An observational study in Phenylketonurias, sponsored by BioMarin Pharmaceutical. Completed at 14 sites in United States. Open to participants aged 14 Years and older. Per ClinicalTrials.gov, last updated 2023-03-14.
Sponsored by BioMarin Pharmaceutical · Observational
This is a study for adults and children ≥ 14 years old who have Phenylketonuria (PKU) with uncontrolled plasma Phe levels. No clinical intervention or study drug is provided by BioMarin in this study.
183 studies on the registry are indexed under Phenylketonurias; 38 are open to participants now.
This study's enrollment of 32 is below the median of 40 across 60 observational studies indexed under Phenylketonurias.
Browse Phenylketonurias studies →BioMarin Pharmaceutical is the lead sponsor of 110 studies on the registry; 13 are open to participants now.
Of its 17 completed or terminated interventional studies of FDA-regulated products, 12 (71%) have results posted.
Counted across the registry records on this site, refreshed daily.
PKU Patients 14 years or older with uncontrolled plasma Phe levels
Exclusion Criteria:
Change in Plasma Phe Levels
Time frame: through study completion, an average of 2 years
Change in dietary protein intake from medical and intact food
Time frame: through study completion, an average of 2 years
This study is completed, as verified in Sep 2022. You cannot join it, but the record below documents what was studied.
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BioMarin Pharmaceutical