CClinicalTrials.gg
TerminatedNCT00517868Updated Aug 23, 2024Results posted

Study of URG101 in Painful Bladder Syndrome and Interstitial Cystitis

A Phase 2 interventional study of URG101 and Placebo in Painful Bladder Syndrome, Interstitial Cystitis and Bladder Pain Syndrome, sponsored by Urigen. Terminated at 6 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2024-08-23.

Sponsored by Urigen · Phase 2, Interventional, and Treatment

Why this study was terminated
The study was terminated due to Food and Drug Administration (FDA) recalled the heparin used in the trial because of possible contamination.
Phase
Phase 2
Study type
Interventional
Enrollment
28
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

A double-blind, placebo-controlled study to evaluate changes in pain, urgency and urinary frequency following administration of URG101 compared to placebo.

02

Conditions studied

  • Painful Bladder Syndrome
  • Interstitial Cystitis
  • Bladder Pain Syndrome

Keywords

  • bladder
  • pain
  • urgency
  • frequency
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • male and female subjects >= 18 years of age
  • moderate to severe symptoms of PBS/IC
  • minimum pain/urgency/frequency scores
  • female subjects on hormone therapy must be on stable dose for >= 3 months

Exclusion criteria

Exclusion Criteria:

  • positive pregnancy test or pregnant or lactating
  • narcotics or medical marijuana within 3 months
  • use of any investigational drug or device within 30 days
  • bacterial cystitis within 30 days
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Crossover assignment
Masking
Double (Participant, Investigator)
Enrollment
28 participants (actual)

Study arms

  • Other
    Crossover

    Placebo Treatment on Visit 1 followed by URG101 Treatment on Visit 2

    Drug: URG101 · Drug: Placebo

  • Other
    Crossover 2

    URG101 Treatment on Visit 1 followed by Placebo Treatment on Visit 2

    Drug: URG101 · Drug: Placebo

Interventions

  • DrugURG101

    Bladder instillation of URG101 or Placebo in random order on treatment 1 and treatment 2 followed by an open-label URG101 on treatment 3 within the same week.

  • DrugPlacebo

    Liquid formulation without active URG101 drug components

05

What researchers measure

Primary outcomes

  1. Change in Daytime Bladder Pain Intensity

    A calculation of average bladder pain intensity differences from baseline to 12 hours post-dose , as determined using an 11-point numerical rating scale (NRS) for bladder pain from time of dosing through 12 hours post dose. The 11-point NRS for bladder pain is a scale from 0 to 10, with 0 indicating no bladder pain and 10 indicating the worst imaginable bladder pain.

    Time frame: Through 12 hours

Secondary outcomes

  1. Change in Question 3 of the Patient Overall Rating of Improvement of Symptoms (PORIS) Questionnaire

    Percentage of subjects achieving ≥ 50% improvement in Question 3 of the PORIS questionnaire at 12 hours post-dose. The PORIS questionnaire is an assessment of the subject's condition after treatment compared to before treatment. In particular, Question 3 of the PORIS questionnaire asks subjects to select the category that best describes the overall change in their condition compared to before receiving study medication; the choices are: worse, no better (0% improvement), slightly improved (25% improvement), moderately improved (50% improvement), greatly improved (75% improvement), or symptoms gone (100% improvement).

    Time frame: Through 12 hours

  2. Change in Total Symptom Score

    A calculation of the average percentage change of Total Symptom Score (including Pelvic/Bladder Pain and Urinary Urgency scales) differences from baseline to 12 hours post-dose, as determined using 11-point numerical rating scales (NRS) for Pelvic/Bladder Pain and Urinary Urgency from time of dosing through 12 hours post dose. The 11-point NRS for Pelvic/Bladder Pain is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'. The 11-point NRS for Urinary Urgency (pressure to urinate) is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'.

    Time frame: Through 12 hours

  3. Change in Daytime Urinary Urgency Score

    A calculation of average percentage change of Urinary Urgency differences from baseline to 12 hours post-dose, as determined using 11-point numerical rating scales (NRS) for Urinary Urgency from time of dosing through 12 hours post dose. The 11-point NRS for Urinary Urgency (pressure to urinate) is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'.

    Time frame: Through 12 hours

06

Results

Posted Aug 23, 2024
Limitations and caveats
The study was intended to include 40 subjects, but it had to be terminated early because the Food and Drug Administration (FDA) unexpectedly recalled the heparin used in the trial due to a possible contamination. Of the 28 subjects enrolled, limited demographic information is available, and the available data are reported for all subjects as a single group. Of the 28 subjects enrolled, there were 18 evaluable full-crossover subjects for the statistical analysis.

Participant flow

Participant flow — Overall Study
MilestoneCrossover Group 1Crossover Group 2
Started1810
Completed1610
Not completed20

Outcome measures

PrimaryChange in Daytime Bladder Pain Intensity

A calculation of average bladder pain intensity differences from baseline to 12 hours post-dose , as determined using an 11-point numerical rating scale (NRS) for bladder pain from time of dosing through 12 hours post dose. The 11-point NRS for bladder pain is a scale from 0 to 10, with 0 indicating no bladder pain and 10 indicating the worst imaginable bladder pain.

Time frame:
Through 12 hours
Reported as:
Mean · Percentage of pain scale change
Change in Daytime Bladder Pain Intensity
Percentage of pain scale changePlaceboURG101
Change in Daytime Bladder Pain Intensity20.73 (5.04 to 36.41)41.86 (27.64 to 56.08)
Statistical analysis
  • Placebo vs URG101 · t-test, 1 sided · p = 0.0363 · Mean difference (final values): -21.14 · 95% CI -44.43 to 2.16
SecondaryChange in Question 3 of the Patient Overall Rating of Improvement of Symptoms (PORIS) Questionnaire

Percentage of subjects achieving ≥ 50% improvement in Question 3 of the PORIS questionnaire at 12 hours post-dose. The PORIS questionnaire is an assessment of the subject's condition after treatment compared to before treatment. In particular, Question 3 of the PORIS questionnaire asks subjects to select the category that best describes the overall change in their condition compared to before receiving study medication; the choices are: worse, no better (0% improvement), slightly improved (25% improvement), moderately improved (50% improvement), greatly improved (75% improvement), or symptoms gone (100% improvement).

Time frame:
Through 12 hours
Reported as:
Count of participants · Participants
Change in Question 3 of the Patient Overall Rating of Improvement of Symptoms (PORIS) Questionnaire
ParticipantsPlaceboURG101
Change in Question 3 of the Patient Overall Rating of Improvement of Symptoms (PORIS) Questionnaire29
SecondaryChange in Total Symptom Score

A calculation of the average percentage change of Total Symptom Score (including Pelvic/Bladder Pain and Urinary Urgency scales) differences from baseline to 12 hours post-dose, as determined using 11-point numerical rating scales (NRS) for Pelvic/Bladder Pain and Urinary Urgency from time of dosing through 12 hours post dose. The 11-point NRS for Pelvic/Bladder Pain is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'. The 11-point NRS for Urinary Urgency (pressure to urinate) is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'.

Time frame:
Through 12 hours
Reported as:
Mean · Percentage of change
Change in Total Symptom Score
Percentage of changePlaceboURG101
Change in Total Symptom Score17.04 ± 29.8738.31 ± 27.73
SecondaryChange in Daytime Urinary Urgency Score

A calculation of average percentage change of Urinary Urgency differences from baseline to 12 hours post-dose, as determined using 11-point numerical rating scales (NRS) for Urinary Urgency from time of dosing through 12 hours post dose. The 11-point NRS for Urinary Urgency (pressure to urinate) is a scale from 0 to 10, with 0 indicating 'none' and 10 indicating the 'worst ever'.

Time frame:
Through 12 hours
Reported as:
Mean · Percentage of change
Change in Daytime Urinary Urgency Score
Percentage of changePlaceboURG101
Change in Daytime Urinary Urgency Score13.30 ± 30.5334.50 ± 30.21
Post-hocDetermination of Serum Lidocaine Levels Post Study Drug Administration

Single-timepoint serum lidocaine measure at one hour following intravesical study drug administration

Time frame:
1 hour post-dose
Reported as:
Mean · µg/mL
Determination of Serum Lidocaine Levels Post Study Drug Administration
µg/mLEvaluable URG101 Subjects
Determination of Serum Lidocaine Levels Post Study Drug Administration0.51 (0.24 to 2.0)

Adverse events

Collected over Adverse Event (AE) collection timeframe: for the duration of study conduct (up to 3 study visits or 5 days total) through 24 hours post-last dose of placebo or study drug Serious Adverse Event (SAE) and All-Cause Mortality (ACM) collection timeframe: for the duration of study conduct (up to 3 study visits or 5 days total) through 30 days post-last dose of placebo or study drug. Non-serious events are listed at a 5% frequency threshold.

Adverse event summary by group
GroupDeathsSeriousOther
Placebo0/28 (0%)0/28 (0%)8/28 (28.6%)
URG1010/28 (0%)1/28 (3.6%)21/28 (75%)
Total0/28 (0%)1/28 (3.6%)28/28 (100%)
Most frequent serious events
Most frequent serious events
EventPlaceboURG101Total
Vaginal BleedingReproductive system and breast disorders0/281/281/28
Most frequent other events
Most frequent other events
EventPlaceboURG101Total
HeadacheNervous system disorders3/285/288/28
Bladder Discomfort/Pain/BurningRenal and urinary disorders1/286/287/28
Vaginal PainReproductive system and breast disorders0/284/284/28
DizzinessNervous system disorders1/282/283/28
Urethral Pain/Burn/DiscomfortRenal and urinary disorders1/281/282/28
Urinary UrgencyRenal and urinary disorders1/281/282/28
HematuriaRenal and urinary disorders1/281/282/28
Urinary Tract InfectionInfections and infestations0/282/282/28

Baseline characteristics

Subjects randomized per crossover arm as of the time of study termination.

Age, Customized
Age, Customized(Participants)All Participants Dosed
≥18 years of age28
Sex/Gender, Customized
Sex/Gender, Customized(Participants)All Participants Dosed
Male1
Female17
Unknown10
Race (NIH/OMB)
Race (NIH/OMB)(Participants)All Participants Dosed
American Indian or Alaska Native0
Asian0
Native Hawaiian or Other Pacific Islander0
Black or African American0
White0
More than one race0
Unknown or Not Reported28
07

Study locations

6 sites
  • Citrus Valley Medical Research
    Glendora, California 91741, United States
  • SD Uro-Research
    San Diego, California 92103, United States
  • University of California, San Diego
    San Diego, California 92103, United States
  • Scripps Clinic Medical Group
    San Diego, California 92130, United States
  • Georgia Urology
    Cartersville, Georgia 30120, United States
  • Urology San Antonio Research, P.A.
    San Antonio, Texas 78229, United States
08

References and documents

Publications

  • Parsons CL, Zupkas P, Proctor J, Koziol J, Franklin A, Giesing D, Davis E, Lakin CM, Kahn BS, Garner WJ. Alkalinized lidocaine and heparin provide immediate relief of pain and urgency in patients with interstitial cystitis. J Sex Med. 2012 Jan;9(1):207-12. doi: 10.1111/j.1743-6109.2011.02542.x. Epub 2011 Nov 14. PubMed 22082303 ↗

Individual participant data

Plan to share: No

09

Registry details

Key details

Study ID
NCT00517868
Lead sponsor
Urigen
Responsible party
Sponsor
First posted
Aug 17, 2007
Start date
Aug 28, 2007
Primary completion
Feb 28, 2008
Completion
Feb 28, 2008
Results posted
Aug 23, 2024
Last update
Aug 23, 2024

Study contacts

Jeff Proctor, M.D.
principal investigator · Georgia Urology

Oversight

Data monitoring committee
No
View the source record on ClinicalTrials.gov ↗

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