alpha-Mannosidosis: all 25 studies
Page 1 of 1. Open to participants first (6), then studies with results posted, then the rest; newest registration first within each.
- Analysis of Velmanase Alfa (Lamzede®)'s Effects in the Body of Children With Alpha-Mannosidosis Under the Age 3RecruitingNCT06184503
- Expanded Access to Velmanase AlfaAvailableNCT04959240
- Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RICRecruitingNCT04528355
- Longitudinal Study of Neurodegenerative DisordersRecruitingNCT03333200
- UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like CellsRecruitingNCT02254863Phase 1
- Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTRecruitingNCT01962415Phase 2
- Allogeneic Bone Marrow Transplant for Inherited Metabolic DisordersCompletedNCT01043640Phase 2Results posted
- Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of MetabolismTerminatedNCT00668564Phase 2Results posted
- Stem Cell Transplantation for HurlerCompletedNCT00176917Phase 2Results posted
- Interventional Study to Assess Efficacy and Safety of Velmanase Alfa in Patients With Alpha MannosidosisWithdrawnNCT04031066Phase 3
- Biomarker for Mannosidosis Disease (BioMannosidosis)WithdrawnNCT03264040
- Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-MannosidosisCompletedNCT02998879Phase 2
- Evaluation of Long-term Efficacy of Treatment With LamazymCompletedNCT02478840Phase 3
- MT2013-31: Allo HCT for Metabolic Disorders and Severe OsteopetrosisActive, not recruitingNCT02171104Phase 2
- Clinical Biomarkers in Alpha-mannosidosisCompletedNCT02141503
- Lamazym Aftercare StudyCompletedNCT01908725Phase 3
- Lamazym Aftercare Study FR Designed to Provide Treatment for French PatientsCompletedNCT01908712Phase 3
- Longitudinal Studies of the GlycoproteinosesCompletedNCT01891422
- A Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisCompletedNCT01681953Phase 3
- Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-MannosidosisCompletedNCT01681940Phase 2
- Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic DisordersTerminatedNCT01372228Phase 1/2
- Dose Finding Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosisStatus unknownNCT01285700Phase 2
- Safety Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosisCompletedNCT01268358Phase 1
- The Natural History of Alpha-MannosidosisCompletedNCT00498420
- Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell TransplantationStatus unknownNCT00005900