CClinicalTrials.gg
RecruitingNCT07091630emnergizeUpdated Sep 24, 2026

A Study to Assess the Efficacy and Safety of Empasiprubart in Adults With CIDP

A Phase 3 interventional study of Empasiprubart IV and Placebo IV in Chronic Inflammatory Demyelinating Polyneuropathy, CIDP and Chronic Inflammatory Demyelinating Polyradiculoneuropathy, sponsored by argenx. Recruiting at 85 sites in 24 countries. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2026-09-24.

Sponsored by argenx · Phase 3, Interventional, and Treatment

Phase
Phase 3
Study type
Interventional
Enrollment
160
Allocation
Randomized
Ages
18 Years and older
Sex
All
01

Study summary

The main purpose of this study is to demonstrate the efficacy and safety of empasiprubart in adults with CIDP. The study consists of a part A where participants will either receive empasiprubart or placebo for 24 weeks (6 months). Following part A, participants will enter part B in which all participants will receive empasiprubart for 96 weeks (24 months).

More information can be found here: https://clinicaltrials.argenx.com/emnergize

02

Conditions studied

  • Chronic Inflammatory Demyelinating Polyneuropathy
  • CIDP
  • Chronic Inflammatory Demyelinating Polyradiculoneuropathy
03

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  • Meets criteria for CIDP based on EAN/PNS Task Force CIDP guidelines, second revision (2021)
  • Has either typical CIDP or 1 of the following CIDP variants: motor CIDP (including motor-predominant CIDP), multifocal CIDP (also known as Lewis-Sumner syndrome), focal CIDP, or distal CIDP
  • Has residual disability and active disease
  • Has not received previous treatment for CIDP; or has stopped receiving CIDP treatment; or is receiving CIDP treatment (pulsed or oral corticosteroids, immunoglobulins, PLEX, or FcRn inhibitors)
  • Participants already receiving CIDP treatment will have to discontinue their CIDP treatment before first IMP administration and must be willing to switch to the study IMP

Exclusion criteria

Exclusion Criteria:

  • Meets the criteria for possible CIDP based on EAN/PNS Task Force CIDP guidelines, second revision (2021)
  • Sensory CIDP (including sensory-predominant CIDP)
  • Polyneuropathy of other causes
  • Clinical diagnosis of systemic lupus erythematosus (SLE)
  • Use of other long-acting immunomodulatory treatment or prior treatment (at any time) with total lymphoid irradiation or bone marrow transplantation
04

Study design

Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
Quadruple (Participant, Care provider, Investigator, Outcomes assessor)
Enrollment
160 participants (estimated)

Study arms

  • Experimental
    Part A - Empasiprubart

    Participants receive empasiprubart during part A

    Biological: Empasiprubart IV

  • Placebo comparator
    Part A - Placebo

    Participants receive placebo during part A

    Other: Placebo IV

  • Experimental
    Part B - Empasiprubart

    Participants receive empasiprubart during part B. Participants from the empasiprubart arm in part A will receive placebo once to maintain the blind of part A.

    Biological: Empasiprubart IV

Interventions

  • BiologicalEmpasiprubart IV

    Intravenous infusion of empasiprubart

  • OtherPlacebo IV

    Intravenous infusion of placebo

05

What researchers measure

Primary outcomes

  1. Reduction of ≥1 point compared with baseline in aINCAT score at week 24

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

    Time frame: Up to 24 weeks

Secondary outcomes

  1. Change from baseline in I-RODS centile points score

    Inflammatory Rasch-built Overall Disability Scale (I-RODS) assesses the limitations of activities and social participation in patients with inflammatory neuropathies like CIDP. The score ranges from 0 to 100 (higher score, worse outcome).

    Time frame: Up to 24 weeks (part A) + 96 weeks (Part B)

  2. Change from baseline in MRC-SS at week 24

    The Medical Research Council Sum Score evaluates motor strength. Evaluated on 6 muscle groups on each side, the score varies from 0 to 60 (lower score, worse outcome)

    Time frame: Up to 24 weeks

  3. Change from baseline in grip strength (3-day moving average) in the dominant hand at week 24

    Time frame: Up to 24 weeks

  4. Time to reduction of ≥1 point from baseline in aINCAT score

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

    Time frame: Up to 24 weeks

  5. Change from baseline in TUG

    The Timed Up and Go Test (TUG) is a simple test top assess a person's mobility in which the time expended to rise from a chair, walk 3 meters, turn around, walk back to the chair, and sit down is measured.

    Time frame: Up to 24 weeks (part A) + 96 weeks (Part B)

  6. Time to increase of ≥1 point compared with baseline in aINCAT score up to week 24

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

    Time frame: Up to 24 weeks

  7. Change from baseline in grip strength (3-day moving average) of both hands over time

    Time frame: Up to 24 weeks (part A)

  8. Change from baseline in grip strength (daily average) for both hands

    Time frame: Up to 96 weeks (Part B)

  9. Change from baseline in MRC-SS over time

    The Medical Research Council Sum Score evaluates motor strength. Evaluated on 6 muscle groups on each side, the score varies from 0 to 60 (lower score, worse outcome).

    Time frame: Up to 96 weeks (Part B)

  10. Change from baseline in aINCAT score over time

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

    Time frame: Up to 24 weeks + 96 weeks (Part B)

  11. Change from baseline in EQ-5D-5L over time

    EQ-5D-5L questionnaire is a patient-reported outcome measure, ranging 0 to 100 (lower score, worse outcome).

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  12. Change from baseline in RT-FSS over time

    Rasch-Transformed Fatigue Severity Scale (RT-FSS) is a patient-reported outcome measure to distinguish fatigue from clinical depression.

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  13. Change from baseline in BPI-SF over time

    The Brief Pain Inventory-Short Form (BPI-SF) is a patientreported outcome measure to assess pain severity and pain interference.

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  14. PGI-S values over time

    The Patient Global Impression of Severity (PGI-S) is a patient-reported outcome measure that reflects the patient's belief about the severity of the illness.

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  15. PGI-C values over time

    The Patient Global Impression of Change (PGI-C) is a patient-reported outcome measure that reflects the patient's belief about the efficacy of treatment.

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  16. Incidence of ADA against empasiprubart in serum

    Anti-drug antibodies

    Time frame: Up to 24 weeks + 96 weeks (Part B)

  17. Incidence of NAb against empasiprubart in serum

    Neutralizing antibodies

    Time frame: Up to 24 weeks + 96 weeks (Part B)

  18. Incidence of AEs and SAEs

    Time frame: Up to 24 weeks + 96 weeks (Part B)

  19. Percentage change from baseline in free C2 and total C2 over time

    Time frame: Up to 24 weeks (part A) + 96 weeks (Part B)

  20. Serum concentrations of empasiprubart over time

    Time frame: Up to 24 weeks (Part A) + 96 weeks (Part B)

  21. Reduction of ≥1 point in aINCAT over time

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome)

    Time frame: Up to 96 weeks (Part B)

  22. Increase of ≥1 point from baseline in aINCAT over time

    The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

    Time frame: Up to 96 weeks (Part B)

06

Study locations

85 of 85 sites recruiting
  • University of Alabama at Birmingham - 1720 University Blvd
    Birmingham, Alabama 35233, United States
    Recruiting
  • Samir Macwan, M.D., Inc. (S corporation)
    Rancho Mirage, California 92270, United States
    Recruiting
  • Colorado Springs Neurological Associates
    Colorado Springs, Colorado 80907, United States
    Recruiting
  • Medstar Health Research Institute
    Washington D.C., District of Columbia 20010, United States
    Recruiting
  • Gables Neurology
    Miami, Florida 33133, United States
    Recruiting
  • Aqualane Clinical Research
    Naples, Florida 34105, United States
    Recruiting
  • Paradigm Health System
    Slidell, Louisiana 70458, United States
    Recruiting
  • Penn Medicine University City
    Philadelphia, Pennsylvania 19104-5545, United States
    Recruiting
  • Jefferson Health Honickman Center
    Philadelphia, Pennsylvania 19107, United States
    Recruiting
  • University Neurology
    Knoxville, Tennessee 37920-1511, United States
    Recruiting
  • National Neuromuscular Research Institute
    Austin, Texas 78756, United States
    Recruiting
  • NeuroCarePlus
    Houston, Texas 77094, United States
    Recruiting
  • Instituto Privado Kremer
    Córdoba, X5004AOA, Argentina
    Recruiting
  • Instituto Médico de la Fundación Estudios Clínicos
    Rosario, S2000DEJ, Argentina
    Recruiting
  • INECO Neurociencias Oroño
    Rosario, Argentina
    Recruiting
  • Kepler Universitätsklinikum Linz - Med Campus III
    Linz, Upper Austria 4021, Austria
    Recruiting
  • Universitätsklinikum AKH Wien
    Vienna, 1090, Austria
    Recruiting
  • Unidade de Pesquisa Clinica e Inovacao da Estacio
    Rio de Janeiro, Rio de Janeiro 22640-100, Brazil
    Recruiting
  • Hospital de Clinicas de Porto Alegre (HCPA) - PPDS
    Pôrto Alegre, Rio Grande do Sul 90560-030, Brazil
    Recruiting
  • Hospital Das Clinicas da Faculdade de Medicina de Ribeirao Preto - UPS - PPDS
    Ribeirão Preto, São Paulo 14051-140, Brazil
    Recruiting
  • L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME
    Brasília, 70200-730, Brazil
    Recruiting
  • Hospital Moinhos de Vento
    Porto Alegre, 90560-032, Brazil
    Recruiting
  • PSEG Centro de Pesquisa Clinica
    São Paulo, 04038-002, Brazil
    Recruiting
  • Multiprofile Hospital for Active Treatment of Neurology and Psychiatry Sv. Naum EAD
    Sofia, Sofia 1113, Bulgaria
    Recruiting
  • University Multiprofile Hospital for Active Treatment
    Pleven, 5803, Bulgaria
    Recruiting
  • Medical Center Medika 2005 - Branch Sofia
    Sofia, 1164, Bulgaria
    Recruiting
  • University Multiprofile Hospital for Active Treatment Aleksandrovska EAD
    Sofia, 1431, Bulgaria
    Recruiting
  • University Multiprofile Hospital for Active Treatment and Emergency Medicine N. I. Pirogov EAD
    Sofia, 1606, Bulgaria
    Recruiting
  • Fujian Medical University Union Hospital - Yushan Campus
    Fuzhou, Fujian 350108, China
    Recruiting
  • The People's Hospital of Baiyun District Guangzhou
    Guangzhou, Guangdong 510440, China
    Recruiting
  • Peking University First Hospital - Changqiao Campus
    Beijing, 100034, China
    Recruiting
  • Guangdong Provincial Hospital of Chinese Medicine
    Guangzhou, 510120, China
    Recruiting
  • Nanfang Hospital Southern Medical University
    Guangzhou, 510515, China
    Recruiting
  • Xi'an Gaoxin Hospital
    Xi'an, 710075, China
    Recruiting
  • Fakultni nemocnice Brno
    Brno, 625 00, Czechia
    Recruiting
  • Rigshospitalet
    Copenhagen, 2100, Denmark
    Recruiting
  • Astra Kliinik
    Tallinn, 11315, Estonia
    Recruiting
  • CHU de Lille - Hôpital Roger Salengro
    Lille, Nord 59000, France
    Recruiting
  • AP-HP - Hôpital de la Pitié Salpétrière
    Paris, Paris 75013, France
    Recruiting
  • AP-HP - Hôpital Henri Mondor
    Créteil, Val-de-Marne 94000, France
    Recruiting
  • CHU de Bordeaux - Hôpital
    Bourdeaux, France
    Recruiting
  • CHU de Nice-Hôpital Pasteur
    Nice, 6001, France
    Recruiting
  • High Technology Hospital MedCenter Ltd
    Batumi, 6000, Georgia
    Recruiting
  • First Medical Clinic LLC
    Batumi, Georgia
    Recruiting
  • Petre Sarajishvili Institute of Neurology
    Tbilisi, 0112, Georgia
    Recruiting
  • Aleksandre Aladashvili Clinic
    Tbilisi, 102, Georgia
    Recruiting
  • Curatio JSC
    Tbilisi, 114, Georgia
    Recruiting
  • LTD New Hospitals
    Tbilisi, 114, Georgia
    Recruiting
  • Geo Hospitals
    Tbilisi, 144, Georgia
    Recruiting
  • Jo Ann Medical Center
    Tbilisi, 159, Georgia
    Recruiting
  • University General Hospital of Alexandroupolis
    Alexandroupoli, Evros 68100, Greece
    Recruiting
  • Eginitio Hospital
    Athens, Greece
    Recruiting
  • Semmelweis Egyetem Genomikai Medicina és Ritka Betegségek Intézete
    Budapest, 1082, Hungary
    Recruiting
  • Hillel Yaffe Medical Center
    Hadera, 3820302, Israel
    Recruiting
  • The Chaim Sheba Medical Center - PPDS
    Ramat Gan, 52621, Israel
    Recruiting
  • Fondazione Serena Onlus - Centro Clinico NeMO Brescia
    Gussago, Brescia 25064, Italy
    Recruiting
  • Azienda Sanitaria Universitaria Giuliano Isontina (ASUGI) - Ospedale di Cattinara
    Trieste, Friuli-VeneziaGiulia 34149, Italy
    Recruiting
  • IRCCS Istituto delle Scienze Neurologiche di Bologna
    Bologna, 40139, Italy
    Recruiting
  • IRCCS Azienda Ospedaliera Metropolitana - Ospedale Policlinico San Martino
    Genova, 16132, Italy
    Recruiting
  • Ospedale San Raffaele S.r.l.
    Milan, 20132, Italy
    Recruiting
  • Fondazione Istituto Neurologico Nazionale Casimiro Mondino IRCCS
    Pavia, 27100, Italy
    Recruiting
  • Azienda Sanitaria Universitaria Giuliano Isontina (ASUGI) - Ospedale di Cattinara
    Trieste, 34149, Italy
    Recruiting
  • Institute of Science Tokyo Hospital
    Bunkyō-Ku, Tokyo 113-8519, Japan
    Recruiting
  • Seirei Hamamatsu Hospital
    Hiroshima, 430-8558, Japan
    Recruiting
  • Southern TOHOKU Medical Clinic
    Kōriyama, 963-8052, Japan
    Recruiting
  • Saga University Hospital
    Saga, 849-0937, Japan
    Recruiting
  • Institutul de Neurologie si Neurochirurgie
    Chisinau, 2028, Moldova
    Recruiting
  • Institutul de Neurologie si Neurochirurgie
    Chisinau, 2028, Moldova
    Recruiting
  • Universitair Medisch Centrum Utrecht
    Utrecht, 3584 CX, Netherlands
    Recruiting
  • Centrum Medyczne Neurologia Slaska
    Katowice, 40-689, Poland
    Recruiting
  • SP ZOZ Szpital Uniwersytecki w Krakowie
    Krakow, 30-688, Poland
    Recruiting
  • Galen Clinic - Warszawa
    Warsaw, Poland
    Recruiting
  • Regina Maria Brasov Hospital
    Brasov, 500091, Romania
    Recruiting
  • S.C. Neurocity S.R.L
    Bucharest, Romania
    Recruiting
  • SC Clubul Sanatatii SRL
    Campulung Muscel, 115100, Romania
    Recruiting
  • Spitalul Judetean de Urgenta Deva
    Deva, 330084, Romania
    Recruiting
  • National Neuroscience Institute
    Singapore, Singapore
    Recruiting
  • Univerzitna nemocnica MARTIN
    Martin, 036 59, Slovakia
    Recruiting
  • Nemocnica s poliklinikou S. Kukuru a.s. - Pentahospitals
    Michalovce, 071 01, Slovakia
    Recruiting
  • Penta Hospitals SK, a.s. - Rimavská Sobota
    Rimavská Sobota, 979 01, Slovakia
    Recruiting
  • Seoul National University Hospital
    Seoul, 03080, South Korea
    Recruiting
  • Korea University Guro Hospital
    Seoul, 08308, South Korea
    Recruiting
  • Queen's Medical Centre
    Nottingham, Nottinghamshire NG72UH, United Kingdom
    Recruiting
  • The National Hospital for Neurology and Neurosurgery - PPDS
    London, WC1N3BG, United Kingdom
    Recruiting
  • Salford Royal Hospital
    Salford, M6 8HD, United Kingdom
    Recruiting
07

References and documents

Related links

Individual participant data

Plan to share: No

08

Registry details

Key details

Study ID
NCT07091630
Lead sponsor
argenx
Responsible party
Sponsor
First posted
Jul 29, 2025
Start date
Sep 16, 2025
Primary completion
Oct 7, 2027 (estimated)
Completion
Jan 23, 2031 (estimated)
Last update
Sep 24, 2026

Study contacts

Sabine Coppieters, MD
Contact
clinicaltrials@argenx.com
857-350-4834

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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