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RecruitingNCT06729996PEP-DMUpdated Jul 29, 2026

Pioglitazone Versus Empagliflozin for Chronic Pancreatitis/Recurrent Acute Pancreatitis/Acute Pancreatitis Associated Diabetes Mellitus

A Phase 2 interventional study of Pioglitazone (PIO) and Empagliflozin (EMPA) in Pancreatitis, Chronic, Pancreatitis, Acute and Diabetes Mellitus, sponsored by Mayo Clinic. Recruiting at 3 sites in United States. Open to participants aged 18 Years to 80 Years. Per ClinicalTrials.gov, last updated 2026-07-29.

Sponsored by Mayo Clinic · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
50
Allocation
Randomized
Ages
18 Years to 80 Years
Sex
All
01

Study summary

The purpose of this study is to evaluate efficacy of pioglitazone (PIO) versus empagliflozin (EMPA) to improve glycemic control in people with Chronic Pancreatitis (CP) or Recurrent Acute Pancreatitis (RAP) or Acute Pancreatitis (AP) associated with Diabetes Mellitus (DM). To evaluate mixed meal response in PIO versus EMPA group to better understand physiology of both therapies in CP-DM.

Read the detailed description

This trial will test the efficacy of PIO versus EMPA in improving glycemic control in CP-DM, RAP-DM and DM after one episode AP. The anticipated enrollment will consist of 40 subjects, age 18-80 years who have been diagnosed with CP or RAP or AP with DM, at two clinical sites in the United States. The primary objective is to evaluate the efficacy of PIO vs. EMPA to improve glycemic control in people with CP or RAP or AP associated with DM.

02

Conditions studied

  • Pancreatitis, Chronic
  • Pancreatitis, Acute
  • Diabetes Mellitus

Keywords

  • pancreatitis
  • diabetes
  • diabetes mellitus
  • empagliflozin
  • pioglitazone
03

Who can participate

Ages eligible
18 Years to 80 Years
Sexes eligible
All
Accepts healthy volunteers
No

Inclusion criteria

  1. Age ≥18-80 years at the time of enrollment.
  2. RAP or CP with DM diagnosed before or after CP diagnosis (Confirmed CP on imaging or RAP based on PROCEED study criteria, or acute pancreatitis followed by diabetes (AP-DM) and confirmed DM as per ADA criteria or clinically diagnosed with DM and on antihyperglycemic therapy)
  3. Able to provide written informed consent and participate in longitudinal follow-up
  4. A Stable retinal exam within 1 year prior to enrollment unless new onset diabetes was diagnosed within 6 months prior to study enrollment. If an eye exam within the past year is not available but the most recent exam is stable, a standard of care eye exam needs to be scheduled during the study period.
  5. HbA1c level 6.5-10.5% at screening visit.
  6. Current ongoing treatment with metformin and/or insulin and other antihyperglycemic medications will be accepted at screening. Patients will be willing to safely withdraw one or more study medication or mealtime insulin under the supervision of the study team by the time of screening. The patients clinical team will be informed promptly. Patients not on any antihyperglycemic medications are also eligible.

    a. If on a GLP-1 medication (e.g., semaglutide [Ozempic, Wegovy, Rybelsus], liraglutide, dulaglutide, exenatide, tirzepatide, etc.), the patient must be on a stable dose for at least 3 months prior to enrollment, with stable weight status at the time of enrollment and the GLP-1 dose cannot be escalated during the study period.

  7. Willing to perform blood glucose and ketone testing on study provided meters as per study protocol.

Exclusion criteria

Exclusion Criteria:

  1. Inability to take PIO or EMPA due to prior hypersensitivity or allergic reaction or current use of medications with potential for drug-drug interactions (Pioglitazone: Drug information - UpToDate, Empagliflozin: Drug information - UpToDate)
  2. Patients on PIO or EMPA at the time of screening
  3. Diagnosed with Type 1 Diabetes
  4. Pregnancy or lactation in women (positive urine pregnancy test at screening will lead to exclusion)
  5. History of bleeding disorders (e.g., Hemophilia A (factor VIII deficiency), hemophilia B (factor IX deficiency), von Willebrand disease, platelet disorders etc)
  6. Presence of hepatic impairment, ALT >3 x ULN with no etiology known at the time of enrollment or any evidence of acute/chronic liver disease
  7. Ongoing treatment for any malignancy requiring systemic treatment (non-melanoma skin cancers treated in dermatologists' office would be acceptable)
  8. Presence of osteoporosis without definitive treatment according to PI discretion.
  9. Recent inflammatory illness within the 30 days preceding enrollment (e.g.: URTI, episode of AP, etc)
  10. History of heart failure classified by NYHA as Class III or greater
  11. History of kidney dysfunction classified by an eGFR of \<30 mL/min/min
  12. Participation in any clinical trial within 30 days before screening for an approved or non-approved investigational medical product.
  13. Active alcohol dependence or chemical dependence including tobacco based on investigator discretion
  14. On a ketogenic diet
  15. Autoimmune pancreatitis, obstructive pancreatitis, and prior surgery of pancreas (Whipple procedure, total pancreatectomy, and distal pancreatectomy)
  16. Any condition which could jeopardize participant safety as per investigator opinion, (hemolytic anemia limiting A1c reliability, any evidence of fluid overload, presence of Congestive heart failure etc).
  17. Recent DKA or signs of decompensated diabetes in last 6 months or increased β hydroxybutyrate levels (>0.4 mmol/L) at screening.
04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Randomized
Intervention model
Parallel assignment
Masking
None (open label)
Enrollment
50 participants (estimated)

Study arms

  • Experimental
    Pioglitazone (PIO)

    PIO (Actos) is a thiazolidinedione and an agonist for peroxisome proliferator activated receptor (PPAR) gamma indicated as an adjunct to diet and exercise to improve glycemic control in adults with type 2 DM in multiple clinical settings. Its use has limitation for type 1 DM or for treatment of diabetic ketoacidosis. It is contraindicated to use in established NYHA class III or IV heart failure.

    Drug: Pioglitazone (PIO)

  • Experimental
    Empagliflozin (EMPA)

    EMPA is a sodium-glucose co-transporter 2 inhibitor, FDA approved drug. It is indicated to reduce the risk of cardiovascular death and hospitalization for heart failure in adults with heart failure, to reduce the risk of cardiovascular death in adults with type 2 DM and established cardiovascular disease and as an adjunct to diet and exercise to improve glycemic control in adults with type 2 DM. It is not recommended in patients with type 1 DM. It may increase the risk of diabetic ketoacidosis. Not recommended for use to improve glycemic control in adults with type 2 DM with an eGFR less than 30mL/min/1.73m2.

    Drug: Empagliflozin (EMPA)

Interventions

  • DrugPioglitazone (PIO)

    Subjects will take 30 mg tablet, once daily in the morning, taken with or without food for 12 weeks and after 12 weeks dose will be escalated to 45 mg based on Hemoglobin A1c (HbA1c) levels (HbA1c \>7.0% at 12 weeks, escalate the dose) once daily in the morning, taken with or without food till 24 weeks.

  • DrugEmpagliflozin (EMPA)

    Subjects will start with 10 mg dose, once daily in the morning, taken with or without food for 12 weeks and after 12 weeks dose will be escalated to 25 mg based on Hemoglobin A1c (HbA1c) levels (HbA1c \>7.0% at 12 weeks, escalate the dose) once daily in the morning, taken with or without food.

05

What researchers measure

Primary outcomes

  1. Hemoglobin A1c (HbA1c)

    Hemoglobin is a protein within red blood cells. As glucose enters the bloodstream, it binds to hemoglobin, or glycates. The more glucose that enters the bloodstream, the higher the amount of glycated hemoglobin. An HbA1C level below 5.7 percent is considered normal. Reported as percentage of glycated hemoglobin

    Time frame: Baseline to 24 weeks

  2. Area under curve (AUC) for glucose

    Pre-post study difference in AUC for glucose

    Time frame: Baseline to 24 weeks

  3. AUC for C-peptide

    Pre-post study difference in AUC for C-Peptide

    Time frame: Baseline to 24 weeks

  4. AUC for Insulin

    Pre-post study difference in AUC for Insulin

    Time frame: Baseline to 24 weeks

  5. AUC for glucagon

    Pre-post study difference in AUC for glucagon

    Time frame: Baseline to 24 weeks

Secondary outcomes

  1. Fasting plasma glucose

    Pre-post study difference in Fasting plasma glucose

    Time frame: Baseline to 24 weeks

  2. Lean mass

    Pre-post study difference in lean mass

    Time frame: Baseline to 24 weeks

  3. Fat mass

    Pre-post study difference in fat mass

    Time frame: Baseline to 24 weeks

  4. Visceral fat

    Pre-post study difference in visceral fat

    Time frame: Baseline to 24 weeks

  5. Fecal elastase

    Pre-post study difference in Fecal elastase (ELISA quantitative test, normal \>200 mcg/g)

    Time frame: Baseline to 24 weeks

  6. High Sensitivity C-Reactive Protein (Hs-CRP)

    Pre-post study difference in Hs-CRP

    Time frame: Baseline to 24 weeks

  7. Total cholesterol, LDL, HDL and Triglyceride

    Pre-post study difference in Total cholesterol, LDL, HDL and Triglyceride

    Time frame: Baseline to 24 weeks

  8. β-Hydroxybutyrate

    Pre-post study difference in β-Hydroxybutyrate

    Time frame: Baseline to 24 weeks

  9. Body weight

    Pre-post study difference in body weight

    Time frame: Baseline to 24 weeks

  10. Blood Pressure

    Pre-post study difference in Blood Pressure

    Time frame: Baseline to 24 weeks

  11. Body Mass Index (BMI)

    Pre-post study difference in BMI

    Time frame: Baseline to 24 weeks

  12. Patient-Reported Outcomes Measurement Information System - 29 Profile v2.1 (PROMIS-29 Profile v2.1)

    The PROMIS-29 Profile assesses following domains: * Physical function * Pain interference * Anxiety * Depression * Fatigue * Sleep disturbance * Ability to participate in social roles and activities PROMIS-29 is scored using T-scores. Higher T-scores indicate a higher level of the underlying construct. Each domain has a set of questions, typically 4 to 6 items, and responses are rated on a 5-point Likert scale (e.g., "Never," "Rarely," "Sometimes," "Often," "Always" or "Not at all," "A little bit," "Somewhat," etc.). The responses are then scored on a T-score scale (with a mean of 50 and a standard deviation of 10 in the general population). T-scores Interpretation: * A T-score of 50 is the average score for the general population. * T-scores above 50 indicate better functioning or less severe symptoms. * T-scores below 50 indicate worse functioning or more severe symptoms.

    Time frame: Baseline to 24 weeks

  13. Insulin sensitivity

    Change in sensitivity from baseline vs 24 weeks (Homeostatic Model Assessment, Matsuda Index)

    Time frame: Baseline to 24 weeks

  14. Beta cell function

    Change in Beta cell function from baseline vs 24 weeks using oral disposition index

    Time frame: Baseline to 24 weeks

Other outcomes

  1. Ketosis

    Percentage of participants experiencing Ketosis based on meter data

    Time frame: Baseline to 24 weeks

  2. Diabetic Ketoacidosis (DKA) events

    Number of DKA events

    Time frame: Baseline to 24 weeks

  3. Insulin needs

    Percentage of participants experiencing requirement for insulin

    Time frame: Baseline to 24 weeks

  4. Chronic pancreatitis exacerbation

    Percentage of participants experiencing CP exacerbation

    Time frame: Baseline to 24 weeks

  5. Acute pancreatitis episodes

    Percentage of participants experiencing AP episodes

    Time frame: Baseline to 24 weeks

  6. Exocrine pancreatic insufficiency

    Percentage of participants experiencing incident exocrine pancreatic insufficiency

    Time frame: Baseline to 24 weeks

  7. Vitamin D

    Decrease in vitamin D

    Time frame: Baseline to 24 weeks

  8. Bone fractures

    Percentage of participants experiencing bone fractures

    Time frame: Baseline to 24 weeks

  9. Adverse events

    Adverse events: Anemia, edema, urinary tract infection, Vaginal yeast infection

    Time frame: Baseline to 24 weeks

06

Study locations

2 of 3 sites recruiting
  • Mayo Clinic
    Rochester, Minnesota 55905, United States
    Recruiting
  • University of Pittsburgh
    Pittsburgh, Pennsylvania 15213, United States
    Recruiting
  • University of Pittsburgh Medical Center
    Pittsburgh, Pennsylvania 15219, United States
    • Shari Reynolds, BS, CCRP · Contact · reynoldssl2@upmc.edu · 412-383-0570
    • Dhiraj Yadav, MD, MPH · Principal investigator
    • Frederico G.S. de Toledo, MD · Sub investigator
    Not yet recruiting
07

References and documents

Individual participant data

Plan to share: No

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT06729996
Lead sponsor
Mayo Clinic
Collaborators
University of Pittsburgh Medical Center
Responsible party
Yogish C. Kudva (Principal Investigator, Mayo Clinic) — Principal investigator
First posted
Dec 12, 2024
Start date
May 29, 2025
Primary completion
May 31, 2027 (estimated)
Completion
May 31, 2027 (estimated)
Last update
Jul 29, 2026

Study contacts

Ravinder Jeet Kaur, M.B.B.S
Contact
Kaur.ravinder@mayo.edu
507-255-1455
Yogish Kudva
principal investigator · Mayo Clinic

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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