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CompletedNCT03375697Updated Apr 27, 2025

A Study to Investigate Safety and Tolerability, Pharmacokinetics and Pharmacodynamics of JNJ-63733657 in Healthy Subjects and Subjects With Alzheimer's Disease

A Phase 1 interventional study of JNJ-63733657 and Placebo in Alzheimer Disease, sponsored by Janssen Research & Development, LLC. Completed at 7 sites in 4 countries. Open to participants aged 55 Years to 75 Years, including healthy volunteers. Per ClinicalTrials.gov, last updated 2025-04-27.

Sponsored by Janssen Research & Development, LLC · Phase 1, Interventional, and Treatment

Phase
Phase 1
Study type
Interventional
Enrollment
72
Allocation
Randomized
Ages
55 Years to 75 Years
Sex
All
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Study summary

The purpose of this study is to assess the safety and tolerability of JNJ-63733657 following single ascending intravenous (IV) dose administration in healthy subjects (Part 1) and multiple ascending IV dose administrations in subjects with prodromal or mild Alzheimer's disease (AD) (Part 2).

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Conditions studied

  • Alzheimer Disease

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03

Who can participate

Ages eligible
55 Years to 75 Years
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

General Inclusion Criteria:

  • Body mass index (BMI) between 18 and 35 kilogram per meter square (kg/m\^2), inclusive (BMI = weight/height\^2) and body weight greater than 40 kilogram (kg) but less than 110 kg at screening
  • Women must not be of childbearing potential

Specific Inclusion Criteria Part 2:

Each potential subject enrolled in Part 2 must satisfy all of the following specific criteria in addition to the general criteria to be enrolled in the study:

  • Clinical Dementia Rating Scale (CDR) global rating score of 0.5 or 1.0 at screening
  • Must have a reliable informant (example, relative, partner, friend)
  • Must have cerebrospinal fluid (CSF) finding consistent with Alzheimer's disease (AD) pathology

Exclusion criteria

Exclusion Criteria:

General Exclusion Criteria

Any potential subject who meets any of the following criteria will be excluded from participating in the study:

  • History of or current liver or renal insufficiency; significant cardiac, vascular, pulmonary, gastrointestinal, endocrine, neurologic (including but not limited to neurodegenerative disease (excluding AD for Part 2) [example, Parkinson's disease], seizure disorders, transient ischemic attacks, etc.), hematologic (including coagulation disorders), rheumatologic, psychiatric, or metabolic disturbances, any inflammatory illness or any other illness that the Investigator considers should exclude the subject
  • Relevant history of or current neurological disease (other than prodromal AD or mild AD for Part 2), which in the opinion of the investigator may make interpretation of possible new neurological signs or symptoms difficult
  • History of human immunodeficiency virus (HIV) antibody positive, or tests positive for HIV at Screening (per screening evaluations)
  • History of hepatitis B surface antigen (HBsAg) or hepatitis C antibody (anti-Hepatitis C virus [HCV]) positive, or other clinically active liver disease, or tests positive for HBsAg or anti-HCV at screening (per screening evaluations)

Specific Exclusion Criteria Part 1 - Mini-Mental State Examination (MMSE) score less than or equal to (\<=) 27 at screening

Specific Exclusion Criteria Part 2

  • Evidence of brain disease, other than AD, that could explain the cognitive deficit (including, but not limited to, vascular encephalopathy or strokes, as imaged by cerebral Magnetic resonance imaging (MRI)
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Study design

Phase
Phase 1
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Sequential assignment
Masking
Double (Participant, Investigator)
Enrollment
72 participants (actual)

Study arms

  • Experimental
    SAD (Part 1): Healthy Subjects

    In Part 1, single ascending intravenous (IV) doses of JNJ-63733657 or placebo will be administered to sequential cohorts (Cohorts 1 to 5) of healthy subjects on Day 1. The progression to the next (higher) dose level is dependent on acceptable safety and tolerability profile of JNJ-63733657 obtained after dose administration of the current dose level. Here, SAD indicates single ascending dose.

    Drug: JNJ-63733657 · Drug: Placebo

  • Experimental
    MAD (Part 2): Subjects With Alzheimer's Disease (AD)

    In Part 2, multiple ascending IV doses of JNJ-63733657 or placebo will be evaluated at three dose levels in sequential cohorts in subjects with prodromal or mild AD; 3 doses will be administered over a period of 8 weeks (Day 1, Day 29, Day 57). The starting dose will be decided based on the data from Part 1. Escalations will be done based on safety and tolerability similar to Part 1. Doses will not exceed those tested in Part 1. Here, MAD indicates multiple ascending dose.

    Drug: JNJ-63733657 · Drug: Placebo

Interventions

  • DrugJNJ-63733657

    Subjects will receive single (Part 1) or multiple (Part 2) ascending dose levels of JNJ-63733657 intravenously.

  • DrugPlacebo

    Subjects will receive matching placebo intravenously.

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What researchers measure

Primary outcomes

  1. Single Ascending Dose (SAD) (Part 1): Number of Subjects With Adverse Events as a Measure of Safety and Tolerability of JNJ-63733657

    An adverse event is any untoward medical event that occurs in a subject administered an investigational product, and it does not necessarily indicate only events with clear causal relationship with the relevant investigational product.

    Time frame: Up to Day 106

  2. Multiple Ascending Dose (MAD) (Part 2): Number of Subjects With Adverse Events as a Measure of Safety and Tolerability of JNJ-63733657

    An adverse event is any untoward medical event that occurs in a subject administered an investigational product, and it does not necessarily indicate only events with clear causal relationship with the relevant investigational product.

    Time frame: Up to Day 162

Secondary outcomes

  1. SAD (Part 1) and MAD (Part 2): Maximum Observed Serum Concentration (Cmax) of JNJ-63733657

    The Cmax is the maximum observed serum concentration of drug JNJ-63733657.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  2. SAD (Part 1) and MAD (Part 2): Time to Reach Maximum Observed Serum Concentration (Tmax) of JNJ-63733657

    Tmax is defined as time to reach the maximum observed serum JNJ-63733657 concentration.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  3. SAD (Part 1) and MAD (Part 2): Area Under the Serum Concentration-time Curve From Time Zero to Time of the Last Observed Quantifiable Concentration (AUC [0-Last]) of JNJ-63733657

    AUC (0-last) is defined as area under the serum JNJ-63733657 concentration-time curve from time 0 to time of the last observed quantifiable concentration.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  4. SAD (Part 1) and MAD (Part 2): Area Under the Serum Concentration-Time Curve From Time Zero to Infinite Time (AUC [0-infinity]) of JNJ-63733657

    AUC (0-infinity) is defined as area under the serum JNJ-63733657 concentration-time curve from time 0 to infinite time.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  5. MAD (Part 2): Area Under the Serum JNJ-63733657 Concentration-time Curve During a Dosing Interval (t) (AUC tau)

    AUC tau is defined as area under the serum JNJ-63733657 concentration-time curve during a dosing interval (tau).

    Time frame: Up to Day 85 (MAD)

  6. MAD (Part 2): Accumulation Ratio (R)

    R is obtained by dividing AUC of JNJ-63733657 at two different time points.

    Time frame: Up to Day 162 (MAD)

  7. SAD (Part 1) and MAD (Part 2): Total Systemic Clearance (CL) of JNJ-63733657

    CL is a quantitative measure of the rate at which JNJ-63733657 is removed from the body. The total systemic clearance after intravenous dose is estimated by dividing the total administered dose by the plasma Area Under the Serum Concentration-Time Curve From Time Zero to Infinite Time (AUC\[0-infinity\]).

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  8. SAD (Part 1) and MAD (Part 2): Volume of Distribution at Steady-State (Vss) of JNJ-63733657

    Vss is defined as the theoretical volume in which the total amount of drug would need to be uniformly distributed to produce the desired blood concentration of a drug. Steady state Vss is the apparent volume of distribution at steady-state which is estimated by (D/AUC\[0-infinity\])\*(AUMC\[0-infinity\])/AUC\[0-infinity\]) where D is the dose of study drug, AUMC(0-infinity) is the area under the first moment curve extrapolated to infinity and AUC(0-infinity) is the area under the serum concentration-time curve from time zero to infinite time.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  9. SAD (Part 1) and MAD (Part 2): Terminal Half-Life(t[1/2]) of JNJ-63733657

    t(1/2) is associated with the terminal slope (lambda \[z\]) of the semi-logarithmic drug concentration-time curve, calculated as 0.693/lambda(z).

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  10. SAD (Part 1) and MAD (Part 2): JNJ-63733657 Concentration in Cerebrospinal Fluid (CSF)

    CSF concentration assessment will be done to characterize the pharmacokinetics (PK) to estimate CSF concentration of JNJ-63733657.

    Time frame: Up to Day 57 (SAD) and up to Day 148 (MAD)

  11. SAD (Part 1) and MAD (Part 2): Number of Subjects With Anti-JNJ-6373365 Antibodies as a Measure of Immunogenicity

    Number of subjects with Anti-JNJ-63733657 antibodies will be evaluated in serum samples and potential CSF samples.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

  12. SAD (Part 1) and MAD (Part 2): Percent Change From Baseline in Total, Free, and Bound tau Biomarker Fragments in CSF

    Percent change from baseline in total, free, and bound tau (phosphorylation site) biomarker fragments in CSF will be evaluated to assess the effect of JNJ-63733657.

    Time frame: Up to Day 106 (SAD) and up to Day 162 (MAD)

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Study locations

7 sites
  • Clinical Pharmacology Unit
    Merksem, 2170, Belgium
  • Klinik für Neurodegenerative Erkrankungen und Gerontopsychiatrie
    Bonn, 53127, Germany
  • CTC North GmbH & Co. KG
    Hamburg, 20251, Germany
  • Universitätsklinikum des Saarlandes
    Homburg / Saar, 66421, Germany
  • Centre for Human Drug Research
    Leiden, 2333 CL, Netherlands
  • Hosp. Clinico San Carlos
    Madrid, 28040, Spain
  • Hosp. Univ. I Politecni La Fe
    Valencia, 46026, Spain
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Registry details

Key details

Study ID
NCT03375697
Lead sponsor
Janssen Research & Development, LLC
Responsible party
Sponsor
First posted
Dec 18, 2017
Start date
Dec 22, 2017
Primary completion
Dec 16, 2019
Completion
Dec 16, 2019
Last update
Apr 27, 2025

Study contacts

Janssen Research & Development, LLC Clinical Trial
study director · Janssen Research & Development, LLC

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
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