An expanded access record providing Lucerastat in Fabry Disease, sponsored by Idorsia Pharmaceuticals Ltd.. Available. Per ClinicalTrials.gov, last updated 2026-08-13.
Sponsored by Idorsia Pharmaceuticals Ltd. · Expanded access
This is a Post Trial Access program for patients with Fabry Disease who previously participated in the ID-069A302 (MODIFY OLE) trial and who were still enrolled in the study at the time the Sponsor decided to discontinue ID-069A302. The program is designed to provide continued access to lucerastat.
244 studies on the registry are indexed under Fabry Disease; 55 are open to participants now.
Browse Fabry Disease studies →Idorsia Pharmaceuticals Ltd. is the lead sponsor of 103 studies on the registry; 4 are open to participants now.
Of its 29 completed or terminated interventional studies of FDA-regulated products, 9 (31%) have results posted.
Counted across the registry records on this site, refreshed daily.
Go through the criteria one by one — yes, no or not sure — and take the list to your doctor or the study team. Kept in this browser only.
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Exclusion Criteria:
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No study locations are listed for this record.
Expanded access is arranged between your doctor and the company. Ask your care team to contact the provider listed on this record.
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Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.
Idorsia Pharmaceuticals Ltd. →