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CompletedNCT03194178ADOROBINUpdated May 6, 2025

Impact of Phonatory and Facial Morphology Disorders, on the Quality of Life of Adolescents With Pierre Robin Sequence

An observational study in Pierre Robin Syndrome, sponsored by Imagine Institute. Completed at 1 site in France. Open to participants aged 12 Years to 18 Years. Per ClinicalTrials.gov, last updated 2025-05-06.

Sponsored by Imagine Institute · Observational

Study type
Observational
Model
Case-only
Time perspective
Prospective
Enrollment
100
Ages
12 Years to 18 Years
Sex
All
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Study summary

The study team has made the hypothesis that the intensity of the phonatory disorders (rhinolalia), and of the maxillo-mandibular growth anomalies (facial morphology), may have negative effects on the quality of life of adolescents with Pierre Robin sequence.

The investigators also want to assess the impact of 2 different surgical protocols of closure of the cleft palate (1 or 2 step(s)), on the current phonatory and morphology aspects. These 2 protocols were performed, by 2 parisian clinical teams, that have now been merged at Necker hospital.

Read the detailed description

In this protocol, the investigator will include patients who were treated, via maxillo-facial surgery, in their early childhood for a Pierre Robin sequence.

In the frame of a follow-up visit, if they accept to participate in the study, they will fulfill with 2 psychologists, 3 quality of life questionnaires, and 1 depression assessment questionnaire.

This will aim at evaluate their quality of life and their social integration, at the time of adolescence.

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Conditions studied

  • Pierre Robin Syndrome
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Who can participate

Ages eligible
12 Years to 18 Years
Sexes eligible
All
Accepts healthy volunteers
No
Sampling method
Non-probability sample

Study population

Patient included will be patients affected with Pierre Robin sequence, and coming at the study reference center in the frame of a routine follow-up visit.

Inclusion criteria

  • Having a Pierre Robin sequence, either isolated, either integrated to a collagenopathy, or associated to any other malformation, but without any mental retardation
  • Being schooled in normal environment, with a maximum of 2 years of academic delay
  • Having being treated, in the early childhood, for a maxillo-facial surgery, either in Paris-Necker or Paris-Trousseau hospitals (1 or 2 step(s) protocols)

Exclusion criteria

Exclusion Criteria:

  • Having any other form of Pierre Robin sequence (syndromic or associated to a mental retardation)
  • Having more than 2 years of academic delay, or being schooled in a specialized environment
  • Having an organic severe intercurrent disease, that could have an impact on the quality of life of the patients.
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Study design

Observational model
Case-only
Time perspective
Prospective
Enrollment
100 participants (estimated)
Patient registry
No

Groups and cohorts

  • Pierre Robin sequence patients

    Patients presenting a Pierre Robin sequence, and who have been cared in their early childhood by either the Necker or Trousseau hospitals teams, and who are between 12 and 18 years old at the beginning of the study.

    Other: Pierre Robin sequence patients

Interventions

  • OtherPierre Robin sequence patients

    4 questionnaires will be completed by the patient : * "Kidscreen 52" (generic quality of life questionnaire) * "Voice Handicap Index" : VHI-9i (specific quality of life questionnaire) * "Child Oral Health Impact Profile" : COHIP (specific quality of life questionnaire) * "MDI-C" (composite depression scale for minors)

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What researchers measure

Primary outcomes

  1. Correlation between generic and specific quality of life of the patients, scored via the questionnaires, and the severity of the troubles (facial and phonatory), assessed by the physicians

    The data obtained via the 4 quality of life questionnaires will be assessed on regards of the severity of the facial dysmorphy and phonatory disorders. The investigators will aggregate these results, and will be able to check if there is a clear correlation between them. They will be able to say if it can be concluded that the physical troubles due to the Pierre Robin sequence affect the quality of life of the patients.

    Time frame: 3 years

Secondary outcomes

  1. Comparison of the generic quality of life of patients with Pierre Robin sequence, scored via the "Kidscreen 52" questionnaire, with the data of the general population

    The investigator will assess the generic quality of life of the study patients, scored via the "Kidscreen 52" questionnaire, on regards of general population (data of the literature)

    Time frame: 3 years

  2. Comparison of the results of the 2 surgical protocols on the maxillo-mandibular growth

    The investigator will compare the long-term maxillo-mandibular growth of the "Pierre Robin" patients, compared to the general population, and compared between the 2 surgical protocols used.

    Time frame: 3 years

  3. Comparison of the results of the 2 surgical protocols on the phonatory aftereffects

    The investigator will compare the phonatory aftereffects of the "Pierre Robin" patients, compared to the general population, and compared between the 2 surgical protocols used.

    Time frame: 3 years

  4. Need of secondary surgery

    The investigators will assess the need to realize a secondary surgery, according the initial surgery protocol used.

    Time frame: 3 years

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Study locations

1 site
  • Necker - Enfants Malades hospital
    Paris, France
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References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

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Registry details

Key details

Study ID
NCT03194178
Lead sponsor
Imagine Institute
Responsible party
Sponsor
First posted
Jun 21, 2017
Start date
Jul 2016
Primary completion
Jul 2019
Completion
Jul 2019
Last update
May 6, 2025

Study contacts

Véronique Abadie, Pr
principal investigator · Necker - Enfants Malades Hospital

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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This study is completed, as verified in May 2025. You cannot join it, but the record below documents what was studied.

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