CClinicalTrials.gg
CompletedNCT03996603IMPLOREUpdated May 7, 2024Results posted

Investigation of Microbiomes of Postmenopausal Women Looking for Outcomes and Response to Estrogen Therapy

A Phase 4 interventional study of Conjugated Estrogens Cream in Female Urogenital Diseases, Vaginal Atrophy and Postmenopausal Atrophic Vaginitis, sponsored by University of Alabama at Birmingham. Completed at 1 site in United States. Open to female participants aged 55 Years and older. Per ClinicalTrials.gov, last updated 2024-05-07.

Sponsored by University of Alabama at Birmingham · Phase 4, Interventional, and Basic science

Phase
Phase 4
Study type
Interventional
Enrollment
25
Allocation
Non-randomized
Ages
55 Years and older
Sex
Female
01

Study summary

In this proposed pilot study, 16S ribosomal RNA (rRNA) gene sequencing will be used in the analysis of bacterial communities (microbiomes) in postmenopausal women with vulvovaginal atrophy (VVA) before and after eight weeks of vaginal estrogen use. The investigators plan to characterize the composition and dynamics of the microbiomes of the vagina, bladder, and rectum for quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) before and after eight weeks of local vaginal estrogen therapy. Although the vagina, bladder, and gut microbiomes have been increasingly independently studied, less is known about the interactions of the bacterial communities among the three environments as well as the dynamic relationship with menopausal status and vaginal estrogen therapy and the investigators seek to elucidate these relationships further.

Read the detailed description

This is an open-label pilot study of vaginal estrogen therapy in postmenopausal participants with vulvovaginal atrophy. The investigators seek to evaluate the effects of vaginal estrogen therapy on the vaginal, urinary, and rectal bacterial communities (microbiomes) and assess the (i) quantitative change in relative abundance of Lactobacillus among the community composition of bacteria in the vagina, and (ii) to evaluate the vaginal maturation index (VMI), vaginal pH, and vaginal inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF (IL - Interleukin, TNF - tumor necrosis factor, MCP - monocyte chemoattractant protein, GM - granulocyte macrophage, CSF - colony stimulating factor) and correlate any notable changes with changes noted in the vaginal microbiome, and (iii and iv) observe for quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) among the bladder and rectal microbiomes. These changes will also be compared to the results yielded from the vaginal microbiome analysis. Additionally the investigators will assess for quantitative changes in the bladder and rectal inflammatory biomarkers (IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF) and correlate these findings with any notable changes in the bladder and rectal microbiomes. Furthermore, changes in these biomarkers will be compared with the data (inflammatory and microbial) yielded from vaginal sampling. Bio-specimens and patient questionnaires will be assessed at baseline and again after eight weeks of vaginal estrogen therapy.

20 participants will receive the intervention (vaginal estrogen therapy) for 8 weeks. 5 participants who meet the same inclusion/exclusion criteria will not receive the intervention and will be sampled at the same time points. The additional 5 participants are intended to serve as a control cohort to demonstrate stability of the microbiome over the study period. The 5 participants may be compared to the 20 participants receiving therapy but that is not part of the primary or secondary outcomes.

The investigators believe that examining the dynamic relationships of the genitourinary-rectal region is innovative and vital to validating the investigator's understanding and assumptions of the pathophysiology and treatment approaches of this disorder.

02

Conditions studied

  • Female Urogenital Diseases
  • Vaginal Atrophy
  • Postmenopausal Atrophic Vaginitis
  • Genitourinary Disease
  • Postmenopausal Symptoms

Keywords

  • Genitourinary Syndrome of Menopause
  • Vaginal Atrophy
  • Vaginal Estrogen Therapy
  • Inflammatory Response
  • Microbial Colonization
  • Urinary Microbiome
  • Vaginal Microbiome
  • Rectal Microbiome
  • Conjugated Estrogen Cream
03

Who can participate

Ages eligible
55 Years and older
Sexes eligible
Female
Accepts healthy volunteers
No

Inclusion criteria

  • Postmenopausal with vulvovaginal atrophy
  • Age ≥55 years old and a screening vaginal pH of ≥5.
  • Without menses for ≥12 months.
  • No uterovaginal or vaginal vault prolapse beyond the hymen.
  • No estrogen replacement within the last month (may come off current treatment, i.e. wash out, to join the study)

Exclusion criteria

Exclusion Criteria:

  • Patients with BMI >35kg/m2
  • Any patients with infections requiring antibiotic or antifungal therapy during the study period.
  • Study patients may not use any vaginal suppositories, douches, or vaginal hygiene wipes within the month preceding enrollment. For patients already on hormone therapy, will be allowed to undergo a "wash out" period of estrogen or progesterone products for one month prior to enrollment.
  • Additional exclusions included patients with systemic conditions requiring immunosuppressive drugs, currently receiving chemotherapy, or history of pelvic radiation.
  • Any patients with contraindications to vaginal estrogen therapy including: vaginal bleeding of unknown etiology; known, suspected, or history of breast cancer or estrogen-dependent neoplasia; active DVT, PE, or h/o these conditions; active arterial thromboembolic disease (ie. stroke or MI) or h/o of these; known liver disease or thrombophilic disorders.
  • Current tobacco use.
  • Allergy to Premarin® or its constituents.
  • Concurrent use of steroid creams for other indications (ie. lichen sclerosis)
04

Study design

Phase
Phase 4
Primary purpose
Basic science
Allocation
Non-randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
25 participants (actual)

Study arms

  • Experimental
    Conjugated Estrogens Cream

    0.625mg/1g cream, 1g applied vaginally nightly for 2 weeks then 2x/week for 8 weeks

    Drug: Conjugated Estrogens Cream

  • No intervention
    Control Cohort

    No intervention will be given.

Interventions

  • DrugConjugated Estrogens Cream

    0.625mg/1g cream, 1g applied vaginally nightly for 2 weeks then 2x/week for 8 weeks

    Also known as: Premarin Vaginal Cream

05

What researchers measure

Primary outcomes

  1. Quantitative Change in Relative Abundance of Lactobacillus Among the Community Composition of Bacteria in the Vagina

    The relative abundance of the Lactobacillus genus, as measured by 16S ribosomal RNA (rRNA) gene sequencing, is the proportion of Lactobacillus genus among the total vaginal microbiome. After analysis of the gene sequencing, the total yield of bacteria at the genus level equals 1. The quantitative change in relative abundance of Lactobacillus among the community composition of bacteria in the vagina will be assessed from baseline to 8 weeks. The investigators hypothesize that a pre-specified statistically significant quantitative increase in the relative abundance of Lactobacillus will be seen among the participants that receive treatment.

    Time frame: Baseline, 8 weeks

Secondary outcomes

  1. Change in Vaginal Maturation Index (VMI)

    The maturation value (MV) is calculated with the following formula: MV = % surface cells + (0.5 × % intermediate cells). The outcome data is reported as the delta change from baseline to 8 weeks. The data for the primary outcome has been entered using the "measure type - NUMBER" because the outcome is a delta or change in the vaginal maturation index.

    Time frame: Baseline, 8 weeks

  2. Change in Vaginal pH

    Change in the vaginal pH from baseline to 8 weeks

    Time frame: Baseline, 8 weeks

  3. Vaginal Inflammatory Biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF

    Change in the vaginal inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

    Time frame: Baseline, 8 weeks

Other outcomes

  1. Quantitative and Qualitative Changes in the Distribution of Operational Taxonomic Units (OTUs) in the Bladder Microbiome.

    Quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) from baseline to 8 weeks.

    Time frame: Baseline, 8 weeks

  2. Quantitative and Qualitative Changes in the Distribution of Operational Taxonomic Units (OTUs) in the Rectal Microbiome.

    Quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) from baseline to 8 weeks.

    Time frame: Baseline, 8 weeks

  3. Bladder Inflammatory Biomarkers (IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF)

    Change in the concentration of bladder inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

    Time frame: Baseline, 8 weeks

  4. Rectal Inflammatory Biomarkers (IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF)

    Change in the concentration of rectal inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

    Time frame: Baseline, 8 weeks

06

Results

Posted May 7, 2024

Participant flow

Participant flow — Overall Study
MilestoneConjugated Estrogens CreamControl Cohort
Started205
Completed165
Not completed40

Outcome measures

PrimaryQuantitative Change in Relative Abundance of Lactobacillus Among the Community Composition of Bacteria in the Vagina

The relative abundance of the Lactobacillus genus, as measured by 16S ribosomal RNA (rRNA) gene sequencing, is the proportion of Lactobacillus genus among the total vaginal microbiome. After analysis of the gene sequencing, the total yield of bacteria at the genus level equals 1. The quantitative change in relative abundance of Lactobacillus among the community composition of bacteria in the vagina will be assessed from baseline to 8 weeks. The investigators hypothesize that a pre-specified statistically significant quantitative increase in the relative abundance of Lactobacillus will be seen among the participants that receive treatment.

Time frame:
Baseline, 8 weeks
Reported as:
Median · Relative abundance
Quantitative Change in Relative Abundance of Lactobacillus Among the Community Composition of Bacteria in the Vagina
Relative abundanceConjugated Estrogens CreamControl Cohort
Baseline0.07 (0.02 to 0.14)0.09 (0.03 to 0.45)
8 weeks0.12 (0.06 to 0.96)0.04 (0.04 to 0.2)
SecondaryChange in Vaginal Maturation Index (VMI)

The maturation value (MV) is calculated with the following formula: MV = % surface cells + (0.5 × % intermediate cells). The outcome data is reported as the delta change from baseline to 8 weeks. The data for the primary outcome has been entered using the "measure type - NUMBER" because the outcome is a delta or change in the vaginal maturation index.

Time frame:
Baseline, 8 weeks
Reported as:
Median · Change in vaginal maturation index value
Change in Vaginal Maturation Index (VMI)
Change in vaginal maturation index valueConjugated Estrogens CreamControl Cohort
Baseline35 (10 to 47.5)42.5 (17.5 to 50)
8 weeks60 (50 to 65)47.5 (45 to 52.5)
SecondaryChange in Vaginal pH

Change in the vaginal pH from baseline to 8 weeks

Time frame:
Baseline, 8 weeks
Reported as:
Median · Vaginal pH
Change in Vaginal pH
Vaginal pHConjugated Estrogens CreamControl Cohort
Baseline7.25 (6.5 to 7.5)7 (5.5 to 8.0)
8 weeks5 (4.5 to 5.5)7 (5.5 to 7.5)
SecondaryVaginal Inflammatory Biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF

Change in the vaginal inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

Time frame:
Baseline, 8 weeks
Reported as:
Median · pg/mg
Vaginal Inflammatory Biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF
pg/mgConjugated Estrogens CreamControl Cohort
IL-1b BASELINE44.4 (5.9 to 84.9)132.9 (28.8 to 236.9)
IL-1b 8 WEEKS10.8 (4.0 to 26.0)373.6 (10.2 to 737.1)
IL-4 BASELINE10.0 (5.3 to 23.1)18.1 (2.3 to 33.8)
IL-4 8 WEEKS2.1 (1.3 to 4.2)11.1 (5.0 to 17.2)
IL-8 BASELINE3158.2 (1956.2 to 8087.5)3724.3 (2254.4 to 5194.2)
IL-8 8 WEEKS757.5 (260.0 to 1980.3)7941.0 (2247.8 to 13643.2)
IL-10 BASELINE22.5 (14.9 to 38.2)12.7 (1.7 to 22.1)
IL-10 8 WEEKS640.7 (NA to NA)7.0 (5.1 to 14.3)
TNF-a BASELINE9.3 (8.9 to 56.9)11.6 (6.1 to 39.7)
TNF-a 8 WEEKS7.1 (6.5 to 10.1)12.0 (7.2 to 30.5)
MCP-1 BASELINE102.5 (22.1 to 232.1)29.1 (24.4 to 186.7)
MCP-1 8 WEEKS6.7 (3.3 to 31.3)59.0 (19.8 to 79.1)
Other pre-specifiedQuantitative and Qualitative Changes in the Distribution of Operational Taxonomic Units (OTUs) in the Bladder Microbiome.

Quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) from baseline to 8 weeks.

Time frame:
Baseline, 8 weeks

No measurements were reported for this outcome.

Other pre-specifiedQuantitative and Qualitative Changes in the Distribution of Operational Taxonomic Units (OTUs) in the Rectal Microbiome.

Quantitative and qualitative changes in the distribution of operational taxonomic units (OTUs) from baseline to 8 weeks.

Time frame:
Baseline, 8 weeks

No measurements were reported for this outcome.

Other pre-specifiedBladder Inflammatory Biomarkers (IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF)

Change in the concentration of bladder inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

Time frame:
Baseline, 8 weeks

No measurements were reported for this outcome.

Other pre-specifiedRectal Inflammatory Biomarkers (IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF)

Change in the concentration of rectal inflammatory biomarkers: IL-1B, IL-4, IL-6, IL-8, IL-10, TNF-a, MCP-1, GM-CSF from baseline to 8 weeks

Time frame:
Baseline, 8 weeks

No measurements were reported for this outcome.

Adverse events

Collected over 8 weeks. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Conjugated Estrogens Cream0/20 (0%)0/20 (0%)0/20 (0%)
Control Cohort0/5 (0%)0/5 (0%)0/5 (0%)

Baseline characteristics

Age, Continuous
Age, Continuous(years)Conjugated Estrogens CreamControl CohortTotal
Median65.5 (57 to 71)71 (61 to 77)66 (57 to 73)
Sex: Female, Male
Sex: Female, Male(Participants)Conjugated Estrogens CreamControl CohortTotal
Female20525
Male000
Race (NIH/OMB)
Race (NIH/OMB)(Participants)Conjugated Estrogens CreamControl CohortTotal
American Indian or Alaska Native000
Asian101
Native Hawaiian or Other Pacific Islander000
Black or African American527
White14317
More than one race000
Unknown or Not Reported000
Region of Enrollment
Region of Enrollment(Participants)Conjugated Estrogens CreamControl CohortTotal
United States20525
Body Mass Index
Body Mass Index(kg/m^2)Conjugated Estrogens CreamControl CohortTotal
Median27.3 (23.8 to 30.9)30.9 (21 to 31.5)27.3 (22.4 to 31.7)
Parity
Parity(births)Conjugated Estrogens CreamControl CohortTotal
Median2 (1.5 to 2)2 (1 to 2)2 (1 to 2)
Spontaneous Vaginal Delivery
Spontaneous Vaginal Delivery(deliveries)Conjugated Estrogens CreamControl CohortTotal
Median2 (0.5 to 2)1 (1 to 2)2 (0.5 to 2)
Hysterectomy
Hysterectomy(Participants)Conjugated Estrogens CreamControl CohortTotal
Count of participants10212

8 further baseline measures are reported on the registry.

07

Study locations

1 site
  • University of Alabama at Birmingham
    Birmingham, Alabama 35233, United States
08

References and documents

Study documents

  • Protocol and statistical analysis plan · Feb 24, 2021

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: No

09

Registry details

Key details

Study ID
NCT03996603
Lead sponsor
University of Alabama at Birmingham
Responsible party
Kyle P Norris, MD (Instructor Fellow, University of Alabama at Birmingham) — Principal investigator
First posted
Jun 25, 2019
Start date
Aug 1, 2019
Primary completion
Jan 14, 2021
Completion
Jan 14, 2021
Results posted
May 7, 2024
Last update
May 7, 2024

Study contacts

Kyle P Norris, MD
principal investigator · University of Alabama at Birmingham

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
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