Fanconi Syndrome clinical trials

The registry lists 15 studies for Fanconi Syndrome across 9 countries. 5 are recruiting or about to start. 4 of them are mainly about Fanconi Syndrome (how this is decided). Per ClinicalTrials.gov, last updated 2026-10-29.

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Status

Recruiting: 4
Completed: 4
Active, not recruiting: 3
Status unknown: 2
Not yet recruiting: 1
Withdrawn: 1

Phase

Phase 2: 4
Phase 1: 2

Where

United States: 7
Spain: 2
China: 2
Belgium: 1
Canada: 1
United Kingdom: 1

Who runs them

Rocket Pharmaceuticals Inc. (4) · The First Affiliated Hospital with Nanjing Medical University (2) · Novartis Pharmaceuticals (2) · Assistance Publique - Hôpitaux de Paris (1) · CENTOGENE GmbH Rostock (1) · Connecticut Children's Medical Center (1) · Cystinosis Research Foundation (1) · Centre Hospitalier Universitaire de Liege (1)

Coming up

0phase 3 studies under way

1study finishes main data collection within a year

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

The study

Mar 2027Accuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease · Connecticut Children's Medical Center

Who these studies take

Of the 4 Fanconi Syndrome studies recruiting now, 1 (25%) set no upper age limit and 2 (50%) stop at 75 or younger. 2 (50%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 0 (0%) take healthy volunteers.

Recruiting studies that take each age, of 4
Age	Women	Men
10	1 (25%)	1 (25%)
18	3 (75%)	3 (75%)
30	3 (75%)	3 (75%)
40	3 (75%)	3 (75%)
50	3 (75%)	3 (75%)
65	2 (50%)	2 (50%)
75	2 (50%)	2 (50%)
85	1 (25%)	1 (25%)

Across all 15 studies, recruiting or not: 40% stop at 75 or younger and 40% at 65; 80% take children; 0% are for women only and 0% for men only; 7% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

Studies

Recruiting first, then most recently updated. Showing 15 of 15. search them.