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CompletedNCT04424511LAKANAUpdated May 21, 2025

Effects of Mass Drug Administration of Azithromycin on Mortality and Other Outcomes Among 1-11 Month Old Infants in Mali

A Phase 3 interventional study of Placebo and Azithromycin in Mortality, sponsored by Tampere University. Completed at 1 site in Mali. Open to participants aged 29 Days to 364 Days, including healthy volunteers. Per ClinicalTrials.gov, last updated 2025-05-21.

Sponsored by Tampere University · Phase 3, Interventional, and Treatment

Phase
Phase 3
Study type
Interventional
Enrollment
149,201
Allocation
Randomized
Ages
29 Days to 364 Days
Sex
All
01

Study summary

The LAKANA trial will assess the impact on mortality and other health outcomes of quarterly and biannual azithromycin mass drug administration (MDA) when delivered to 1-11-month (29-364 days) old infants in a high-mortality setting where malaria is holoendemic but there is also a functioning seasonal malaria chemoprevention (SMC) program in place. The long-term goal is to more precisely define the role of mass azithromycin treatments as an intervention for reducing childhood mortality, and to determine the most effective treatment regimen. The main study hypotheses in terms of mortality effect are: i) Biannual azithromycin MDA to 1-11 month old infants reduces their mortality, ii) Quarterly azithromycin MDA to 1-11 month old infants reduces their mortality, iii) Quarterly azithromycin MDA has a bigger mortality effect than biannual MDA.

Read the detailed description

Mass drug administration (MDA) of azithromycin has been shown to reduce under-5 mortality in some but not all sub-Saharan African settings. Because of the observed heterogeneity and possible effect modification by SMC or other co-interventions, further trials in new settings are needed in order to make evidence-based public health recommendations about the use of this treatment. The objectives of the LAKANA trial are:

  • To evaluate the impact of two azithromycin MDA regimens on infant mortality and other health outcomes, when provided in a rural West-African high-mortality context with an ongoing seasonal malaria chemoprevention program.
  • To evaluate the effect of alternative MDA frequencies on antimicrobial resistance (AMR) and host microbiota composition.
  • To test hypotheses that azithromycin MDA eliminates malaria parasitaemia and reduces systemic and intestinal inflammation in asymptomatic children and to collect and store biological samples for assessing other possible mechanisms of azithromycin effect.
  • To investigate the feasibility of alternative azithromycin MDA strategies, including economic analysis.

The LAKANA trial will be conducted in 1151 villages from 7-10 health districts in the Kayes, Kita and Koulikoro regions of Mali. LAKANA is a cluster-randomized, placebo-controlled, double-blinded, parallel-group, three-arm clinical trial, with adaptive design. Participating villages will be randomly allocated to three different intervention groups in a ratio of 3 : 2 : 4 (control : azithromycin quarterly : azithromycin biannually). Within each participating village, consenting households will be visited quarterly (at 3-month intervals), nine times. At the first eight of these visits, 1-11-month-old eligible infants (age 29-364 days), for whom there is a consent for study drug provision, will be given a single dose of study drug (azithromycin mixture or respective placebo mixture).

Mortality and serious adverse events (SAEs) data will be collected, and mortality-related questions answered using data from all the included 1151 villages. Mixed-effect Poisson regression model will be used to estimate the intervention effects on mortality, with random intercepts for the clusters. The investigators will explore effect modification by testing for interaction between the MDA intervention and the following variables:

  • Age at the time of the MDA
  • Sex of the child
  • Weight-for-age
  • Seasonality: rainy season vs non-rainy season at the time of the MDA
  • SMC given to the child within 3 months before an MDA
  • Order of MDA in the village
  • District of residence
  • Distance from the nearest health facility (in km)
  • Household asset index
  • Water, Sanitation, and Hygiene (WASH) index
  • National outreach strategy category (standard/advanced)

The investigators will address the other study questions using a smaller separate secondary sample of 59 villages located around four selected health centers close to the city of Kita and a similar number of villages closer to Bamako, i.e. in Koulikoro or Kati (tertiary sample).

02

Conditions studied

  • Mortality

Keywords

  • Mass Drug Administration
  • Azithromycin
  • Infant and Child Mortality
  • Infant and Child health
  • Infant and Child growth
  • Infant and Child morbidity
  • Antimicrobial Resistance
  • Feasibility
  • Acceptability
  • Safety
  • Cost
  • Inflammation
  • Infection
03

Who can participate

Ages eligible
29 Days to 364 Days
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

On a cluster (village) level:

  1. Location within Kayes, Kita, or Koulikoro region of Mali
  2. Considered accessible and safe by the local health authorities and research team
  3. Considered non-urban by the local health authorities and research team
  4. Permission from community leadership

On a household level (for trial enrollment):

  1. Location within a cluster that is included in the study
  2. Verbal consent from a head of household or an adult authorized by her / him

On a child level (for receiving study medication):

  1. Residence in a household enrolled in the trial
  2. Age between 29 and 364 days
  3. Verbal consent from at least one caregiver

Exclusion criteria

Exclusion Criteria:

On child level (for not receiving study medication):

  1. Weight below 3.0 kg
  2. Known allergy to macrolides, as judged by a caregiver report of the infant experiencing an adverse reaction after oral ingestion of medication, which was deemed likely to be a macrolide by the interviewing data collector.
04

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
149,201 participants (actual)

Study arms

  • Placebo comparator
    Control

    Placebo mixture will be administered as a single dose in oral suspension form for children 1-11 months of age: 1. Single-dose of 0.5 ml / kg child weight 2. Participating households within villages allocated to this group will be visited quarterly (at 3-month intervals), for nine times. At the first eight of these visits, 1-11 month old eligible infants, for whom there is a consent for study drug provision, will be weighed and given a single dose of placebo mixture.

    Drug: Placebo

  • Active comparator
    Azithromycin-biannually (Azi-biannual)

    Azithromycin or placebo will be administered as a single dose in oral suspension form for children 1-11 months of age: 1. Single-dose of 0.5 ml / kg child weight 2. Participating households within villages allocated to this group will be visited quarterly (at 3-month intervals), for nine times. At the first eight of these visits, 1-11 month old eligible infants, for whom there is a consent for study drug provision, will be weighed and given a single dose of study drug. 3. Azithromycin will be given at quarterly visits between January and June, and Placebo mixture will be given at quarterly visits between July and December. Azithromycin dose will be 20 mg / kg.

    Drug: Placebo · Drug: Azithromycin

  • Active comparator
    Azithromycin-quarterly

    Azithromycin will be administered as a single dose in oral suspension form for children 1-11 months of age: 1. Single-dose of 0.5 ml (20 mg) / kg child weight. 2. Participating households within villages allocated to this group will be visited quarterly (at 3-month intervals), for nine times. At the first eight of these visits, 1-11 month old eligible infants, for whom there is a consent for study drug provision, will be weighed and given a single dose of azithromycin.

    Drug: Azithromycin

Interventions

  • DrugPlacebo

    Placebo mixture will be administered as a single dose in oral suspension form for children 1-11 months of age. Weight-based dosing will be used: single-dose of 0.5 ml / kg child weight.

  • DrugAzithromycin

    Azithromycin will be administered as a single dose in oral suspension form for children 1-11 months of age. Weight-based dosing will be used: single-dose of 0.5 ml (20 mg) / kg child weight.

05

What researchers measure

Primary outcomes

  1. Mortality

    Mortality rate (deaths per 1,000 years at risk) among children 1-11 months of age.

    Time frame: 3-month time interval (total of 8 intervals per cluster)

Secondary outcomes

  1. Morbidity

    Morbidity (14-day period prevalence of fever with respiratory symptoms (ARI), fever without respiratory symptoms (malaria), and diarrhea) in children aged 4-14 months assessed in each participating cluster (village) from the secondary outcome sample.

    Time frame: 3-month time interval (total of 8 intervals per cluster)

  2. Length-for-age Z-score

    Length-for-age Z-score in 6-8 and 12-14 months old children from the secondary outcome sample. Length measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial. Length-for-age Z-score will be calculated using the WHO Child Growth Standards.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  3. Length

    Attained length in cm in 6-8 and 12-14 months old children from the secondary outcome sample. Length measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  4. Weight

    Attained weight in grams in 6-8 and 12-14 months old children from the secondary outcome sample. Weight measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  5. Weight-for age Z-score

    Weight-for age Z-score in 6-8 and 12-14 months old children from the secondary outcome sample. Weight measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial. Weight-for-age Z-score will be calculated using the WHO Child Growth Standards.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  6. Weight-for-length Z-score

    Weight-for-length Z-score in 6-8 and 12-14 months old children from the secondary outcome sample. Length and weight measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial. Weight-for-length Z score will be calculated using the WHO Child Growth Standards.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  7. Mid-upper arm circumference

    Mid-upper arm circumference in 6-8 and 12-14 months old children from the secondary outcome sample. Measures will be taken at 15, 18, 21, and 24 months after the enrollment of the village into the trial.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  8. Percentage of moderate or severe stunting

    Percentage of moderate or severe stunting (length-for-age Z-score \< -2 / -3) in 6-8 and 12-14 months old children from the secondary outcome sample.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  9. Percentage of moderate or severe wasting

    Percentage of moderate or severe wasting (Weight-for-length Z-score \< -2 / -3) in 6-8 and 12-14 months old children from the secondary outcome sample.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  10. Percentage of moderate or severe Underweight

    Percentage of moderate or severe Underweight (Weight-for-age Z-score \< -2 / -3) in 6-8 and 12-14 months old children from the secondary outcome sample.

    Time frame: 3-month time interval (total of 3 intervals per cluster)

  11. Prevalence of phenotypic and genotypic macrolide resistance

    prevalence of phenotypic azithromycin resistance among S. pneumoniae or E. coli strains isolated from 4-14-month-old children, who have received 1-4 rounds of azithromycin MDA

    Time frame: 12-month time interval (total of 3 intervals per cluster)

  12. Prevalence of phenotypic and genotypic macrolide resistance

    prevalence of phenotypic azithromycin resistance among S. pneumoniae or E. coli strains isolated from 49-59-month-old children, who live in the same Malian communities but have not received azithromycin MDA

    Time frame: 12-month time interval (total of 3 intervals per cluster)

  13. Prevalence of phenotypic and genotypic macrolide resistance

    prevalence of phenotypic azithromycin resistance among S. pneumoniae or E. coli strains isolated from 15-26-month-old children, who have received 1-4 rounds of azithromycin MDA and live in a village that stopped azithromycin MDA 1 year before

    Time frame: 12-month time interval (total of 3 intervals per cluster)

  14. Prevalence of phenotypic and genotypic macrolide resistance

    prevalence of phenotypic azithromycin resistance among S. pneumoniae or E. coli strains isolated from 24-35-month-old children, who have received 1-4 rounds of azithromycin MDA 1 year before and who live in a village that continued azithromycin MDA

    Time frame: 12-month time interval (total of 3 intervals per cluster)

  15. Prevalence of phenotypic and genotypic AMR resistance to other "ACCESS" group antibiotics

    Prevalence of phenotypic and genotypic AMR against other antibiotics categorised by the World Health Organization (WHO) into "ACCESS" group, among azithromycin-resistant E. coli strains isolated from stool samples or azithromycin-resistant S. pneumoniae strains isolated from nasopharyngeal swabs (secondary outcome sample).

    Time frame: 12-month time interval (total of 3 intervals per cluster)

  16. Blood C-reactive protein concentration

    Biological samples taken from 4-11 months old infants to assess effect of azithromycin MDA on systemic inflammation (blood C-reactive protein concentration) (secondary outcome sample).

    Time frame: Biological samples taken before and 14 days after the fourth MDA round, 9 months after village enrollment.

  17. Blood malaria parasitemia and hemoglobin concentration

    Biological samples taken from 4-11 months old infants to assess effect of azithromycin MDA on malaria prevalence and blood hemoglobin concentration (secondary outcome sample).

    Time frame: Biological samples taken before and 14 days after the fourth MDA round, 9 months after village enrollment.

  18. Fecal neopterin, myeloperoxidase, and alpha-1-antitrypsin concentrations

    Biological samples taken from 4-11 months old infants to assess effect of azithromycin MDA on intestinal inflammation and function (secondary outcome sample).

    Time frame: Biological samples taken before and 14 days after the fourth MDA round, 9 months after village enrollment.

  19. Incidence of Adverse events

    Incidence of adverse events within 14 days of study drug administration. Data collected from 4-11 months old infants at 9 months after enrollment (secondary outcome sample).

    Time frame: 3-month time interval

  20. Incidence of Serious Adverse events

    Incidence of serious adverse events (Death, life-threatening event, hospitalization, and other serious events as judged by a study physician) within 14 days of study drug administration, among 1-11 months old infants.

    Time frame: within 14 days after MDA round.

  21. Mortality in children aged 12-59 month

    Mortality rate (deaths per 1000 years at risk) among children who were 12-59 month old when the latest azithromycin MDA took place in their village of residence.

    Time frame: 3-month time interval (total of 8 intervals per cluster)

  22. Percentage of guardians and health care workers reporting MDA acceptable

    Data collected through interviews of guardians and health care workers to assess acceptability of MDA.

    Time frame: 24 months after enrollment

  23. Percentage of the study population reached with MDA

    Data collected on MDA distribution and through interviews of guardians and health care workers to assess equity of MDA.

    Time frame: 24 months after enrollment

  24. Cost and Cost-effectiveness of the intervention

    Data collected on MDA distribution to assess the economic aspects of MDA.The effectiveness will be determined by the trial outcome - both the primary outcome of mortality and the secondary outcomes of morbidity and possible AMR effects. The effectiveness will be expressed in different units such as deaths averted, or disability adjusted life years (DALYs).

    Time frame: 24 months after enrollment

06

Study locations

1 site
  • Center for Vaccine Development CVD-Mali
    Bamako, BP 251, Mali
07

References and documents

Study documents

  • Protocol, analysis plan and consent form · Nov 13, 2024

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: Yes — Individual participant data collected during the trial, after deidentification. (The details are to be determined).

Supporting information: Study protocol, Sap, Icf, Csr

08

Registry details

Key details

Study ID
NCT04424511
Lead sponsor
Tampere University
Collaborators
Center for Vaccine Development CVD-Mali, Bamako, Mali, University College London Hospitals, Tro Da Ltd, UK, Duke-NUS Graduate Medical School, Bill and Melinda Gates Foundation (Funder), Pfizer Inc. (Provider of study drugs)
Responsible party
Per Ashorn (MD, PhD, Professor of Pediatrics, Tampere University) — Principal investigator
First posted
Jun 11, 2020
Start date
Oct 15, 2020
Primary completion
Dec 31, 2024
Completion
Dec 31, 2024
Last update
May 21, 2025

Study contacts

Per Ashorn, MD, PhD
principal investigator · Center for Child Health Research, Tampere University
Ulla Ashorn, PhD
principal investigator · Center for Child Health Research, Tampere University
Samba Sow, MD, MSc
principal investigator · Center for Vaccine Development CVD-Mali
Nigel Klein, MBBS, PhD
principal investigator · University College London Hospitals
Camilla Ducker, MBBS, MSc
principal investigator · Tro Da Ltd, UK
Yin Bun Cheung, PhD
principal investigator · Centre for Quantitative Medicine, Duke-NUS Medical School
Dagmar Alber, PhD
principal investigator · University College London Hospitals

Oversight

Data monitoring committee
Yes
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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