CClinicalTrials.gg
CompletedNCT00000692Updated Jun 24, 2005

Phase I Rising Dose Tolerability Study of SC-48334 in Patients With Acquired Immunodeficiency Syndrome (AIDS) and Advanced AIDS Related Complex

A Phase 1 interventional study of Butyldeoxynojirimycin in HIV Infections, sponsored by G D Searle. Completed at 6 sites in United States. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2005-06-24.

Sponsored by G D Searle · Phase 1, Interventional, and Treatment

Phase
Phase 1
Study type
Interventional
Enrollment
48
Ages
18 Years and older
Sex
All
01

Study summary

To determine the following about the use of SC-48334 in patients with AIDS and advanced AIDS related complex (ARC):

  1. The largest maximum tolerated dose (MTD); 2. Effectiveness against HIV; 3. Pharmacokinetics - how fast SC-48334 reaches the bloodstream, what concentration is reached, and how long it remains in the patient's blood.

SC-48334 is a chemical that prevents the biochemical actions of certain enzymes in the body, and recent studies have shown that it may also prevent the activity of HIV. The study will attempt to show whether SC-48334 can safely and effectively break the cycle of HIV infection in AIDS and advanced ARC by progressively eliminating HIV.

Read the detailed description

SC-48334 is a chemical that prevents the biochemical actions of certain enzymes in the body, and recent studies have shown that it may also prevent the activity of HIV. The study will attempt to show whether SC-48334 can safely and effectively break the cycle of HIV infection in AIDS and advanced ARC by progressively eliminating HIV.

Six patients are enrolled sequentially into each of eight different dose levels and the drug is administered by mouth at least 60 minutes before meals according to the following schedule: Day 1: One-quarter of total assigned daily dose. Patients receive the dosage in the hospital as either an inpatient or outpatient and are observed for 12 hours, during which time they are evaluated and blood is drawn for pharmacokinetic studies. Patients return at 24 and 48 hours for a limited physical examination and additional pharmacokinetic studies. Days 4 - 31: Total assigned daily dose, one-quarter 4 times a day. Patients are observed for at least 5 days in the hospital following the start of this part of the program, during which time clinical, laboratory, and pharmacokinetic information is obtained in order to establish baseline values. After the 6th day, patients are evaluated with a complete physical exam, urinalysis, and laboratory studies once a week and a limited physical exam and brief laboratory studies 3 times a week. At each of the eight dose levels, the second and third patients receive their first dose only after the first patient has been followed for 72 hours after receiving the first dose. Patients 4, 5, and 6 begin treatment only after patients 2 and 3 have completed 14 days of the four-part total dose. Patients are treated on an outpatient basis, with 5 to 6 days spent in the hospital for evaluation.

02

Conditions studied

  • HIV Infections

Keywords

  • Acquired Immunodeficiency Syndrome
  • AIDS-Related Complex
  • Antiviral Agents
  • Biological Availability
  • 1-Deoxynojirimycin
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

Concurrent Medication:

Allowed:

  • Aerosolized pentamidine.
  • Nystatin.
  • Clotrimazole.
  • Topical acyclovir.

Concurrent Treatment:

Allowed:

  • Blood transfusions for = or > grade 3 hemoglobin toxicity.

Exclusion criteria

Exclusion Criteria

Co-existing Condition:

Patients with the following conditions will be excluded:

  • Clinical significant diarrhea (> 3 stools per day for > 7 days without definable cause).
  • Active opportunistic infection, requiring ongoing therapy, at time of enrollment.
  • Any malignancy besides Kaposi's sarcoma, basal cell carcinoma, or squamous cell carcinoma unless the squamous cell carcinoma requires ongoing therapy.
  • Neurologic disease including dementia, peripheral neuropathy, myelopathy (CDC category IVb).

Concurrent Medication:

Excluded:

  • Antimetabolites.
  • Alkylating agents.
  • Drugs with known hepatic or bone marrow toxicity.

Patients with significant organ dysfunction will be excluded.

Prior Medication:

Excluded:

  • Antimetabolites.
  • Alkylating agents.
  • Excluded within 30 days of study entry:
  • Any investigational medication.
  • Drugs with anti-HIV activity.
  • Excluded within 90 days of study entry:
  • Ribavirin treatment.
  • Excluded within 6 months of study entry:
  • Cancer chemotherapy.

Prior Treatment:

Excluded within 6 months of study entry:

  • Radiation therapy.

Patients must demonstrate the following clinical and laboratory findings:

  • AIDS or advanced AIDS related complex (ARC), according to Centers for Disease Control (CDC) category IV, excluding neurologic disease in IVb.
  • Ability to understand the terms of study participation.

Current use of illicit drugs or abuse of alcohol.

04

Study design

Phase
Phase 1
Primary purpose
Treatment
Masking
None (open label)
Enrollment
48 participants

Interventions

  • DrugButyldeoxynojirimycin
05

Study locations

6 sites
  • Univ of California / San Diego Treatment Ctr
    San Diego, California 921036325, United States
  • Stanford Univ School of Medicine
    Stanford, California 94305, United States
  • Univ of Miami School of Medicine
    Miami, Florida 331361013, United States
  • Rush Presbyterian - Saint Luke's Med Ctr
    Chicago, Illinois 60612, United States
  • Harvard (Massachusetts Gen Hosp)
    Boston, Massachusetts 02114, United States
  • Julio Arroyo
    West Columbia, South Carolina 29169, United States
06

References and documents

Publications

  • Tierney M, Pottage J, Kessler H, Fischl M, Richman D, Merigan T, Powderly W, Smith S, Karim A, Sherman J, et al. The tolerability and pharmacokinetics of N-butyl-deoxynojirimycin in patients with advanced HIV disease (ACTG 100). The AIDS Clinical Trials Group (ACTG) of the National Institute of Allergy and Infectious Diseases. J Acquir Immune Defic Syndr Hum Retrovirol. 1995 Dec 15;10(5):549-53. PubMed 8548334 ↗
07

Registry details

Key details

Study ID
NCT00000692
Lead sponsor
G D Searle
Collaborators
National Institute of Allergy and Infectious Diseases (NIAID)
First posted
Aug 31, 2001
Last update
Jun 24, 2005

Study contacts

MS Hirsch
study chair
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is completed, as verified in Mar 2003. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion