.
  3. Participants who show a significant improvement of PV or PF in the period from screening to baseline according to clinical judgment (eg, the patient has achieved DC or a substantial reduction in PDAI activity score during screening period).
  4. The participant has been administered therapy(ies) other than oral prednisone or conventional immunosuppressants (e.g., azathioprine, cyclophosphamide, methotrexate, mycophenolate mofetil) or dapsone within 2 months before the baseline visit and that can affect clinical disease activity. For example, excluded medications are intravenous methylprednisolone, dapsone, sulfasalazine, tetracyclines, nicotinamide at doses above the recommended daily allowance (RDA)/dietary reference intake (DRI), plasmapheresis/ plasma exchange, immunoadsorption, and IVIg.
  5. Use of any monoclonal antibody (including rituximab or another anti-CD20 biologic) within 6 months before the baseline visit.
  6. Known hypersensitivity to any of the components of the administered treatments.
  7. The participant has a known contraindication to oral prednisone.
  8. The participant has a history of refractory disease, as defined by a failure to respond to first-line and second-line therapies
  9. Participants who have a history of malignancy unless deemed cured by adequate treatment with no evidence of recurrence for ≥3 years before first IMP administration. Participants with any of the following cancers can be included at any time, provided they are adequately treated prior to their participation in the study:

    • Basal cell or squamous cell skin cancer,
    • Carcinoma in situ of the cervix,
    • Carcinoma in situ of the breast,
    • Incidental histological finding of prostate cancer
  10. Participants with clinical evidence of other significant serious disease or participants who recently underwent or have planned a major surgery during the period of the trial, or any other condition in the opinion of the investigator, that could confound the results of the trial or put the patient at undue risk.
  11. Pregnant and lactating women and those intending to become pregnant during the trial.
  12. Current or history (i.e. within 12 months of screening) of alcohol, drug, or medication abuse.
  13. Any other known autoimmune disease that, in the opinion of the investigator, would interfere with an accurate assessment of clinical symptoms of PV or PF or put the participant at undue risk.
  14. The participant has a Karnofsky Performance score \<60%.
  15. Vaccination with live viral vaccines within 28 days prior to randomization.
  16. The participant has clinically significant uncontrolled active or chronic bacterial, viral, or fungal infection.
  17. Positive serum test at screening for an active viral infection with any of the following conditions: Hepatitis B Virus, Hepatitis C Virus , HIV.
  18. The participant has total immunoglobulin G (IgG) \<6 g/L at screening.
  19. The participant has previously participated in a trial with efgartigimod and has received at least one administration of IMP.
  20. Use of an investigational drug within 3 months or 5 half-lives of the drug (whichever is longer) prior to first IMP administration
04

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
222 participants (actual)

Study arms

  • Experimental
    efgartigimod PH20 SC

    patients receiving efgartigimod PH20 SC on top of prednisone

    Biological: efgartigimod PH20 SC · Drug: prednisone

  • Experimental
    placebo

    patients receiving placebo on top of prednisone

    Other: Placebo · Drug: prednisone

Interventions

  • Biologicalefgartigimod PH20 SC

    Subcutaneous injection of efgartigimod using rHuPH20 (PH20) as a permeation enhancer

  • OtherPlacebo

    Subcutaneous injection of placebo

  • Drugprednisone

    Oral prednisone tablets

05

What researchers measure

Primary outcomes

  1. Number of Pemphigus Vulgaris (PV) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy

    Proportion of participants with pemphigus vulgaris who had CRmin within 30 weeks, defined as the absence of new lesions and complete healing of established lesions while the participant was receiving prednisone at ≤10 mg/day for at least 8 weeks.

    Time frame: up to 30 weeks treatment period

Secondary outcomes

  1. Number of Pemphigus Vulgaris (PV) and Pemphigus Foliaceus (PF) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy Within 30 Weeks

    Proportion of participants with pemphigus vulgaris and pemphigus foliaceus who had CRmin within 30 weeks, defined as the absence of new lesions and complete healing of established lesions while the participant was receiving prednisone at ≤10 mg/day for at least 8 weeks.

    Time frame: up to 30 weeks treatment period

  2. Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris Participants

    Normalized Cumulative prednisone dose (NCPD, mg/kg/day) is the average daily intake of all weight-adjusted prednisone doses received during the study, taking into account the number of days in study

    Time frame: Up to 30 weeks

  3. Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris Participants

    Time to complete remission (absence of new lesions and complete healing of established lesions) in participants with pemphigus vulgaris

    Time frame: Up to 30 weeks

  4. Time to Disease Control (DC) in Pemphigus Vulgaris (PV) Participants

    Time to disease control in participants with pemphigus vulgaris (Absence of new lesions and the start of healing of established lesions)

    Time frame: Up to 30 weeks

  5. Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

    Normalized Cumulative prednisone dose (NCPD, mg/kg/day) is the average daily intake of all weight-adjusted prednisone doses received during the study, taking into account the number of days in study

    Time frame: Up to 30 weeks

  6. Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

    Time to complete remission (absence of new lesions and complete healing of established lesions) in participants with pemphigus vulgaris and pemphigus foliaceus

    Time frame: Up to 30 weeks

  7. Time to Disease Control in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

    Time to disease control in participants with pemphigus vulgaris and pemphigus foliaceus (Absence of new lesions and the start of healing of established lesions)

    Time frame: Up to 30 weeks

06

Results

Posted Oct 1, 2024

Participant flow

Participant flow — Overall Study
MilestoneEfgartigimod PH20 SCPlacebo PH20 SC
Started14775
Completed10446
Not completed4329
Withdrew: Adverse event32
Withdrew: Withdrawal by subject37
Withdrew: Lost to follow-up20
Withdrew: Physician decision41
Withdrew: Requires prohibited medication10
Withdrew: Lack of efficacy, geopolitical situation in ukraine, flares after crmin, sae due to prednisone, etc3019

Outcome measures

PrimaryNumber of Pemphigus Vulgaris (PV) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy

Proportion of participants with pemphigus vulgaris who had CRmin within 30 weeks, defined as the absence of new lesions and complete healing of established lesions while the participant was receiving prednisone at ≤10 mg/day for at least 8 weeks.

Time frame:
up to 30 weeks treatment period
Reported as:
Count of participants · Participants
Number of Pemphigus Vulgaris (PV) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy
ParticipantsEfgartigimod PH20 SCPlacebo PH20 SC
Number of Pemphigus Vulgaris (PV) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy4420
SecondaryNumber of Pemphigus Vulgaris (PV) and Pemphigus Foliaceus (PF) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy Within 30 Weeks

Proportion of participants with pemphigus vulgaris and pemphigus foliaceus who had CRmin within 30 weeks, defined as the absence of new lesions and complete healing of established lesions while the participant was receiving prednisone at ≤10 mg/day for at least 8 weeks.

Time frame:
up to 30 weeks treatment period
Reported as:
Count of participants · Participants
Number of Pemphigus Vulgaris (PV) and Pemphigus Foliaceus (PF) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy Within 30 Weeks
ParticipantsEfgartigimod PH20 SCPlacebo PH20 SC
Number of Pemphigus Vulgaris (PV) and Pemphigus Foliaceus (PF) Participants Who Achieve Complete Clinical Remission (CR) on Minimal Prednisone Therapy Within 30 Weeks5524
SecondaryNormalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris Participants

Normalized Cumulative prednisone dose (NCPD, mg/kg/day) is the average daily intake of all weight-adjusted prednisone doses received during the study, taking into account the number of days in study

Time frame:
Up to 30 weeks
Reported as:
Mean · mg/kg/day
Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris Participants
mg/kg/dayEfgartigimod PH20 SCPlacebo PH20 SC
Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris Participants0.416 ± 0.2150.444 ± 0.232
SecondaryTime to Complete Clinical Remission (CR) in Pemphigus Vulgaris Participants

Time to complete remission (absence of new lesions and complete healing of established lesions) in participants with pemphigus vulgaris

Time frame:
Up to 30 weeks
Reported as:
Median · days
Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris Participants
daysEfgartigimod PH20 SCPlacebo PH20 SC
Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris Participants106 (79 to 161)120 (85 to 188)
SecondaryTime to Disease Control (DC) in Pemphigus Vulgaris (PV) Participants

Time to disease control in participants with pemphigus vulgaris (Absence of new lesions and the start of healing of established lesions)

Time frame:
Up to 30 weeks
Reported as:
Median · days
Time to Disease Control (DC) in Pemphigus Vulgaris (PV) Participants
daysEfgartigimod PH20 SCPlacebo PH20 SC
Time to Disease Control (DC) in Pemphigus Vulgaris (PV) Participants16 (15 to 21)15 (8 to 17)
SecondaryNormalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

Normalized Cumulative prednisone dose (NCPD, mg/kg/day) is the average daily intake of all weight-adjusted prednisone doses received during the study, taking into account the number of days in study

Time frame:
Up to 30 weeks
Reported as:
Mean · mg/kg/day
Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris and Pemphigus Foliaceus Participants
mg/kg/dayEfgartigimod PH20 SCPlacebo PH20 SC
Normalized Cumulative Prednisone Dose During the Treatment Period in Pemphigus Vulgaris and Pemphigus Foliaceus Participants0.403 ± 0.2100.431 ± 0.225
SecondaryTime to Complete Clinical Remission (CR) in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

Time to complete remission (absence of new lesions and complete healing of established lesions) in participants with pemphigus vulgaris and pemphigus foliaceus

Time frame:
Up to 30 weeks
Reported as:
Median · days
Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris and Pemphigus Foliaceus Participants
daysEfgartigimod PH20 SCPlacebo PH20 SC
Time to Complete Clinical Remission (CR) in Pemphigus Vulgaris and Pemphigus Foliaceus Participants106 (84 to 142)113 (81 to 149)
SecondaryTime to Disease Control in Pemphigus Vulgaris and Pemphigus Foliaceus Participants

Time to disease control in participants with pemphigus vulgaris and pemphigus foliaceus (Absence of new lesions and the start of healing of established lesions)

Time frame:
Up to 30 weeks
Reported as:
Median · days
Time to Disease Control in Pemphigus Vulgaris and Pemphigus Foliaceus Participants
daysEfgartigimod PH20 SCPlacebo PH20 SC
Time to Disease Control in Pemphigus Vulgaris and Pemphigus Foliaceus Participants15 (15 to 17)15 (9 to 16)

Adverse events

Collected over Up to 38 weeks. Non-serious events are listed at a 5% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Efgartigimod PH20 SC0/147 (0%)18/147 (12.2%)113/147 (76.9%)
Placebo PH20 SC0/75 (0%)10/75 (13.3%)47/75 (62.7%)
Most frequent serious events
Showing 10 of 27
Most frequent serious events
EventEfgartigimod PH20 SCPlacebo PH20 SC
COVID-19Infections and infestations2/1472/75
SPINAL COMPRESSION FRACTUREInjury, poisoning and procedural complications2/1470/75
HYPERTENSIONVascular disorders2/1470/75
ANAEMIABlood and lymphatic system disorders0/1471/75
VISION BLURREDEye disorders1/1471/75
GASTRITIS EROSIVEGastrointestinal disorders0/1471/75
URINARY TRACT INFECTIONInfections and infestations1/1471/75
DIABETES MELLITUSMetabolism and nutrition disorders1/1471/75
DIABETES MELLITUS INADEQUATE CONTROLMetabolism and nutrition disorders0/1471/75
HYPERGLYCAEMIAMetabolism and nutrition disorders0/1471/75
Most frequent other events
Showing 10 of 15
Most frequent other events
EventEfgartigimod PH20 SCPlacebo PH20 SC
HYPERTENSIONVascular disorders21/1473/75
INSOMNIAPsychiatric disorders18/1479/75
COVID-19Infections and infestations17/1473/75
MYOPATHYMusculoskeletal and connective tissue disorders9/1478/75
ORAL CANDIDIASISInfections and infestations6/1476/75
URINARY TRACT INFECTIONInfections and infestations4/1476/75
DERMATITIS ACNEIFORMSkin and subcutaneous tissue disorders7/1476/75
HYPERTRIGLYCERIDAEMIAMetabolism and nutrition disorders11/1472/75
BLOOD LACTATE DEHYDROGENASE INCREASEDInvestigations10/1473/75
INCREASED TENDENCY TO BRUISEBlood and lymphatic system disorders5/1475/75

Baseline characteristics

Age, Continuous
Age, Continuous(years)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Mean48.9 ± 12.5552.3 ± 13.3750.1 ± 12.90
Sex: Female, Male
Sex: Female, Male(Participants)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Female7342115
Male7433107
Race/Ethnicity, Customized
Race/Ethnicity, Customized(Participants)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Race — Asian491665
Race — Black or African American123
Race — White9653149
Race — Other145
Race/Ethnicity, Customized
Race/Ethnicity, Customized(Participants)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Ethnicity — Hispanic or Latino358
Ethnicity — Not Hispanic or Latino14470214
Pemphigus Vulgaris (PV)
Pemphigus Vulgaris (PV)(Participants)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Count of participants12466190
Pemphigus Foliaceus (PF)
Pemphigus Foliaceus (PF)(Participants)Efgartigimod PH20 SCPlacebo PH20 SCTotal
Count of participants23932
07

Study locations

134 sites
  • Investigator site 77 - US0010086
    Birmingham, Alabama 35233, United States
  • Investigator site 97 - US0010091
    Scottsdale, Arizona 85259, United States
  • Investigator site 121 - US0010092
    Redwood City, California 94063, United States
  • Investigator site 125 - US0010153
    Castle Rock, Colorado 80109, United States
  • Investigator site 2 - US0010087
    Boca Raton, Florida 33428, United States
  • Investigator site 99 - US0010117
    Miami, Florida 33173, United States
  • Investigator site 78 - US0010109
    Orlando, Florida 32827, United States
  • Investigator site 127 - US0010155
    West Lafayette, Indiana 47906, United States
  • Investigator site 61 - US0010090
    Minneapolis, Minnesota 55455, United States
  • Investigator site 102 - US0010098
    Saint Louis, Missouri 63110, United States
  • Investigator site 19 - US0010088
    Buffalo, New York 14203-1070, United States
  • Investigator site 136 - US0010196
    New York, New York 10128, United States
  • Investigator site 60 - US0010096
    Durham, North Carolina 27710, United States
  • Investigator site 20 - US0010094
    Cleveland, Ohio 44106-1716, United States
  • Investigator site 73 - US00100
    Philadelphia, Pennsylvania 19104, United States
  • Investigator site 101 - US0010097
    Philadelphia, Pennsylvania 19140, United States
  • Investigator site 98 - US0010107
    Dallas, Texas 75246, United States
  • Investigator site 1 - US0010084
    Dripping Springs, Texas 78620, United States
  • Investigator site 126 - US0010182
    Houston, Texas 77004, United States
  • Investigator site 88 - US0010114
    Houston, Texas 77008, United States
  • Investigator site 59 - US0010106
    Norfolk, Virginia 23502, United States
  • Investigator site 24 - AU0610006
    Sydney, New South Wales 2217, Australia
  • Investigator site 5 - AU0610007
    Parkville, Victoria 3050, Australia
  • Investigator site 103 - AU0610013
    Melbourne, 3065, Australia
  • Investigator site 30 - BG350012
    Pleven, 5800, Bulgaria
  • Investigator site 31 - BG3590013
    Plovdiv, 4000, Bulgaria
  • Investigator site 4 - BG3590010
    Sofia, 1431, Bulgaria
  • Investigator site 2 - BG3590009
    Sofia, 1510, Bulgaria
  • Investigator site 13 - BG3590011
    Sofia, 1606, Bulgaria
  • Investigator site 110 - CN0860017
    Beijing, 100034, China
  • Investigator site 111 - CN0860018
    Chendu, 610000, China
  • Investigator site 131 - CH0860027
    Chongqing, 400042, China
  • Investigator site 118 - CN0860023
    Fujian, 350005, China
  • Investigator site 120 - CN0860022
    Guangzhou, 510000, China
  • Investigator site 128 - CH0860053
    Guangzhou, 51000, China
  • Investigator site 109 - CN0860021
    Guanzhou, 510000, China
  • Investigator site 119 - CN0860024
    Nanjing, China
  • Investigator site 112 - CN0860020
    Shanghai, 200025, China
  • Investigator site 108 - CN0860016
    Shanghai, 200040, China
  • Investigator site 113 - CN0860025
    Wuhan, 430022, China
  • Investigator site 123 - CN0860019
    Wuhan, 430022, China
  • Investigator site 129 - CH0860026
    Zhengzhou, 450008, China
  • Investigator site 34 - FR0330028
    Bobigny, 93000, France
  • Investigator site 33 - FR0330027
    La Tronche, 38700, France
  • Investigator site 46 - FR0330029
    Rouen, 76031, France
  • Investigator site 32 - FR0330026
    Saint-Étienne, 42055, France
  • Investigator site 63 - GE9950014
    Tbilisi, 0159, Georgia
  • Investigator site 132 - GE9950030
    Tbilisi, 0160, Georgia
  • Investigator site 35 - GE9950013
    Tbilisi, 0162, Georgia
  • Investigator site 36 - GE9950015
    Tbilisi, 0179, Georgia
  • Investigator site 64 - DE0490029
    Berlin, 10117, Germany
  • Investigator site 48 - DE0490030
    Dresden, 01307, Germany
  • Investigator site 49 - DE0490024
    Frankfurt am main, 60590, Germany
  • Investigator site 47 - DE0490023
    Freiburg, 79104, Germany
  • Investigator site 38 - DE0490028
    Kiel, 24105, Germany
  • Investigator site 37 - DE0490002
    Lübeck, 23538, Germany
  • Investigator site 68 - DE0490001
    Marburg, 35043, Germany
  • Investigator site 25 - DE0490025
    Tübingen, 72076, Germany
  • Investigator site 79 - DE0490027
    Ulm, 89081, Germany
  • Investigator site 21 - DE0490026
    Würzburg, 97080, Germany
  • Investigator site 40 - GR0300004
    Athens, 11525, Greece
  • Investigator site 51 - GR0300006
    Athens, 16121, Greece
  • Investigator site 69 - GR0300001
    Athens, 16121, Greece
  • Investigator site 39 - GR0300003
    Chaïdári, 12462, Greece
  • Investigator site 50 - GR0300002
    Thessaloníki, 54643, Greece
  • Investigator site 41 - GR0300005
    Thessaloníki, 56429, Greece
  • Investigator site 133 - HU0360023
    Budapest, 1085, Hungary
  • Investigator site 22 - HU0360003
    Debrecen, 4032, Hungary
  • Investigator site 14 - HU0360001
    Pécs, 7632, Hungary
  • Investigator site 42 - HU0360002
    Szeged, 6720, Hungary
  • Investigator site 80 - IN0910002
    Ahmedabad, 380016, India
  • Investigator site 100 - IN0910001
    Chandigarh, 160012, India
  • Investigator site 90 - IN0910004
    Lucknow, 226005, India
  • Investigator site 91 - IN0910003
    Nagpur, 440003, India
  • Investigator site 12 - ISR9720002
    Tel Aviv, 64239, Israel
  • Investigator site 11 - IT0390006
    Roma, Lazio 00167, Italy
  • Investigator site 104 - IT0390039
    Catania, 95123, Italy
  • Investigator site 52 - IT0390031
    Firenze, 50125, Italy
  • Investigator site 92 - IT0390030
    Genova, 16132, Italy
  • Investigator site 70 - IT0390038
    Perugia, 06129, Italy
  • Investigator site 43 - IT390005
    Roma, 00168, Italy
  • Investigator site 71 - IT0390040
    Siena, 53100, Italy
  • Investigator site 94 - JP0810046
    Aichi, 480-1195, Japan
  • Investigator site 81 - JP0810040
    Hiroshima, 734-8551, Japan
  • Investigator site 85 - JP0810050
    Kurume, 830-001, Japan
  • Investigator site 82 - JP0810042
    Kōfu, 400-8506, Japan
  • Investigator site 84 - JP0810047
    Okayama, 700-8558, Japan
  • Investigator site 93 - JP0810041
    Okayama, 701-0192, Japan
  • Investigator site 86 - JP0810049
    Osaka, 545-8586, Japan
  • Investigator site 74 - JP0810045
    Sapporo, 060-8648, Japan
  • Investigator site 124 - JP0810067
    Sendai, 980-8574, Japan
  • Investigator site 83 - JP0810043
    Tokyo, 113-8431, Japan
  • Investigator site 26 - PL0480027
    Katowice, 40-081, Poland
  • Investigator site 95 - PL0480036
    Poznań, 60-369, Poland
  • Investigator site 27 - PL0480025
    Rzeszów, 35-055, Poland
  • Investigator site 28 - PL0480028
    Wrocław, 50-566, Poland
  • Investigator site 72 - PL0480032
    Łódź, 90-647, Poland
  • Investigator site 106 - RO0400013
    Bucharest, 011216, Romania
  • Investigator site 105 - RO0400014
    Cluj-Napoca, 400006, Romania
  • Investigator site 107 - RO0400015
    Iaşi, 700111, Romania

Showing the first 100 of 134 sites across 21 countries.

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References and documents

Study documents

  • Study protocol · Dec 9, 2022
  • Statistical analysis plan · Nov 22, 2023

Documents are hosted by the registry — open the source record to download them.

09

Registry details

Key details

Study ID
NCT04598451
Lead sponsor
argenx
Responsible party
Sponsor
First posted
Oct 22, 2020
Start date
Dec 1, 2020
Primary completion
Aug 22, 2023
Completion
Aug 22, 2023
Results posted
Oct 1, 2024
Last update
Oct 1, 2024

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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This study is completed, as verified in Sep 2024. You cannot join it, but the record below documents what was studied.

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Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

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