CClinicalTrials.gg
RecruitingNCT03435796Updated Sep 18, 2026

Long-Term Follow-up Protocol for Participants Treated With Gene-Modified T Cells

A Phase 2/3 interventional study of Gene-modified (GM) T cell therapy in Neoplasms, sponsored by Celgene. Recruiting at 222 sites in 22 countries. Per ClinicalTrials.gov, last updated 2026-09-18.

Sponsored by Celgene · Phase 2/3, Interventional, and Other

Phase
Phase 2/3
Study type
Interventional
Enrollment
1,541
Allocation
Not applicable
Sex
All
01

Study summary

This is a prospective study for the long-term follow-up (LTFU) of safety and efficacy for all pediatric and adult participants exposed to Gene-modified (GM) T-cell therapy participating in a previous Celgene sponsored or Celgene alliance partner sponsored study.

Participants who received at least one infusion of GM T cells will be asked to enroll in this LTFU protocol upon either premature discontinuation from, or completion of the prior parent treatment protocol.

02

Conditions studied

  • Neoplasms

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Keywords

  • Long-term follow up
  • Gene-Modified T Cells
  • CAR T Cell
03

Who can participate

Ages eligible
Child (0–17), Adult (18–64), Older adult (65+)
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Received at least one gene-modified (GM) T-cell infusion in a previous Celgene sponsored, Juno Therapeutics, other affiliates of BMS, or Celgene alliance partner-sponsored trial, and have discontinued, or completed the post-treatment follow-up period in the parent treatment protocol, as applicable.
  • Must understand and voluntarily sign an Informed Consent Form/Informed Assent Form prior to any study-related assessments/procedures being conducted.

Exclusion criteria

Exclusion Criteria:

Not Applicable

Other protocol-defined inclusion/exclusion criteria apply

04

Study design

Phase
Phase 2 / Phase 3
Primary purpose
Other
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
1,541 participants (estimated)

Study arms

  • Other
    Participants exposed to Gene-modified (GM) T cell therapy

    Genetic: Gene-modified (GM) T cell therapy

Interventions

  • GeneticGene-modified (GM) T cell therapy

    No investigational product will be administered

05

What researchers measure

Primary outcomes

  1. Incidence of delayed Adverse Events (AEs)

    Time frame: Up to 15 years from last gene-modified (GM) T cell infusion

  2. Persistence of GM T cell drug products

    Time frame: Up to 15 years from last GM T cell infusion

  3. Analysis of vector integration sites

    Time frame: Up to 15 years from last GM T cell infusion

  4. Incidence of replication-competent lentiviruses

    Time frame: Up to 15 years from last GM T cell infusion

  5. Physical growth as assessed by physical examination (pediatric participants only)

    Time frame: Up to 15 years from last GM T cells infusion or until Tanner Stage 5 is reached

  6. Incidence of sexual maturation as assessed by the Tanner staging system (pediatric participants only)

    Time frame: Up to 15 years from last GM T cells infusion or until Tanner Stage 5

  7. Proportion of participants who progressed on the study: participants with original diagnosis of malignancies

    Time frame: Up to 15 years from last GM T cells infusion

  8. Overall Survival (participants with original diagnosis of malignancies)

    Time frame: Up to 15 years from last GM T cells infusion

Secondary outcomes

  1. Lymphocyte count (B-cell)

    If B-cell recovery criteria are not met at Month 60 (Year 5), then annual monitoring will continue up to 15 years, until subject withdrawal of consent, or death, whichever occurs first.

    Time frame: Up to 15 years

06

Study locations

173 of 222 sites recruiting
  • University of Alabama Birmingham
    Birmingham, Alabama 10016, United States
    • Luciano Costa, Site 01171 · Contact · 205-934-9695
    Recruiting
  • Banner MD Anderson Cancer Center
    Gilbert, Arizona 85234, United States
    • Rajneesh Nath, Site 01049 · Contact · 480-256-3223
    Recruiting
  • Mayo Clinic Phoenix
    Phoenix, Arizona 85054, United States
    • Jeremy Larsen, Site 01200 · Contact
    Recruiting
  • Local Institution - 01039
    Scottsdale, Arizona 85258, United States
    Completed
  • Local Institution - 01021
    Tucson, Arizona 85724, United States
    Withdrawn
  • City Of Hope
    Duarte, California 91010, United States
    • Tanya Siddiqi, Site 01011 · Contact · 626-256-4673
    Recruiting
  • University Of California San Diego Moores Cancer Center
    La Jolla, California 92093, United States
    • Thomas Kipps, Site 01019 · Contact · 858-822-6135
    Recruiting
  • Local Institution - 01206
    Los Angeles, California 90048, United States
    Withdrawn
  • Local Institution - 01043
    Sacramento, California 95816, United States
    Withdrawn
  • University of California, San Francisco- California
    San Francisco, California 94143, United States
    • Charalambos Andreadis, Site 01108 · Contact · 415-238-1909
    Recruiting
  • UCLA Medical Centre-Santa Monica
    Santa Monica, California 90095, United States
    • Sarah Larson, Site 01184 · Contact · 310-829-5471
    Recruiting
  • Stanford Cancer Center
    Stanford, California 94305, United States
    • Michaela Liedtke, Site 01119 · Contact · 650-498-6000
    Recruiting
  • University Of Colorado Cancer Center
    Aurora, Colorado 80045, United States
    • Manali Kamdar, Site 01208 · Contact · 720-848-0752
    Recruiting
  • Colorado Blood Cancer Institute
    Denver, Colorado 80218, United States
    • Tara Gregory, Site 01212 · Contact · 720-754-4800
    Recruiting
  • Yale Cancer Center
    New Haven, Connecticut 06520, United States
    • Iris Isufi, Site 01059 · Contact · 203-688-4242
    Recruiting
  • Local Institution - 01050
    Washington D.C., District of Columbia 20007, United States
    Withdrawn
  • The Mayo Clinic - Jacksonville, Davis-E
    Jacksonville, Florida 32224, United States
    • Sikander Ailawadhi, Site 01201 · Contact · 904-953-0853
    Recruiting
  • Sylvester Comprehensive Cancer Center, University of Miami Hospital and Clinics
    Miami, Florida 33136, United States
    • Lazaros Lekakis, Site 01214 · Contact · 305-748-0641
    Recruiting
  • Baptist Cancer Center
    Miami, Florida 33176, United States
    • Yuliya Linhares, Site 01047 · Contact · 786-596-2000
    Recruiting
  • Local Institution - 01035
    Orlando, Florida 32804, United States
    Completed
  • USF Health Morsani Center for Advanced Healthcare
    Tampa, Florida 33606, United States
    • Loutfi Succari, Site 01247 · Contact · 813-974-2681
    Recruiting
  • H. Lee Moffitt Cancer Center and Research Institute University of South Florida
    Tampa, Florida 33612, United States
    • Melissa Alsina, Site 01153 · Contact · 813-745-7202
    Recruiting
  • Winship Cancer Institute of Emory University
    Atlanta, Georgia 30322, United States
    • Sagar Lonial, Site 01103 · Contact · 404-778-1900
    Recruiting
  • Northside Hospital, Inc
    Atlanta, Georgia 30342, United States
    • Scott Solomon, Site 01207 · Contact · 404-255-1930
    Recruiting
  • Northwestern Memorial Hospital
    Chicago, Illinois 60611, United States
    • Reem Karmali, Site 01014 · Contact · 312-695-0990
    Recruiting
  • University Of Chicago Medical Center
    Chicago, Illinois 60637-1447, United States
    • Peter Riedell, Site 01018 · Contact · 773-702-8412
    Recruiting
  • Local Institution - 01040
    Maywood, Illinois 60153, United States
    Withdrawn
  • Local Institution - 01063
    Niles, Illinois 60714, United States
    Withdrawn
  • IN Univ Simon Cancer Center
    Indianapolis, Indiana 46202, United States
    • Rafat Abonour, Site 01161 · Contact · 317-690-1577
    Recruiting
  • Franciscan Health Indianapolis
    Indianapolis, Indiana 46237, United States
    • Anand Tandra, Site 01217 · Contact · 317-871-0000
    Recruiting
  • Local Institution - 01020
    Indianapolis, Indiana 46237, United States
    Completed
  • Kansas University Medical Center
    Westwood, Kansas 66205, United States
    • Al-Ola Abdallah, Site 01174 · Contact · 918-261-6196
    Recruiting
  • Cancer Center of Kansas
    Wichita, Kansas 67214, United States
    • Bassam Mattar, Site 01031 · Contact · 316-262-4467
    Recruiting
  • University Of Kentucky
    Lexington, Kentucky 40536, United States
    • Chaitanya Iragavarapu, Site 01046 · Contact
    Recruiting
  • Norton Cancer Institute Louisville Oncology
    Louisville, Kentucky 40207, United States
    • Don Stevens, Site 01032 · Contact · 502-899-3366
    Recruiting
  • Local Institution - 01026
    New Orleans, Louisiana 70112, United States
    Withdrawn
  • University of Maryland - Greenebaum Comprehensive Cancer Center
    Baltimore, Maryland 21201, United States
    • Mehmet Kocoglu, Site 01164 · Contact · 501-526-6990
    Recruiting
  • Sidney Kimmel Comp Cancer Center at Johns Hopkins
    Baltimore, Maryland 21231, United States
    • Syed Abbas Ali, Site 01017 · Contact · 443-287-7104
    Recruiting
  • Local Institution - 01114
    Bethesda, Maryland 20892-1203, United States
    Completed
  • Local Institution - 01107
    Boston, Massachusetts 02114, United States
    Withdrawn
  • Massachusetts General Hospital / Dana-Farber Cancer Institute
    Boston, Massachusetts 02114, United States
    • Jeremy Abramson, Site 01012 · Contact · 617-571-3037
    Recruiting
  • Local Institution - 01106
    Boston, Massachusetts 02115, United States
    Withdrawn
  • University of Massachusetts Memorial Medical Center
    North Worcester, Massachusetts 01655, United States
    • Poorva Bindal, Site 01213 · Contact · 774-442-3903
    Recruiting
  • University Of Michigan Comprehensive Cancer Center
    Ann Arbor, Michigan 48109, United States
    • Monalisa Ghosh, Site 01024 · Contact · 734-936-4000
    Recruiting
  • Karmanos Cancer Center Wayne State University
    Detroit, Michigan 48201, United States
    • Abhinav Deol, Site 01025 · Contact · 313-576-8093
    Recruiting
  • Local Institution - 01056
    Southfield, Michigan 48075, United States
    Completed
  • M Health Fairview University of Minnesota Medical Center - East Bank
    Minneapolis, Minnesota 55455, United States
    • Veronika Bachanova, Site 01112 · Contact · 612-625-5469
    Recruiting
  • Mayo Clinic
    Rochester, Minnesota 55905, United States
    • Yi Lin, Site 01105 · Contact
    Recruiting
  • Siteman Cancer Center
    St Louis, Missouri 63110, United States
    • Ravi Vij, Site 01176 · Contact · 314-409-4144
    Recruiting
  • University Of Nebraska Medical Center
    Omaha, Nebraska 68198-6840, United States
    • Matthew Lunning, Site 01015 · Contact · 402-559-7164
    Recruiting
  • Local Institution - 01030
    East Brunswick, New Jersey 08816, United States
    Completed
  • Hackensack University Medical Center
    Hackensack, New Jersey 07601, United States
    • David Siegel, Site 01102 · Contact · 201-996-5900
    Recruiting
  • Morristown Memorial Hosp
    Morristown, New Jersey 07962, United States
    • Mohamad Cherry, Site 01027 · Contact · 973-971-7906
    Recruiting
  • Local Institution - 01053
    New Brunswick, New Jersey 08903, United States
    Withdrawn
  • New York Oncology Hematology P.C.
    Albany, New York 12206, United States
    • Courtney Bellomo, Site 01041 · Contact
    Recruiting
  • Roswell Park Cancer Institute
    Buffalo, New York 14263, United States
    • Francisco Hernandez-Ilizaliturri, Site 01111 · Contact · 716-845-3099
    Recruiting
  • Local Institution - 01066
    New York, New York 10016, United States
    Withdrawn
  • New York University - Langone Medical Center - The Center for Musculoskeletal Care
    New York, New York 10016, United States
    • Amit Saxena, Site 01070 · Contact · 646-501-7400
    Recruiting
  • Weill Cornell Medicine / New York Presbyterian Hospital
    New York, New York 10021, United States
    • Roger Niles Pearse, Site 01198 · Contact · 212-746-2956
    Recruiting
  • Icahn School Of Medicine At Mount Sinai
    New York, New York 10029, United States
    • Sundar Jagannath, Site 01109 · Contact · 212-241-7873
    Recruiting
  • Columbia University Medical Center/New York-Presbyterian Hospital
    New York, New York 10032, United States
    • Ran Reshef, Site 01209 · Contact · 212-342-0530
    Recruiting
  • Memorial Sloan Kettering Cancer Center
    New York, New York 10065, United States
    • Maria Palomba, Site 01177 · Contact · 212-639-7186
    Recruiting
  • Local Institution - 01051
    Rochester, New York 14642, United States
    Withdrawn
  • The University of North Carolina at Chapel Hill
    Chapel Hill, North Carolina 27599, United States
    • Saira Sheikh, Site 01071 · Contact · 919-966-0545
    Recruiting
  • Levine Cancer Institute
    Charlotte, North Carolina 28204, United States
    • Bei Hu, Site 01204 · Contact · 980-442-5231
    Recruiting
  • Duke University Medical Center
    Durham, North Carolina 27705, United States
    • Taewoong Choi, Site 01175 · Contact
    Recruiting
  • Novant Health
    Salisbury, North Carolina 28147, United States
    • Alan Skarbnik, Site 01058 · Contact · 347-266-6406
    Recruiting
  • Oncology Hematology Care, Inc.
    Cincinnati, Ohio 45242, United States
    • James Essell, Site 01037 · Contact · 513-686-5482
    Recruiting
  • University Hospitals of Cleveland
    Cleveland, Ohio 44106-5000, United States
    • Leland Metheny, Site 01042 · Contact · 216-844-0139
    Recruiting
  • Cleveland Clinic Foundation
    Cleveland, Ohio 44195, United States
    • Brian Hill, Site 01062 · Contact · 216-445-9451
    Recruiting
  • Ohio State University Comprehensive Cancer Center (OSUCCC) - The James Cancer Hospital and Solove Research Institute
    Columbus, Ohio 43210, United States
    • Srinivas Devarakonda, Site 01074 · Contact · 570-423-0522
    Recruiting
  • University of Oklahoma Peggy and Charles Stephenson Cancer Center
    Oklahoma City, Oklahoma 73104, United States
    • Adam Asch, Site 01038 · Contact · 405-271-4022
    Recruiting
  • Willamette Valley Cancer Institute
    Eugene, Oregon 97401, United States
    • Jeff Sharman, Site 01052 · Contact · 541-683-5001
    Recruiting
  • Providence Portland Medical Center
    Portland, Oregon 97213, United States
    • Stacy Lewis, Site 01028 · Contact · 503-215-5696
    Recruiting
  • Oregon Health and Science University OHSU
    Portland, Oregon 97239, United States
    • Richard Maziarz, Site 01022 · Contact · 503-231-2498
    Recruiting
  • Local Institution - 01061
    Philadelphia, Pennsylvania 19104, United States
    Completed
  • University of Pennsylvania Perelman Center for Advanced Medicine
    Philadelphia, Pennsylvania 19104, United States
    • Stephen Schuster, Site 01016 · Contact · 215-614-1846
    Recruiting
  • Thomas Jefferson University - Clinical Research Institute
    Philadelphia, Pennsylvania 19107, United States
    • Xia Bi, Site 01173 · Contact · 302-220-7456
    Recruiting
  • Fox Chase Cancer Center
    Philadelphia, Pennsylvania 19111, United States
    • Asya Varshavsky-Yanovsky, Site 01172 · Contact
    Recruiting
  • UPMC Cancer Pavillion
    Pittsburgh, Pennsylvania 15232, United States
    • Alison Sehgal, Site 01210 · Contact · 412-648-6579
    Recruiting
  • Hematology and Oncology Associates of SC, LLC
    Greenville, South Carolina 29615, United States
    • Saeeda Chowdhury, Site 01034 · Contact · 864-241-6252
    Recruiting
  • Local Institution - 01064
    Sioux Falls, South Dakota 57105, United States
    Withdrawn
  • Sarah Cannon Research Inst
    Nashville, Tennessee 37203, United States
    • Jesus Berdeja, Site 01101 · Contact · 615-329-0570
    Recruiting
  • Texas Oncology
    Dallas, Texas 75230, United States
    • Jay Courtright, Site 01044 · Contact · 972-566-4291
    Recruiting
  • Texas Oncology - Baylor Charles A. Sammons Cancer Center
    Dallas, Texas 75246, United States
    • Houston Holmes, Site 01180 · Contact · 214-584-3402
    Recruiting
  • UT Southwestern Medical Center
    Dallas, Texas 75390, United States
    • Larry Anderson, Site 01104 · Contact · 214-648-5906
    Recruiting
  • The University of Texas Health Science Center at Houston
    Houston, Texas 77030, United States
    • Maureen Mayes, Site 01215 · Contact · 713-500-6905
    Recruiting
  • University of Texas- MD Anderson
    Houston, Texas 77030, United States
    • Hun Lee, Site 01013 · Contact · 713-794-1829
    Recruiting
  • Sam Clinical Research Center
    San Antonio, Texas 78229, United States
    • Paul Shaughnessy, Site 01211 · Contact · 210-670-2313
    Recruiting
  • Local Institution - 01033
    Temple, Texas 76508, United States
    Withdrawn
  • Local Institution - 01054
    Tyler, Texas 75702, United States
    Completed
  • University of Utah - Huntsman Cancer Institute
    Salt Lake City, Utah 84112, United States
    • Douglas Sborov, Site 01199 · Contact · 801-585-0255
    Recruiting
  • Intermountain Healthcare - LDS Hospital
    Salt Lake City, Utah 84143, United States
    • Dannish Hoda, Site 01029 · Contact
    Recruiting
  • University Of Virginia Health System
    Charlottesville, Virginia 22903, United States
    • Indumathy Varadarajan, Site 01065 · Contact · 434-924-9333
    Recruiting
  • Local Institution - 01045
    Norfolk, Virginia 23502, United States
    Completed
  • Local Institution - 01023
    Richmond, Virginia 23298, United States
    Withdrawn
  • Swedish Cancer Institute
    Seattle, Washington 98104, United States
    • Daniel Egan, Site 01166 · Contact · 617-699-2437
    Recruiting
  • Local Institution - 01060
    Seattle, Washington 98105, United States
    Withdrawn
  • Fred Hutchinson Cancer Center
    Seattle, Washington 98109, United States
    • Jordan Gauthier, Site 01110 · Contact · 206-667-2713
    Recruiting
  • Local Institution - 01055
    Tacoma, Washington 98405, United States
    Withdrawn

Showing the first 100 of 222 sites across 22 countries.

07

References and documents

Publications

  • Wierda WG, Dorritie KA, Gauthier J, Nath R, Kipps TJ, Riedell PA, Eradat HA, Kenderian SS, Kharfan-Dabaja MA, Shah NN, Solomon SR, Stephens DM, Ermann DA, Arnason JE, Deol A, Feldman TA, Andreadis CB, Ghosh M, Ma S, Schuster SJ, Gergis U, Vose JM, Soumerai JD, van Besien K, Tuazon SA, Perna SK, Ou SS, Ananthakrishnan R, Rane N, Papp E, Ansari S, Thompson EG, Okal A, Peiser L, Chen Y, Sengupta S, Ray PR, Wang J, Siddiqi T. Lisocabtagene maraleucel combined with ibrutinib in R/R CLL or SLL: primary results from TRANSCEND CLL 004. Blood. 2026 Jul 28:blood.2026033565. doi: 10.1182/blood.2026033565. Online ahead of print. PubMed 42520199 ↗
  • Abramson JS, Siddiqi T, Gordon LI, Lunning MA, Wang M, Arnason JE, Kamdar M, Maloney DG, Shadman M, Andreadis CB, Sehgal A, Solomon SR, Ghosh N, Hidalgo-Lopez JE, Wang J, Ding X, Ogasawara K, Singh A, Palomba ML. Five-year survival outcomes from TRANSCEND NHL 001 of lisocabtagene maraleucel in R/R LBCL. Blood. 2026 Jun 3:blood.2025032270. doi: 10.1182/blood.2025032270. Online ahead of print. PubMed 42237652 ↗
  • Abramson JS, Palomba ML, Gordon LI, Lunning M, Wang M, Arnason J, Purev E, Maloney DG, Andreadis C, Sehgal A, Solomon SR, Ghosh N, Dehner C, Kim Y, Ogasawara K, Kostic A, Siddiqi T. Two-year follow-up of lisocabtagene maraleucel in relapsed or refractory large B-cell lymphoma in TRANSCEND NHL 001. Blood. 2024 Feb 1;143(5):404-416. doi: 10.1182/blood.2023020854. PubMed 37890149 ↗

Individual participant data

Plan to share: Yes — BMS will provide access to individual anonymized participant data upon request from qualified researchers, and subject to certain criteria. Additional information regarding Bristol Myer Squibb's data sharing policy and process can be found at https://www.bms.com/researchers-and-partners/clinical-trials-and-research.html

Supporting information: Study protocol, Sap, Csr

08

Registry details

Key details

Study ID
NCT03435796
Lead sponsor
Celgene
Responsible party
Sponsor
First posted
Feb 19, 2018
Start date
Jul 19, 2018
Primary completion
May 29, 2043 (estimated)
Completion
May 29, 2043 (estimated)
Last update
Sep 18, 2026

Study contacts

BMS Clinical Trials Contact Center www.BMSClinicalTrials.com
Contact
Clinical.Trials@bms.com
855-907-3286
First line of the email MUST contain NCT # and Site #.
Contact
Bristol-Myers Squibb
study director · Bristol-Myers Squibb

Oversight

Data monitoring committee
No
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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