CClinicalTrials.gg
CompletedNCT03287869Updated Aug 17, 2020Results posted

A Trial to Evaluate the Safety and Tolerability of Brexpiprazole in the Treatment of Participants With Bipolar I Disorder.

A Phase 3 interventional study of Brexpiprazole in Bipolar I Disorder and Acute Mania, sponsored by Otsuka Pharmaceutical Development & Commercialization, Inc.. Completed at 73 sites in 6 countries. Open to participants aged 18 Years to 65 Years. Per ClinicalTrials.gov, last updated 2020-08-17.

Sponsored by Otsuka Pharmaceutical Development & Commercialization, Inc. · Phase 3, Interventional, and Treatment

Phase
Phase 3
Study type
Interventional
Enrollment
381
Ages
18 Years to 65 Years
Sex
All
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Study summary

This study evaluated the safety and evaluate the safety and tolerability of open-label brexpiprazole (2 - 4 mg/day, with a starting dose of 2 mg/day) for the treatment of adult subjects with bipolar I disorder. All participants received a starting dose of brexpiprazole.

Read the detailed description

While the availability of atypical antipsychotics had increased the therapeutic options available, there remains a need for safer and more effective therapies in the treatment of manic and depressive episodes of bipolar I disorder. Brexpiprazole's specific receptor activity profile likely correlates with its established efficacy in schizophrenia and major depressive disorder, and may prove to be an effective target for the treatment of acute mania of bipolar I disorder.

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Conditions studied

  • Bipolar I Disorder
  • Acute Mania

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Keywords

  • Bipolar
  • Mania
  • Brexpiprazole
03

Who can participate

Ages eligible
18 Years to 65 Years
Sexes eligible
All
Accepts healthy volunteers
No

Eligibility criteria

Inclusion Criteria (rollover participants from 331-201-00080 \& 331-201-00081 trials)

  • Participants remaining in hospital at the Day 21 visit of trial 331-201-00080 or 331-201-00081 were permitted to enroll in the 331-201-00083 trial at the week 3 visit of the double-blind trial if they were planned to be discharged from the hospital before the week 1 visit of trial 331-201-0083. Participants not discharged by the week 1 visit of trial 331-201-0083 were withdrawn.
  • Participants who, in the opinion of the investigator, could potentially benefit from administration of oral brexpiprazole for the treatment of bipolar I disorder and who completed 3 weeks of post-randomization treatment in Trial 331-201-00080 \& Trial 331-201-00081.

Exclusion Criteria (rollover participants from 331-201-00080 \& 331-201-00081 trials)

  • Participants with a major protocol violation during the course of their participation in the double-blind phase 3 trials (331-201-00080 or 331-201-00081).
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Study design

Phase
Phase 3
Primary purpose
Treatment
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
381 participants (actual)

Study arms

  • Experimental
    Brexpiprazole

    Brexpiprazole was administered in participants orally with flexible dosing from 2 mg/day from Days 1 to 3 regardless of treatment assignment in the previous double-blind trial, followed by titration to 3 mg/day on Day 4. Participants may have been titrated (or re-titrated) to a higher dose of brexpiprazole, up to a maximum of 4 mg/day, based on treatment response and at the investigator's discretion anytime at Day 7 or thereafter. Participants who were unable to tolerate their current dose could have been titrated down to a minimum of 2 mg/day any time after Day 4.

    Drug: Brexpiprazole

Interventions

  • DrugBrexpiprazole

    Brexpiprazole tablets

    Also known as: OPC-34712

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What researchers measure

Primary outcomes

  1. Number of Participants With at Least One Treatment Emergent Adverse Event (TEAE) by Severity

    An adverse event (AE) was defined as any untoward medical occurrence in a clinical investigation participant administered a drug; it does not necessarily have to have a causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (eg, a clinically significant abnormal laboratory finding), symptom, or disease temporally associated with the use of a drug, whether or not it is considered related to the drug. A TEAE is defined as an adverse event with an onset that occurs after receiving study drug. AEs severity were graded on a 3-point scale as: 1 = mild; discomfort noticed, but no disruption to daily activity, 2 = moderate; discomfort sufficient to reduce or affect normal daily activity, and 3 = severe; inability to work or perform normal daily activity.

    Time frame: From Day 1 (after dosing) through 29 weeks (26 weeks treatment, 3 weeks safety follow-up)

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Results

Posted Aug 17, 2020
Limitations and caveats
As predefined in the protocol, there were no primary or secondary efficacy endpoints in this trial.

Participant flow

Participant flow — Overall Study
MilestonePrior BrexpiprazolePrior Placebo
Started188193
Analyzed for safety (safety sample)184184
Completed105100
Not completed8393
Withdrew: Adverse event1412
Withdrew: Lack of efficacy10
Withdrew: Lost to follow-up1319
Withdrew: Non-compliance with study drug59
Withdrew: Progressive disease10
Withdrew: Protocol deviation21
Withdrew: Withdrawal by subject3643
Withdrew: Early closure of the site01
Withdrew: Physician decision55
Withdrew: Reason not specified63

Outcome measures

PrimaryNumber of Participants With at Least One Treatment Emergent Adverse Event (TEAE) by Severity

An adverse event (AE) was defined as any untoward medical occurrence in a clinical investigation participant administered a drug; it does not necessarily have to have a causal relationship with this treatment. An AE can therefore be any unfavorable and unintended sign (eg, a clinically significant abnormal laboratory finding), symptom, or disease temporally associated with the use of a drug, whether or not it is considered related to the drug. A TEAE is defined as an adverse event with an onset that occurs after receiving study drug. AEs severity were graded on a 3-point scale as: 1 = mild; discomfort noticed, but no disruption to daily activity, 2 = moderate; discomfort sufficient to reduce or affect normal daily activity, and 3 = severe; inability to work or perform normal daily activity.

Time frame:
From Day 1 (after dosing) through 29 weeks (26 weeks treatment, 3 weeks safety follow-up)
Reported as:
Count of participants · Participants
Number of Participants With at Least One Treatment Emergent Adverse Event (TEAE) by Severity
ParticipantsPrior BrexpiprazolePrior Placebo
TEAE, Any grade7986
TEAE, Mild6068
TEAE, Moderate3129
TEAE, Severe85

Adverse events

Collected over From Day 1 (after dosing) through 29 weeks (26 weeks treatment, 3 weeks safety follow-up). Non-serious events are listed at a 5% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Prior Brexpiprazole0/184 (0%)11/184 (6%)13/184 (7.1%)
Prior Placebo0/184 (0%)8/184 (4.3%)26/184 (14.1%)
Most frequent serious events
Showing 10 of 11
Most frequent serious events
EventPrior BrexpiprazolePrior Placebo
ManiaPsychiatric disorders5/1841/184
DepressionPsychiatric disorders3/1842/184
Acute Myocardial InfarctionCardiac disorders0/1841/184
Vertigo PositionalEar and labyrinth disorders0/1841/184
Upper Gastrointestinal HaemorrhageGastrointestinal disorders1/1840/184
Chest PainGeneral disorders0/1841/184
CellulitisInfections and infestations1/1840/184
MigraineNervous system disorders0/1841/184
Bipolar DisorderPsychiatric disorders0/1841/184
Suicidal BehaviourPsychiatric disorders1/1840/184
Most frequent other events
Most frequent other events
EventPrior BrexpiprazolePrior Placebo
AkathisiaNervous system disorders8/18417/184
HeadacheNervous system disorders5/18410/184

Baseline characteristics

Enrolled Sample included all participants who signed an inform consent form (ICF) for the trial.

Age, Continuous
Age, Continuous(years)Prior BrexpiprazolePrior PlaceboTotal
Mean45.6 ± 11.046.1 ± 11.545.8 ± 11.2
Sex: Female, Male
Sex: Female, Male(Participants)Prior BrexpiprazolePrior PlaceboTotal
Female9792189
Male91101192
Race/Ethnicity, Customized
Race/Ethnicity, Customized(Participants)Prior BrexpiprazolePrior PlaceboTotal
Race — White129146275
Race — Black or African American524799
Race — American Indian or Alaska Native303
Race — Asian202
Race — Race-Other202
Race/Ethnicity, Customized
Race/Ethnicity, Customized(Participants)Prior BrexpiprazolePrior PlaceboTotal
Ethnicity — Hispanic or Latino212445
Ethnicity — Not Hispanic or Latino165169334
Ethnicity — Ethnicity-Other202
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Study locations

73 sites
  • Woodland International Research Group
    Little Rock, Arkansas 72211, United States
  • Woodland Research Northwest, LLC
    Rogers, Arkansas 72758, United States
  • Citrials Inc.
    Bellflower, California 90706, United States
  • Radiant Research
    Cerritos, California 90703, United States
  • ProScience Research Group
    Culver City, California 90230, United States
  • Collaborative Neuroscience Network, LLC
    Garden Grove, California 92845, United States
  • Behavioral Research Specialists, LLC
    Glendale, California 91206, United States
  • Apostle Clinical Trials
    Long Beach, California 90813, United States
  • Pacific Research Partners, LLC
    Oakland, California 94607, United States
  • NRC Research Institute
    Orange, California 92868, United States
  • Asclepes Research Centers, PC
    Panorama City, California 91402, United States
  • CI Trials
    Riverside, California 92705, United States
  • CNRI-San Diego
    San Diego, California 92102, United States
  • Artemis Institute for Clinical Research
    San Diego, California 92103, United States
  • Sharp Mesa Vista Hospital
    San Diego, California 92123, United States
  • CI Trials
    Santa Ana, California 92705, United States
  • Collaborative Neuroscience Network, LLC
    Torrance, California 90502, United States
  • Shreenath Clinical Service
    Yorba Linda, California 92886, United States
  • Optimus U Corp
    Coral Gables, Florida 33134, United States
  • Segal Trials
    Fort Lauderdale, Florida 33308, United States
  • Galiz Research
    Hialeah, Florida 33016, United States
  • Research Centers of America, LLC
    Hollywood, Florida 33024, United States
  • Florida Behavioral Medicine
    Largo, Florida 33770, United States
  • University of South Florida Board of Trustees
    Tampa, Florida 33613, United States
  • iResearch Atlanta, LLC
    Decatur, Georgia 30030, United States
  • Alexian Brothers Center for Psychiatric Research
    Hoffman Estates, Illinois 60169, United States
  • NeuroPsychiatric Research
    Winfield, Illinois 60190, United States
  • Louisiana Clinical Research
    Shreveport, Louisiana 71101, United States
  • CBH Health
    Gaithersburg, Maryland 20877, United States
  • St. Charles Psychiatric Associates
    Saint Charles, Missouri 63304, United States
  • Arch Clinical Trials, LLC
    Saint Louis, Missouri 63118, United States
  • St. Louis Clinical Trials
    Saint Louis, Missouri 63141, United States
  • Hassman Research Institute, LLC
    Berlin, New Jersey 08009, United States
  • Clinical Trials of America-NC, LLC
    Hickory, North Carolina 28601, United States
  • Richard H Weisler, MD PA Associates
    Raleigh, North Carolina 27609, United States
  • SP Research PLLC
    Oklahoma City, Oklahoma 73112, United States
  • Cutting Edge Research Group
    Oklahoma City, Oklahoma 73116, United States
  • Community Clinical Research, Inc.
    Austin, Texas 78754, United States
  • InSite Clinical Research
    DeSoto, Texas 75115, United States
  • North Texas Clinical Trials
    Fort Worth, Texas 76104, United States
  • Pillar Clinical Research LLC
    Garland, Texas 75042, United States
  • Pillar Clinical Research, LLC
    Richardson, Texas 75080, United States
  • Core Clinical Research
    Everett, Washington 98201, United States
  • Mid Columbia Research
    Richland, Washington 99352, United States
  • Mental Health Center Prof. Dr. Ivan Temkov - Burgas EOOD, Department for Treatment of Emergency Psychiatric Condition
    Burgas, 8000, Bulgaria
  • State Psychiatry Hospital - Kardzhali,Third Male Department, First Female Department
    Kardzhali, 6600, Bulgaria
  • State Psychiatry Hospital Sv. Ivan Rilski, First Male department, First Female Department
    Novi Iskar, 1282, Bulgaria
  • University Multiprofile Hospital for Active Treatment Sveti Georgi EAD, Clinic of Psychiatry
    Plovdiv, 4002, Bulgaria
  • "Mental Health Centre-Ruse" EOOD, Male department for persons with severe mental disorders, Female department for persons with severe mental disorders
    Ruse, 7003, Bulgaria
  • University Multiprofile Hospital for Active Treatment -Alexandrovska EAD, Clinic of Psychiatry, First Department of Psychiatry
    Sofia, 1431, Bulgaria
  • Multiprofile Hospital for Active Treatment - Targovishte AD, Department of Psychiatry
    Targovishte, 7700, Bulgaria
  • Mental Health Center - Veliko Tarnovo EOOD, Department of Psychiatry for Active Treatment of Persons with Severe Mental Disorders
    Veliko Tarnovo, 5000, Bulgaria
  • Mental Health Center - Vratsa EOOD, Department of Psychiatry
    Vratsa, 3000, Bulgaria
  • CHC Rijeka-Clinic for Psychiatrics
    Rijeka, 51000, Croatia
  • Poliklinika Neuron /Polyclinic Neuron
    Zagreb, 10000, Croatia
  • Indywidualna Specjalistyczna Praktyka Lekarska Wieslaw Jerzy Cubala
    Gdańsk, 80-438, Poland
  • NZOZ Prywatna Klinika Psychiatryczna Inventiva
    Tuszyn, 95-080, Poland
  • CHC Dr Dragisa Misovic
    Belgrade, 11000, Serbia
  • Clinic for Psychiatric Disorders, Dr Laza Lazarevic
    Belgrade, 11000, Serbia
  • Clinic for Psychiatry
    Belgrade, 11000, Serbia
  • Specialized Hospital for Psychiatry Diseases Kovin
    Kovin, 26220, Serbia
  • Clinical Center Kragujevac, Clinic of Psychiatry
    Kragujevac, 34000, Serbia
  • Klinika za psihijariju, Klinicki Centar Vojvodine
    Novi Sad, 21000, Serbia
  • Regional Clinical Hospital n.a I.I. Mechnicov
    Dnipro, 49005, Ukraine
  • SI of Neurology Psychiatry and Narcology NAMS
    Kharkiv, 61068, Ukraine
  • Kherson Regional Psychiatric Hospital
    Kherson, 73488, Ukraine
  • Kyiv Regional Medical Incorporation Psychiatry
    Kyiv, 04080, Ukraine
  • CI of LOR Lviv Regional Clinical Psychiatric Hospital, Department #25
    Lviv, 79021, Ukraine
  • Communal Institution of Lviv Regional Council "Lviv Regional Clinical Psychiatric Hospital", department #20
    Lviv, 79021, Ukraine
  • Odesa Regional Psychiatric Hospital 2
    Odesa, 67513, Ukraine
  • Maltsev Regional Clinical Psychiatric Hospital
    Poltava, 36013, Ukraine
  • Ternopil Regional Municipal Clinical Psychoneurological Hospital
    Ternopil', 46027, Ukraine
  • O.I. Yushenko Vinnitsa Regional Clinic
    Vinnitsa, 21018, Ukraine
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References and documents

Study documents

  • Study protocol · Oct 23, 2017
  • Statistical analysis plan · Jul 17, 2019

Documents are hosted by the registry — open the source record to download them.

Individual participant data

Plan to share: Yes — Anonymized Individual participant data (IPD) that underlie the results of this study will be shared with researchers to achieve aims pre-specified in a methodologically sound research proposal. Small studies with less than 25 participants are excluded from data sharing.

Supporting information: Study protocol, Sap, Csr

09

Registry details

Key details

Study ID
NCT03287869
Lead sponsor
Otsuka Pharmaceutical Development & Commercialization, Inc.
Collaborators
H. Lundbeck A/S
Responsible party
Sponsor
First posted
Sep 19, 2017
Start date
Oct 24, 2017
Primary completion
Jul 31, 2019
Completion
Jul 31, 2019
Results posted
Aug 17, 2020
Last update
Aug 17, 2020

Oversight

FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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This study is completed, as verified in Aug 2020. You cannot join it, but the record below documents what was studied.

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