ClinicalTrials.gg
CompletedNCT03041038Updated Aug 25, 2021Results posted

The Efficacy and Safety of Secukinumab in Patients With Ichthyoses

A Phase 2 interventional study of Secukinumab and Placebo in Ichthyosis, Autosomal Recessive Congenital Ichthyosis and Lamellar Ichthyosis, sponsored by Northwestern University. Completed at 2 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2021-08-25.

Sponsored by Northwestern University · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
20
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The ichthyoses are a group of lifelong genetic disorders which share characteristics of generalized skin thickening, scaling and underlying cutaneous inflammation. There are no therapies based on growing understanding of what causes the disease. However, there have been recent discoveries of marked elevations in expression of interleukin-17A (IL-17A) and IL-17-related cytokines in the skin of individuals with ichthyosis, which may explain the inflammation. Investigators propose that IL-17-targeting therapeutics will safely suppress the inflammation and possibly the other features of ichthyosis, improving quality of life.

Read the detailed description

The ichthyoses are a group of lifelong genetic disorders which share characteristics of generalized skin thickening, scaling and underlying cutaneous inflammation. The vast majority are orphan disorders and are associated with extremely poor quality of life related to social ostracism from altered appearance, associated itchiness and discomfort, and functional limitations from the skin disease. Among the most common of these orphan disorders are autosomal recessive congenital ichthyosis (ARCI) with its phenotypic subsets of lamellar ichthyosis (ARCI-LI) and congenital ichthyosiform erythroderma (ARCI-CIE), epidermolytic ichthyosis (EI) and Netherton syndrome (NS). Therapy is time-consuming for patients or parents and is supportive, focusing on clearance of the scaling. There are no therapies based on growing understanding of what causes the disease. There have been recent discoveries of marked elevations in expression of interleukin-17A (IL-17A) and IL-17-related cytokines in the skin of individuals with ichthyosis, which may explain the inflammation. Psoriasis, another inflammatory skin disorder with redness and scaling, has now been shown to result from IL-17 pathway activation and IL-17A inhibition is the most effective therapy known to treat psoriasis. Investigators propose that IL-17-targeting therapeutics will safely suppress the inflammation and possibly the other features of ichthyosis, improving quality of life. In this long-term, open-label extension, Investigators propose to treat adults with ichthyosis and at least moderate erythema with subcutaneously administered anti-IL-17 antibody (secukinumab) and to serially assess clinical response to this therapy and its safety.

02

Conditions studied

  • Ichthyosis
  • Autosomal Recessive Congenital Ichthyosis
  • Lamellar Ichthyosis
  • Congenital Ichthyosiform Erythroderma
  • Epidermolytic Ichthyosis
  • Netherton Syndrome
03

In context

Ichthyosis

33 studies on the registry are indexed under Ichthyosis; 11 are open to participants now.

This study's enrollment of 20 is below the median of 26 across 23 interventional studies indexed under Ichthyosis.

Browse Ichthyosis studies →

Lead sponsor

Northwestern University is the lead sponsor of 1,423 studies on the registry; 198 are open to participants now.

Of its 105 completed or terminated interventional studies of FDA-regulated products, 78 (74%) have results posted.

Counted across the registry records on this site, refreshed daily.

04

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Go through the criteria one by one — yes, no or not sure — and take the list to your doctor or the study team. Kept in this browser only.

Inclusion criteria

  • Subject has provided
  • Subjects are at least 18 years of age or older at the time of screening
  • Female subjects must not be pregnant or breast-feeding
  • Female subjects of with a negative urine pregnancy test and using at least one form of (abstinence allowed)
  • Subjects must have a confirmed diagnosis of ARCI (divided phenotypically into ARCI-LI or ARCI-CIE), EI or NS (by genotype or willingness to be genotyped)
  • Subjects must be clinically judged to be immunocompetent.
  • Subjects will have no allergy to secukinumab or components of the product.
  • Subjects will have normal baseline laboratory testing (CMP, CBC, negative, , C negative, QuantiFERON®-TB gold negative)
  • Subjects must have an erythema score of at least 18 on IASI and an IASI-E score of 12 (at least moderate severity of erythema) at baseline

Exclusion criteria

Exclusion Criteria:

  • Subjects who are unable to give or assent.
  • Subjects without a confirmed diagnosis ARCI, EI, or NS.
  • Subjects who have a known allergy to secukinumab.
  • Female subjects who are pregnant, considering becoming pregnant, or will breastfeed.
  • Subjects who have prior biologic use targeting IL-17A/IL-17 receptor A or IL-12/IL-23 or who have prior use of TNF-alpha blockers.
  • Subjects who have used a systemic retinoid within one month prior to initiation.
  • Subjects who have used topical retinoids or keratolytics within one week prior to initiation.
  • Subjects who have used emollient on the area to be biopsied in the previous 24 hours
Terms in these criteria, in plain language(5)

Underlined terms in the criteria open these too. Explained by clinicaltrials.gg, not part of the registry record. The study team decides who can take part.

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Childbearing potential

Able to become pregnant: from the first period until menopause, unless permanently unable to through surgery (removal of the womb, or of both ovaries or both fallopian tubes).

Criteria for people of childbearing potential usually ask for a negative pregnancy test and for contraception during the study and for a time after it.

Contraception

Ways of preventing pregnancy. “Highly effective” methods fail less than 1% of the time a year when used correctly — for example an IUD or an implant.

Criteria usually say which methods count and how long to keep using them after the last dose, sometimes for male participants too. Some studies accept a partner’s vasectomy if it was confirmed successful and that person is the participant’s only sexual partner.

HIV

The human immunodeficiency virus, which weakens the immune system.

Many studies now accept people whose HIV is controlled on treatment, judged by the viral load and the CD4 count. Check the limits this study sets.

Hepatitis B tests

Hepatitis B is a virus that infects the liver. These are separate tests: HBsAg positive usually means a current infection (a recent vaccination can briefly cause it too); total anti-HBc (HBcAb) positive means an infection now or in the past; HBV DNA measures how much virus is in the blood.

Some studies accept a past infection if HBV DNA is undetectable, sometimes with antiviral medicine during the study. Check what this study allows.

05

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Crossover assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
20 participants (actual)

Study arms

  • Experimental
    Secukinumab

    Secukinumab 300mg (liquid formation) administered subcutaneously weekly for 5 weeks then monthly until end of trial

    Drug: Secukinumab

  • Placebo comparator
    Placebo

    Placebo (sterile saline) 2ml administered subcutaneously weekly for 5 weeks then monthly until end of trial

    Drug: Placebo

Interventions

  • Anti IL-17A antibody

    Also known as: Cosentyx

  • DrugPlacebo

    Also known as: Sterile Saline

06

What researchers measure

Primary outcomes

  1. Reduction at Week 16 in the Ichthyosis Area Severity Index (IASI)

    Primary Efficacy Endpoint. The IASI score was modelled after the Eczema Area and Severity Index (EASI) and Psoriasis Area and Severity Index (PASI), commonly used in clinical trials for atopic dermatitis and psoriasis, respectively. This scale measures erythema and scaling and has a range of 0-48 (sum of a max score of 24 for erythema and 24 for scaling). A higher score means worse clinical severity. Mean difference IASI total score at Baseline was compared to IASI total score at Week 16.

    Time frame: 16 Weeks

  2. Total Number of Bacterial or Fungal Mucocutaneous Infections Through Week 16

    Primary Safety Endpoint

    Time frame: 16 weeks of secukinumab/placebo double blind followed by 32 week open label treatment

07

Results

Posted Aug 25, 2021

Participant flow

Participant flow — Overall Study
MilestoneSecukinumabPlacebo
Started119
Week 16108
Week 3298
Completed57
Not completed62
Withdrew: Withdrawal by subject40
Withdrew: Lost to follow-up11
Withdrew: Protocol violation11

Outcome measures

PrimaryReduction at Week 16 in the Ichthyosis Area Severity Index (IASI)

Primary Efficacy Endpoint. The IASI score was modelled after the Eczema Area and Severity Index (EASI) and Psoriasis Area and Severity Index (PASI), commonly used in clinical trials for atopic dermatitis and psoriasis, respectively. This scale measures erythema and scaling and has a range of 0-48 (sum of a max score of 24 for erythema and 24 for scaling). A higher score means worse clinical severity. Mean difference IASI total score at Baseline was compared to IASI total score at Week 16.

Time frame:
16 Weeks
Reported as:
Mean · units on a scale
Reduction at Week 16 in the Ichthyosis Area Severity Index (IASI)
units on a scaleSecukinumabPlacebo
Reduction at Week 16 in the Ichthyosis Area Severity Index (IASI)2.4 (-7.8 to 12.7)4.3 (-6.5 to 15.1)
PrimaryTotal Number of Bacterial or Fungal Mucocutaneous Infections Through Week 16

Primary Safety Endpoint

Time frame:
16 weeks of secukinumab/placebo double blind followed by 32 week open label treatment
Reported as:
Number · infections
Total Number of Bacterial or Fungal Mucocutaneous Infections Through Week 16
infectionsSecukinumabPlaceboOpen Label
Total Number of Bacterial or Fungal Mucocutaneous Infections Through Week 165510

Adverse events

Collected over 56 weeks. Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Secukinumab0/11 (0%)1/11 (9.1%)3/11 (27.3%)
Placebo0/9 (0%)0/9 (0%)2/9 (22.2%)
Open Label0/18 (0%)1/18 (5.6%)6/18 (33.3%)
Most frequent serious events
Most frequent serious events
EventSecukinumabPlaceboOpen Label
Hospitalization-GERDGastrointestinal disorders1/110/91/18
Hospitalization-pyelonephritisInfections and infestations0/110/91/18
Most frequent other events
Most frequent other events
EventSecukinumabPlaceboOpen Label
Skin InfectionInfections and infestations0/110/93/18
Bronchial infectionInfections and infestations0/111/90/18
Upper Respiratory InfectionInfections and infestations1/111/91/18
Urinary tract infectionInfections and infestations0/111/92/18
ConjunctivitisInfections and infestations1/110/90/18
Flu-like symptomsInfections and infestations1/110/91/18
Otitis externa bacterialInfections and infestations0/110/91/18

Baseline characteristics

Age, Continuous
Age, Continuous(years)SecukinumabPlaceboTotal
Mean34.2 ± 11.735.5 ± 12.734.7 ± 12.9
Sex: Female, Male
Sex: Female, Male(Participants)SecukinumabPlaceboTotal
Female8412
Male358
Ethnicity (NIH/OMB)
Ethnicity (NIH/OMB)(Participants)SecukinumabPlaceboTotal
Hispanic or Latino112
Not Hispanic or Latino10818
Unknown or Not Reported000
Race (NIH/OMB)
Race (NIH/OMB)(Participants)SecukinumabPlaceboTotal
American Indian or Alaska Native000
Asian000
Native Hawaiian or Other Pacific Islander000
Black or African American101
White9817
More than one race000
Unknown or Not Reported112
Ichthyosis Subtype
Ichthyosis Subtype(Participants)SecukinumabPlaceboTotal
CIE325
EI224
LI426
NS235
Site
Site(Participants)SecukinumabPlaceboTotal
Mount Sinai426
Northwestern7714
Weight
Weight(kilograms)SecukinumabPlaceboTotal
Mean69.9 ± 13.575.5 ± 30.472.4 ± 22.0
Ichthyosis Area Severity Index (IASI)
Ichthyosis Area Severity Index (IASI)(units on a scale)SecukinumabPlaceboTotal
Mean33.7 ± 6.536.2 ± 4.734.8 ± 5.9
08

Study locations

2 sites
  • Department of Dermatology, Northwestern University Feinberg School of Medicine
    Chicago, Illinois 60611, United States
  • Department of Dermatology Icahn School of Medicine at Mount Sinai
    New York, New York 10029, United States
09

References and documents

Publications

  • Lefferdink R, Rangel SM, Chima M, Ibler E, Pavel AB, Kim H, Wu B, Abu-Zayed H, Wu J, Jackson K, Singer G, Choate KA, Guttman-Yassky E, Paller AS. Secukinumab responses vary across the spectrum of congenital ichthyosis in adults. Arch Dermatol Res. 2023 Mar;315(2):305-315. doi: 10.1007/s00403-022-02325-3. Epub 2022 Feb 26. PubMed 35218370 ↗

Study documents

PDFs hosted by the registry, ClinicalTrials.gov.

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Updates

Tracking since Sep 25, 2026
No changes since tracking began. The registry record was last updated on Aug 25, 2021, before this site started recording changes on Sep 25, 2026. Its history is on ClinicalTrials.gov ↗
11

Registry details

Key details

Study ID
NCT03041038
Responsible party
Amy Paller (Principal Investigator, Northwestern University) — Principal investigator
First posted
Feb 2, 2017
Start date
Dec 2016
Primary completion
Aug 31, 2020
Completion
Aug 31, 2020
Results posted
Aug 25, 2021
Last update
Aug 25, 2021

Study contacts

Amy Paller, MD
principal investigator · Northwestern University Department of Dermatology
Emma Guttman-Yassky, MD, PhD
principal investigator · Mt. Sinai Hospital Department of Dermatology

Oversight

Data monitoring committee
Yes
View the source record on ClinicalTrials.gov ↗

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