ClinicalTrials.gg
No longer availableNCT03544060Updated Sep 16, 2021

Volanesorsen Early Access Program for Patients With Familial Chylomicronemia Syndrome (FCS)

An expanded access record providing Volanesorsen in Familial Chylomicronemia, sponsored by Akcea Therapeutics. No longer available. Open to participants aged 18 Years and older. Per ClinicalTrials.gov, last updated 2021-09-16.

Sponsored by Akcea Therapeutics (part of Ionis Pharmaceuticals, Inc.) · Expanded access

Study type
Expanded access
Access type
Individual patients
Ages
18 Years and older
Sex
All
01

Study summary

The purpose of this program is to provide expanded access to volanesorsen for up to 100 Patients with Familial Chylomicronemia Syndrome (FCS).

Read the detailed description

The Program is intended to provide expanded access to volanesorsen for eligible patients with FCS who have limited or no available treatment options.

02

Conditions studied

  • Familial Chylomicronemia

Keywords

  • Familial Chylomicronemia
  • Familial Lipoprotein Lipase Deficiency
  • Hyperlipoproteinemias
  • Familial Hyperlipoproteinemia Type 1
  • Hyperlipoproteinemia Type 1
  • Hyperchylomicronemia, Familial
  • Lipoprotein Lipase Deficiency, Familial
  • Hyperlipidemias
  • Dyslipidemias
  • Lipid Metabolism Disorders
  • Lipid Metabolism, Inborn Errors
  • Metabolic Diseases
  • Metabolism, Inborn Errors
  • Genetic Diseases, Inborn
03

In context

Hyperlipoproteinemia Type I

21 studies on the registry are indexed under Hyperlipoproteinemia Type I; 3 are open to participants now.

Browse Hyperlipoproteinemia Type I studies →

Lead sponsor

Akcea Therapeutics is the lead sponsor of 15 studies on the registry; 1 is open to participants now.

Of its 9 completed or terminated interventional studies of FDA-regulated products, 8 (89%) have results posted.

Counted across the registry records on this site, refreshed daily.

04

Who can participate

Ages eligible
18 Years and older
Sexes eligible
All

Go through the criteria one by one — yes, no or not sure — and take the list to your doctor or the study team. Kept in this browser only.

Inclusion criteria

  • Patients who participated in the APPROACH Open Label trial, must have completed the open label extension trial for volanesorsen for a length of time consistent with the study protocol (≥ 1 year). Patients in the APPROACH open Label trial for less than a year require approval from Akcea to participate in the EAP. Patients who did not participate in the APPROACH open label trial require approval from Akcea for entry into EAP.
  • Patients not participating in the APPROACH open label trial must have a diagnosis of FCS as determined by the participating physician, as outlined in the Volanesorsen EAP protocol. Akcea will review each application to determine eligibility.
  • Male patients and female patients of must continue to use appropriate with their partners, or refrain from sexual activity

Exclusion criteria

Exclusion Criteria:

  • Patients who have any new conditions or worsening of existing conditions which in the opinion of the Physician would make the patient unsuitable for treatment with volanesorsen.
  • Volanesorsen naïve patients with baseline values ≤ 140,000/mm3
  • Patients not willing to adhere to mandatory blood draws for platelet monitoring
  • Patients who in the opinion of Akcea's medical team, are not eligible candidates for volanesorsen therapy.
  • Any patient who plans to or becomes pregnant.
  • Any patient who was withdrawn from the APPROACH open label study due to a serious adverse event related to volanesorsen therapy.
Terms in these criteria, in plain language(3)

Underlined terms in the criteria open these too. Explained by clinicaltrials.gg, not part of the registry record. The study team decides who can take part.

Childbearing potential

Able to become pregnant: from the first period until menopause, unless permanently unable to through surgery (removal of the womb, or of both ovaries or both fallopian tubes).

Criteria for people of childbearing potential usually ask for a negative pregnancy test and for contraception during the study and for a time after it.

Contraception

Ways of preventing pregnancy. “Highly effective” methods fail less than 1% of the time a year when used correctly — for example an IUD or an implant.

Criteria usually say which methods count and how long to keep using them after the last dose, sometimes for male participants too. Some studies accept a partner’s vasectomy if it was confirmed successful and that person is the participant’s only sexual partner.

Platelets

Blood cells that help blood clot. Too few raises the risk of bleeding and bruising. A usual adult range is about 150–400 × 10⁹/L (150,000–400,000 per µL); each lab has its own reference range.

05

Access details

Study type
Expanded access
Access type
Individual patients

Available treatment

  • Volanesorsen administered by subcutaneous (SC) injections in the abdomen, thigh, or upper arm.

    Also known as: Waylivra

06

Where to request access

No study locations are listed for this record.

07

Updates

Tracking since Sep 25, 2026
No changes since tracking began. The registry record was last updated on Sep 16, 2021, before this site started recording changes on Sep 25, 2026. Its history is on ClinicalTrials.gov ↗
08

Registry details

Key details

Study ID
NCT03544060
Lead sponsor
Akcea Therapeutics
Collaborators
CaligorRx, Inc.
Responsible party
Sponsor
First posted
Jun 1, 2018
Last update
Sep 16, 2021
View the source record on ClinicalTrials.gov ↗

Requesting access

Expanded access is arranged between your doctor and the company. Ask your care team to contact the provider listed on this record.

No contact was published for this record. The registry link below has the sponsor’s details.

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Discussion

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