National Institutes of Health: Muscular Dystrophies trials

The registry lists 17 Muscular Dystrophies studies with National Institutes of Health as lead sponsor. 4 are open to participants now and 0 have results posted.

Phase 1 1Phase 3 2No phase 14(a study in two phases counts in both)

Studies

Open to participants first, then studies with results posted, then the rest; newest registration first within each.

• Toward Ubiquitous Lower Limb Exoskeleton Use in Children and Young AdultsRecruitingNCT06998134
• Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement DisordersRecruitingNCT05726591Not applicable
• Investigational Use of Neuromuscular UltrasoundRecruitingNCT05237973
• Study of Inherited Neurological DisordersRecruitingNCT00004568
• Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular DystrophyCompletedNCT02194725
• Calibration and Validation of the PROMIS and Neuro-QOL Questionnaires in Cerebral Palsy and Congenital Muscular DystrophyCompletedNCT02153970
• Evaluating a New Knee-Ankle-Foot Brace to Improve Gait in Children With Movement DisordersCompletedNCT01961557Not applicable
• Heart Imaging in Children With Muscular DystrophyTerminatedNCT01633242
• Genetic and Physical Study of Childhood Nerve and Muscle DisordersCompletedNCT01568658
• Studying Skeletal Muscle, Heart, and Diaphragm Imaging in Boys With Duchenne Muscular DystrophyCompletedNCT01451281
• The Role of Family Functioning in Promoting Adaptation in Siblings of Individuals With Duchenne Muscular Dystrophy (DMD)TerminatedNCT01386515
• The PTC124 (Ataluren) Clinical Trial for Duchenne Muscular Dystrophy: Exploration of the Experiences of Parents, Clinician Researchers, and the Industry SponsorCompletedNCT01182324
• A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD)CompletedNCT00018109Phase 3
• Gentamicin Treatment of Muscular DystrophyCompletedNCT00005574Phase 1
• Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular DystrophyCompletedNCT00004646Phase 3
• Study of Muscle Abnormalities in Patients With Specific Genetic MutationsCompletedNCT00001871
• Studies of Patients With Skin Disease, Patients With Neurological Degenerations, and Normal VolunteersCompletedNCT00001164