CClinicalTrials.gg
TerminatedNCT02037347Updated Nov 30, 2016Results posted

Study to Evaluate the Use of Palifermin to Treat Toxic Epidermal Necrolysis

A Phase 1/2 interventional study of Palifermin in Toxic Epidermal Necrolysis and Stevens-Johnson Syndrome, sponsored by Brett King. Terminated at 2 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2016-11-30.

Sponsored by Brett King · Phase 1/2, Interventional, and Treatment

Why this study was terminated
Low enrollment numbers precluded completion of the study during a reasonable amount of time.
Phase
Phase 1/2
Study type
Interventional
Enrollment
1
Allocation
Not applicable
Ages
18 Years and older
Sex
All
01

Study summary

To test the ability of palifermin (a recombinant human keratinocyte growth factor) to decrease mucocutaneous injury and to promote epithelial repair in Toxic Epidermal Necrolysis and Stevens-Johnson Syndrome-Toxic Epidermal Necrolysis Overlap, diseases in which there is extensive sloughing of the skin and mucosa, including that of the eyes, gastrointestinal tract, respiratory and genitourinary systems.

02

Conditions studied

  • Toxic Epidermal Necrolysis
  • Stevens-Johnson Syndrome
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Skin biopsy in early disease showing apoptotic keratinocytes in the epidermis and in more advanced disease necrosis of the entire epidermis
  • Epidermal detachment or erythematous to purpuric macules involving more than 10% of body surface area in addition to involvement of the oropharynx; there may be further involvement of other mucosal surfaces, ie. conjunctivae, gastrointestinal tract, respiratory and genitourinary epithelia
  • Age of 18 years old or older
  • The patient is expected to survive longer than 48 hours

Exclusion criteria

Exclusion Criteria:

  • Skin detachment above 90% of the body surface area
  • Skin detachment has not progressed during the previous 48 hours
  • A positive serum pregnancy test
  • Age \< 18 years old
  • Known hematologic or solid organ malignancy
04

Study design

Phase
Phase 1 / Phase 2
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
1 participant (actual)

Study arms

  • Experimental
    Palifermin

    Palifermin 60 micrograms/kg/day IV for 3 consecutive days

    Drug: Palifermin

Interventions

  • DrugPalifermin

    Also known as: Kepivance

05

What researchers measure

Primary outcomes

  1. Time-to-cutaneous Re-epithelialization

    Time frame: The number of days between the start of palifermin administration and complete re-epithelialization of skin up to 14 days

Secondary outcomes

  1. Time-to-mucosal Re-epithelialization

    Time frame: The number of days between the start of palifermin administration and complete re-epithelialization of oral mucosa up to 14 days

  2. Time-to-cessation of Epidermal Necrosis

    Time frame: The number of days between the start of palifermin administration and cessation of further epidermal necrosis up to 14 days

06

Results

Posted Nov 30, 2016

Participant flow

Participant flow — Overall Study
MilestonePalifermin
Started1
Completed1
Not completed0

Outcome measures

PrimaryTime-to-cutaneous Re-epithelialization
Time frame:
The number of days between the start of palifermin administration and complete re-epithelialization of skin up to 14 days
Reported as:
Number · days
Time-to-cutaneous Re-epithelialization
daysPalifermin
Time-to-cutaneous Re-epithelialization6
SecondaryTime-to-mucosal Re-epithelialization
Time frame:
The number of days between the start of palifermin administration and complete re-epithelialization of oral mucosa up to 14 days

No measurements were reported for this outcome.

SecondaryTime-to-cessation of Epidermal Necrosis
Time frame:
The number of days between the start of palifermin administration and cessation of further epidermal necrosis up to 14 days
Reported as:
Number · days
Time-to-cessation of Epidermal Necrosis
daysPalifermin
Time-to-cessation of Epidermal Necrosis3

Adverse events

Non-serious events are listed at a 0% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Palifermin—1/1 (100%)0/1 (0%)
Most frequent serious events
Most frequent serious events
EventPalifermin
ischemic necrosisGastrointestinal disorders1/1

Baseline characteristics

73-year-old male.

Age, Customized
Age, Customized(years)Palifermin
Age73
Sex/Gender, Customized
Sex/Gender, Customized(participants)Palifermin
Male1
07

Study locations

2 sites
  • Bridgeport Hospital
    Bridgeport, Connecticut 06610, United States
  • Yale-New Haven Hospital
    New Haven, Connecticut 06510, United States
08

Registry details

Key details

Study ID
NCT02037347
Lead sponsor
Brett King
Collaborators
Swedish Orphan Biovitrum
Responsible party
Brett King (Assistant Professor of Dermatology, Yale University) — Sponsor-investigator
First posted
Jan 15, 2014
Start date
Oct 2010
Primary completion
Dec 2014
Completion
Dec 2014
Results posted
Nov 30, 2016
Last update
Nov 30, 2016

Oversight

Data monitoring committee
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is terminated, as verified in Oct 2016. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion