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CompletedNCT02356289Updated Sep 23, 2015

Single Ascending Dose Study of MYK-461 in Healthy Volunteers

A Phase 1 interventional study of Placebo and MYK-461 in Healthy, sponsored by MyoKardia, Inc.. Completed at 1 site in United Kingdom. Open to participants aged 18 Years to 55 Years, including healthy volunteers. Per ClinicalTrials.gov, last updated 2015-09-23.

Sponsored by MyoKardia, Inc. · Phase 1, Interventional, and Treatment

Phase
Phase 1
Study type
Interventional
Enrollment
48
Allocation
Randomized
Ages
18 Years to 55 Years
Sex
All
01

Study summary

The purpose of this study is to establish initial safety, tolerability, pharmacokinetics and pharmacodynamics of MYK-461 in human subjects. This is a randomized, double-blind, placebo-controlled, sequential group, single ascending (oral) dose study in healthy volunteers aged 18-55 years.

02

Conditions studied

  • Healthy

Keywords

  • Hypertrophic Cardiomyopathy
03

Who can participate

Ages eligible
18 Years to 55 Years
Sexes eligible
All
Accepts healthy volunteers
Yes

Inclusion criteria

  • Normal body mass index (BMI)
  • Normal LVEF
  • Normal electrocardiogram (ECG)
  • Females must not be breastfeeding and must be permanently sterilized or are postmenopausal.

Exclusion criteria

Exclusion Criteria:

  • Any structural abnormalities on echocardiography
  • Positive results of HIV test and/or seropositive for HCV or HBV.
04

Study design

Phase
Phase 1
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Triple (Participant, Care provider, Investigator)
Enrollment
48 participants (actual)

Study arms

  • Experimental
    MYK-461

    single-dose, tablet formulation

    Drug: MYK-461

  • Placebo comparator
    Placebo

    single-dose, tablet formulation

    Drug: Placebo

Interventions

  • DrugPlacebo
  • DrugMYK-461
05

What researchers measure

Primary outcomes

  1. Safety: Incidence of adverse events

    Time frame: 28 Days

Secondary outcomes

  1. Determination of pharmacokinetics parameters

    maximum concentration (Cmax)

    Time frame: 28 Days

  2. Determination of pharmacokinetics parameters

    time of the maximum measured concentration (Tmax)

    Time frame: 28 Days

  3. Determination of pharmacokinetics parameters

    area under the concentrationtime curve (AUC)

    Time frame: 28 Days

  4. Determination of pharmacokinetics parameters

    half-life (t1/2)

    Time frame: 28 Days

06

Study locations

1 site
  • Quintles LTD
    London, United Kingdom
07

Registry details

Key details

Study ID
NCT02356289
Lead sponsor
MyoKardia, Inc.
Responsible party
Sponsor
First posted
Feb 5, 2015
Start date
Jan 2015
Primary completion
Jul 2015
Completion
Jul 2015
Last update
Sep 23, 2015

Study contacts

Jonathan C Fox, MD, PhD
study director · MyoKardia, Inc.

Oversight

Data monitoring committee
Yes
View the source record on ClinicalTrials.gov ↗

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This study is completed, as verified in Sep 2015. You cannot join it, but the record below documents what was studied.

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