Achondroplasia: all 47 studies

Page 1 of 1. Open to participants first (12), then studies with results posted, then the rest; newest registration first within each.

• Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaRecruitingNCT07441876Phase 2/3
• Prospective Longitudinal Multicentric Study to Measure Limb Movement in Patients With FGFR3-related Skeletal DysplasiaRecruitingNCT07388966
• A Study in Children With AchondroplasiaRecruitingNCT07301463
• A Study of ABSK061 to Assess Safety, Tolerability, Pharmacokinetics, and Efficacy in Children With AchondroplasiaNot yet recruitingNCT07297875Phase 1/2
• Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)RecruitingNCT07169279Phase 2
• A Study of TYRA-300 in Children With Achondroplasia: BEACH301RecruitingNCT06842355Phase 2
• VIrtual STudy in Achondroplasia for the US (VISTA)RecruitingNCT06168201
• A Clinical Trial to Evaluate Efficacy and Safety of TransCon CNP Compared With Placebo in Infants (0 to <2 Years of Age) With AchondroplasiaRecruitingNCT06079398Phase 2
• A Clinical Trial to Investigate Long-term Safety, Tolerability, and Efficacy of Weekly Subcutaneous Doses With TransCon CNP in Children and Adolescents With AchondroplasiaEnrolling by invitationNCT05929807Phase 2/3
• Registry for Patients With Achondroplasia / Hypochondroplasia (OMPR-Ach/Hy)RecruitingNCT05328050
• Extension Study of Infigratinib in Children With Achondroplasia (ACH)Enrolling by invitationNCT05145010Phase 2
• Achondroplasia Natural History Multicenter Clinical StudyRecruitingNCT02597881
• A Study to Learn About Recifercept in Patients With AchondroplasiaCompletedNCT05659719Results posted
• A Clinical Trial to Evaluate Efficacy and Safety of TransCon CNP Compared With Placebo in Children With AchondroplasiaCompletedNCT05598320Phase 2/3Results posted
• Continuation Study of Long-term Safety, Tolerability, Pharmacokinetics and Efficacy of Recifercept in AchondroplasiaTerminatedNCT05116046Phase 2Results posted
• A Study Of Safety, Tolerability And Effectiveness Of Recifercept In Children With AchondroplasiaTerminatedNCT04638153Phase 2Results posted
• A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of TransCon CNP Administered Once Weekly in Prepubertal Children With AchondroplasiaCompletedNCT04085523Phase 2Results posted
• Resveratrol Trial for Relief of Pain in PseudoachondroplasiaTerminatedNCT03866200Phase 2Results posted
• Observational Study Investigating Clinical & Anthropometric Characteristics of Children With Achondroplasia.TerminatedNCT03794609Results posted
• A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With AchondroplasiaCompletedNCT03583697Phase 2Results posted
• A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With AchondroplasiaCompletedNCT03197766Phase 3Results posted
• A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With AchondroplasiaCompletedNCT02055157Phase 2Results posted
• Evaluate the Efficacy and Safety of KK8398 in Patients With Achondroplasia（AOBA Study）Active, not recruitingNCT06926491Phase 3
• A Clinical Trial to Evaluate Efficacy and Safety of Navepegritide in Adolescents (12 - 18 Years of Age) With Achondroplasia.Active, not recruitingNCT06732895Phase 2
• A Phase 2 Clinical Trial to Evaluate Efficacy, Safety, and Tolerability of Navepegritide in Combination With Lonapegsomatropin in Children With AchondroplasiaActive, not recruitingNCT06433557Phase 2
• A Study to Evaluate the Efficacy and Safety of Infigratinib in Children and Adolescents With AchondroplasiaCompletedNCT06164951Phase 3
• Bioequivalence Study to Compare Two Injection Devices for BMN 111 in Healthy ParticipantsTerminatedNCT05813314Phase 1
• Adaption and Testing of the Quality of Life in Short Stature Youth (QoLISSY) Questionnaire for Parents With Children From 0-4Status unknownNCT05603936
• A Study to Evaluate the Efficacy and Safety of Recombinant Human Growth Hormone in Children With AchondroplasiaCompletedNCT05353192Phase 4
• A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Multiple Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children With AchondroplasiaCompletedNCT05246033Phase 2
• A Clinical Trial to Evaluate Safety of Vosoritide in At-risk Infants With AchondroplasiaActive, not recruitingNCT04554940Phase 2
• Study of Infigratinib in Children With AchondroplasiaCompletedNCT04265651Phase 2
• Radiological Analysis on Patients With Achondroplasia DisorderStatus unknownNCT04184817
• Prospective Clinical Assessment Study in Children With Achondroplasia (ACH)CompletedNCT04035811
• An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With AchondroplasiaActive, not recruitingNCT03989947Phase 2
• A Multi-center, Longitudinal, Observational Study of Children With AchondroplasiaCompletedNCT03875534
• Lifetime Impact Study for AchondroplasiaCompletedNCT03872531
• The Norwegian Adult Achondroplasia StudyCompletedNCT03780153
• Lifetime Impact of Achondroplasia Study in Europe-LIAISECompletedNCT03449368
• An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With AchondroplasiaActive, not recruitingNCT03424018Phase 3
• A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)Active, not recruitingNCT02724228Phase 2
• A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With AchondroplasiaCompletedNCT01603095
• A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult VolunteersCompletedNCT01590446Phase 1
• C-Type Natriuretic Peptide and AchondroplasiaCompletedNCT01541306
• Special Survey for Long Term ApplicationCompletedNCT01516229
• A Survey Collecting Data on Adult Height in Patients With Achondroplasia Treated With SomatropinCompletedNCT01435629
• Issues Surrounding Prenatal Genetic Testing for AchondroplasiaCompletedNCT00001536

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