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CompletedNCT03336398Updated Mar 25, 2026Results posted

Investigation of the NMDA Antagonist Ketamine as a Treatment for Tinnitus

A Phase 2 interventional study of Ketamine Hydrochloride in saline in Tinnitus, sponsored by New York State Psychiatric Institute. Completed at 1 site in United States. Open to participants aged 21 Years to 60 Years. Per ClinicalTrials.gov, last updated 2026-03-25.

Sponsored by New York State Psychiatric Institute · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
42
Allocation
Not applicable
Ages
21 Years to 60 Years
Sex
All
01

Study summary

Tinnitus, or ringing in the ears, is a very common problem that often accompanies hearing loss. It affects up to 1 in 10 adults, and about 30% of people who experience chronic tinnitus find it very distressing. In these patients, symptoms of depression and anxiety often accompany tinnitus and there are no approved treatments. Clinical trials are ongoing to test a glutamate NMDA receptor antagonist (called esketamine), which is injected into the inner ear. However, the preliminary results with this medication show that it only works for tinnitus that results from acute injury. It does not treat tinnitus resulting from progressive hearing loss.

Research in humans and animals suggest that the neurotransmitters glutamate and GABA are important in the development and maintenance of tinnitus. This data shows that over-activation of the NMDA receptor and a decrease in GABA signaling in the brain play a crucial role. Previous studies show that ketamine, which an antagonist at the NMDA receptor, increases GABA levels in the brain in participants with depression. Thus, in this experiment, this study will test the effect of ketamine on tinnitus, since it blocks the NMDA glutamate receptor and increase GABA levels.

Two groups of participants will be included in this study: those who experience distress (symptoms of anxiety or depression) with tinnitus and those who have tinnitus but do not experience distress. Each participant will receive both ketamine and placebo on different days. Magnetic Resonance Spectroscopy (MRS) scans will be

Read the detailed description

Tinnitus has a prevalence of approximately 1 in 10 adults in the United States. Among those with tinnitus, 36% had nearly constant symptoms and almost 30% of those report that their tinnitus as a big or a very big problem. Currently there are few effective treatments for tinnitus, and no approved medications. Cognitive behavioral and retraining therapy provide some relief, but many patients fail to respond.

Animal research and human studies indicate that maladaptive plasticity plays a role in tinnitus, which involves glutamatergic signaling largely at the NMDA and AMPA receptors. Additionally, GABA signaling has been shown to be impaired in tinnitus. Rodent models show a diminished sensitivity to GABA signaling and human magnetic resonance spectroscopy (MRS) studies show decreased GABA levels in the auditory cortex.

Ketamine is a non-competitive NMDA receptor antagonist that has also been shown to activate AMPA receptors, and modulates ongoing plasticity. Additionally, ketamine activates a subpopulation of cortical GABAergic interneurons and projection neurons and increases GABA levels in the human brain, measured with MRS. Ketamine is FDA approved as an anesthetic, and recent work has demonstrated its efficacy in treating refractory depression and chronic pain. Importantly, these demonstrate that low dose ketamine, at doses lower than those required for anesthesia, are effective in lifting depressed mood and improving the sensation of chronic pain.

For many, tinnitus has an important affective component to it, with distress and co-morbid symptoms of depression and anxiety. The onset and severity of tinnitus can correlate with stressful events, and it has been posited that stress lowers the threshold of perception, and unmasks tinnitus. Tinnitus then triggers more anxiety and depressed mood, which in turn reinforces the symptoms. An advantage of ketamine may be its effect on depression and anxiety, in addition to tinnitus, to interrupt this cycle.

The goal of this study is to perform a proof-of-concept preliminary study of ketamine in tinnitus associated with sensori-neural hearing loss. This will be studied both in participants who report depressed mood and anxiety and those who do not. MRS imaging will be used to assess ketamine-induced changes in GABA in the auditory cortex.

02

Conditions studied

  • Tinnitus

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03

Who can participate

Ages eligible
21 Years to 60 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Participant aged 21-60
  • Tinnitus associated with at least mild sensori-neural hearing loss of at least 6 months duration
  • Score at least 32 on the Tinnitus Handicap Inventory and a score of 5dB or greater on the minimum masking level
  • Tinnitus not due to medical disease (other than sensorineural hearing loss)
  • Score of at least 14 on the Hamilton Depression Rating Scales with a score of at least 2 on the Hamilton Anxiety Rating Scale (in the distressed group).

Exclusion criteria

Exclusion Criteria:

  • DSM-V psychiatric disorders other than mild-moderate depression and anxiety, including substance use disorder.
  • History of recreational ketamine use, recreational PCP use,exposure to ketamine as an anesthetic, or an adverse reaction to ketamine
  • Currently taking psychotropic medication (e.g.antipsychotics, antidepressants, benzodiazepines)
  • Presence or positive history of significant medical or neurological illness, including high blood pressure (SBP >140, DBP > 90), cardiac illness, abnormality on EKG, head injury.
  • Pregnancy, abortion, or lack of effective birth control during 15 days before the scan
  • Metal implants, pacemaker, other metal (e.g. shrapnel or surgical prostheses) or paramagnetic objects contained within the
  • Medicinal patch that cannot be removed for the scans.
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
42 participants (actual)

Study arms

  • Experimental
    Tinnitus Patients

    Tinnitus patients with symptoms over 6 months duration. This group will receive both 0.5 mg/kg ketamine hydrochloride in saline and placebo, saline, with Magnetic Resonance Spectroscopy scans and audiometry testing and scales.

    Drug: Ketamine Hydrochloride in saline

Interventions

  • DrugKetamine Hydrochloride in saline

    0.5 mg/kg IV of ketamine hydrochloride in saline will be administered with one of the MRS Scan

    Also known as: Ketamine HCI

05

What researchers measure

Primary outcomes

  1. GABA and Glutamate (Glx) Levels in the Auditory Cortex Derived From 3T Magnetic Resonance Spectroscopy

    The GABA and Glutamate/Glutamine (Glx) peaks will be quantified as ratios (relative to water) and are obtained from the auditory cortex using 3T Magnetic Resonance Spectroscopy (MRS). Brain spectra containing GABA and Glutamate/Glutamine (Glx) resonances will be acquired of the auditory cortex using the volume-selective PRESS J-editing difference method. Data will be acquired from a voxel centered on Heschl's sulcus. The GABA and Glx peak areas will be quantified as ratios relative to the area of the unsuppressed voxel tissue water. The primary outcomes are GABA and GLX levels (relative to water) as they are obtained over time in frames reported as least squares mean with standard error. The first two frames serve as baseline measures, while frames 3 through 8 occur after the infusion over 40 minutes. This will be reported for saline and ketamine scans. An increase in GABA/water may correlate with tinnitus improvement, based on previous MRS studies showing low GABA/water in tinnitus.

    Time frame: GABA and GLX are binned into frames before and after the infusion. The pre-infusion frames (1 and 2) include about 12 minutes of data. The post-infusion frames occur over 40 minutes following the delivery of ketamine/saline (frames 3 through 8).

06

Results

Posted Mar 25, 2026

Participant flow

Participants recruited by advertisements and word of mouth.

Participant flow — Overall Study
MilestoneParticipants With Tinnitus
Started42
Participants receiving ketamine39
Participants receiving saline41
Completed39
Not completed3

Outcome measures

PrimaryGABA and Glutamate (Glx) Levels in the Auditory Cortex Derived From 3T Magnetic Resonance Spectroscopy

The GABA and Glutamate/Glutamine (Glx) peaks will be quantified as ratios (relative to water) and are obtained from the auditory cortex using 3T Magnetic Resonance Spectroscopy (MRS). Brain spectra containing GABA and Glutamate/Glutamine (Glx) resonances will be acquired of the auditory cortex using the volume-selective PRESS J-editing difference method. Data will be acquired from a voxel centered on Heschl's sulcus. The GABA and Glx peak areas will be quantified as ratios relative to the area of the unsuppressed voxel tissue water. The primary outcomes are GABA and GLX levels (relative to water) as they are obtained over time in frames reported as least squares mean with standard error. The first two frames serve as baseline measures, while frames 3 through 8 occur after the infusion over 40 minutes. This will be reported for saline and ketamine scans. An increase in GABA/water may correlate with tinnitus improvement, based on previous MRS studies showing low GABA/water in tinnitus.

Time frame:
GABA and GLX are binned into frames before and after the infusion. The pre-infusion frames (1 and 2) include about 12 minutes of data. The post-infusion frames occur over 40 minutes following the delivery of ketamine/saline (frames 3 through 8).
Reported as:
Mean · Ratio
GABA and Glutamate (Glx) Levels in the Auditory Cortex Derived From 3T Magnetic Resonance Spectroscopy
RatioTinnitus Patients
Saline scan GABA frame 12.11 ± 0.19
Saline scan GABA frame 22.12 ± 0.22
Saline scan GABA frame 32.09 ± 0.21
Saline scan GABA frame 42.03 ± 0.16
Saline scan GABA frame 52.05 ± 0.19
Saline scan GABA frame 62.07 ± 0.26
Saline scan GABA frame 72.10 ± 0.23
Saline scan GABA frame 82.05 ± 0.2
ketamine scan GABA frame 12.14 ± 0.21
ketamine scan GABA frame 22.11 ± 0.21
ketamine scan GABA frame 32.07 ± 0.19
ketamine scan GABA frame 42.05 ± 0.19
ketamine scan GABA frame 52.12 ± 0.25
ketamine scan GABA frame 62.15 ± 0.24
ketamine scan GABA frame 72.13 ± 0.19
ketamine scan GABA frame 82.11 ± 0.22
Saline scan GLX frame 111.92 ± 1.01
Saline scan GLX frame 211.84 ± 1.09
Saline scan GLX frame 311.83 ± 1.38
Saline scan GLX frame 411.84 ± 1.34
Saline scan GLX frame 511.84 ± 1.34
Saline scan GLX frame 611.91 ± 1.28
Saline scan GLX frame 711.80 ± 1.38
Saline scan GLX frame 811.77 ± 1.55
ketamine scan GLX frame 111.90 ± 0.79
ketamine scan GLX frame 211.78 ± 0.87
ketamine scan GLX frame 311.72 ± 0.84
ketamine scan GLX frame 411.83 ± 1.09
ketamine scan GLX frame 511.83 ± 1.28
ketamine scan GLX frame 611.58 ± 1.40
ketamine scan GLX frame 711.56 ± 1.47
ketamine scan GLX frame 811.53 ± 1.35
Statistical analysis
  • Tinnitus Patients · Mixed Models Analysis · p = 0.05

Adverse events

Collected over Duration of study (2-4 weeks). Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Tinnitus Patients Ketamine Scan Day0/42 (0%)0/42 (0%)3/42 (7.1%)
Tinnitus Patients Saline Scan Day0/42 (0%)0/42 (0%)1/42 (2.4%)
Most frequent other events
Most frequent other events
EventTinnitus Patients Ketamine Scan DayTinnitus Patients Saline Scan Day
dizzinessNervous system disorders3/421/42

Baseline characteristics

Age, Continuous
Age, Continuous(years)Participants With Tinnitus
Mean43 ± 12
Sex: Female, Male
Sex: Female, Male(Participants)Participants With Tinnitus
Female18
Male24
Race (NIH/OMB)
Race (NIH/OMB)(Participants)Participants With Tinnitus
American Indian or Alaska Native1
Asian4
Native Hawaiian or Other Pacific Islander0
Black or African American4
White30
More than one race2
Unknown or Not Reported1
07

Study locations

1 site
  • 1051 Riverside Drive
    New York, New York 10032, United States
08

References and documents

Study documents

  • Protocol and statistical analysis plan · Mar 4, 2025

Documents are hosted by the registry — open the source record to download them.

09

Registry details

Key details

Study ID
NCT03336398
Lead sponsor
New York State Psychiatric Institute
Responsible party
Diana Martinez (Medical Doctor, New York State Psychiatric Institute) — Principal investigator
First posted
Nov 8, 2017
Start date
Sep 1, 2019
Primary completion
Jun 17, 2023
Completion
Jul 1, 2024
Results posted
Mar 25, 2026
Last update
Mar 25, 2026

Study contacts

Diana Martinez
principal investigator · NYSPI/Columbia University

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
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