CClinicalTrials.gg
Status unknownNCT03288168CNOG-MB001Updated Apr 17, 2020

Children's and Adolescents' Medulloblastoma Molecular Subgroups in China

An observational study in Medulloblastoma, Childhood, sponsored by Xinhua Hospital, Shanghai Jiao Tong University School of Medicine. Status unknown at 9 sites in China. Open to participants aged Up to 18 Years. Per ClinicalTrials.gov, last updated 2020-04-17.

Sponsored by Xinhua Hospital, Shanghai Jiao Tong University School of Medicine · Observational

The sponsor has not verified this record recently (last verified Apr 2020), so the status shown — last known as Active, not recruiting — may be out of date.
Study type
Observational
Model
Cohort
Time perspective
Retrospective
Enrollment
200
Ages
Up to 18 Years
Sex
All
01

Study summary

Recently, diagnosis and treatments for medulloblastoma becomes more complicated than before since the new World Health Organization (WHO) diagnosis criteria has put molecular marker onto an ever important position. Reports and studies revealed highly correlated connection between subgroups of medulloblastoma and patient outcomes. Children's Oncology Group (COG) has launched many new studies on molecular subgroups-based specific treatment trails. In China, children and adolescents with brain tumor have been treated variously for a long time in lack of standardized comprehensive treatments. Same poor situation in basic research and clinical studies makes the Chinese children with brain tumor hardly catch up with international level in molecular diagnosis and specific treatments. There are limited studies, which were conducted by immunohistochemistry for identifying medulloblastoma molecular subgroups, indicating the similar correlation of the subgroups and outcomes to world-wide reports. As the Children's Neuro-Oncology Group (CNOG) was established in China in May 2017, it makes studies from multiple centers in children's brain tumors become practical. And the availability of DNA methylation array, NanoString and other methods in medulloblastoma subgroup identification assures the quality of the method for this study.

Read the detailed description

Studies discovered that medulloblastoma is a group of tumors with different pathogenesis through different pathways, and majorly can be divided into four molecular subgroups. Moreover, multicenter retrospective studies from US, Canada and European Countries revealed that the molecular subgroup of medulloblastoma becomes an independent correlated risk factor for the patient outcomes. This finding made WHO classification of tumours of central nervous system consider the markers in molecular pathway be an ever important indicator in the new diagnosis criteria. In COG prospective studies for target therapies, subgroup distinguishing becomes indispensable, and the use of immunohistochemistry combined with NanoString, DNA methylation arrays or other molecular methods makes subgroup identification more reliable. In China, there are limited single institutional studies, which were all conducted by immunohistochemistry or polymerase chain reaction (PCR), on molecular sub-grouping of medulloblastoma, especially in pediatric patients. This multicenter retrospective study enrolls children and adolescents (0-18y/o) with primary medulloblastoma from CNOG member institutions across the country, with available paraffin embedded samples and reliable follow-up information, to assess the correlation of molecular subgroups of medulloblastoma and outcomes in Chinese population.

This multicenter study recruits eligible patients from CNOG member institutions. Data validation and verification is double conducted by each center and investigators in central data base. Case report form (CRF) was designed by principle investigator and will be modified in the period of uploading first 5 cases by each participated center. The estimated enrollment is 200 cases after sample size assessment. Descriptive statistical analysis, Two-Sample (Independent group) T-Test and one-way ANOVA will be used in epidemiological analysis. Cox-regression / Kaplan-Meier plot will be used in survival analysis. Chi-square test will be used to validate the test efficiency of immunohistochemistry and NanoString methods.

02

Conditions studied

  • Medulloblastoma, Childhood

Browse trials for

Keywords

  • Observation
  • Molecular Subgroup
  • NanoString
03

Who can participate

Ages eligible
Up to 18 Years
Sexes eligible
All
Accepts healthy volunteers
No
Sampling method
Non-probability sample

Study population

Children and adolescents from 0-18 y/o, diagnosed with Medulloblastoma in CNOG-MB001 study participated institutions in mainland China, with available detailed clinical records, full followup records and available tumor samples, fitting eligibility criteria, are enrolled in this study.

Inclusion criteria

  • Participants must have classical histology posterior fossa medulloblastoma as determined by institutional neuro-pathological evaluation.
  • Participants must have tumor tissue samples (either paraffin embedded tissue block or frozen tissue) for NanoString test for distinguishing the molecular subgroups of medulloblastoma in Xinhua hospital affiliated to Shanghai Jiaotong University School of Medicine (SHXH).
  • Participants must provide tumor tissue samples (either paraffin embedded tissue block or frozen tissue) for immunohistochemistry assessment in verifying the molecular subgroups of medulloblastoma, or conduct the same immunohistochemistry test according to central analysis in SHXH, and send the slides to SHXH for center reviewing.
  • Diagnostic imaging (pre and post operation (OP) contrast MRI or CT, Post-OP imaging conducted within 72 hours, no later than 14 days) must be forwarded to SHXH for central review to confirm eligibility.
  • Sufficient pathologic material must be available for central analysis and review in SHXH.
  • The patients must have no previous radiotherapy or chemotherapy other than corticosteroids.
  • Ability to understand and willingness to comply with follow-up visits.
  • Life expectancy more than 4 weeks.

Exclusion criteria

Exclusion Criteria:

  • Patients must not have received any prior tumor-directed therapy other than surgical intervention and corticosteroids.
  • Tumor tissue sample not available for biological studies (from the initial diagnosis and/or relapse).
  • Clinically significant unrelated systemic illness (e.g., serious infection or significant cardiac, pulmonary, hepatic, or other organ dysfunction) that would compromise the patient's ability to tolerate standard treatment or would likely interfere with study results.
  • Patients obtained no radiation and/or chemo therapies are not excluded in this study since the nature history of the disease will also be evaluated.
04

Study design

Observational model
Cohort
Time perspective
Retrospective
Enrollment
200 participants (estimated)
Patient registry
No
Biospecimen retention
Samples with dna

Groups and cohorts

  • 0-18 y/o Patients with Medulloblastoma

    Patients treated with comprehensive treatments including surgery, chemo-therapy with / without (less than 3 y/o) radiation, during the period of Jan 2008 and Dec 2012, whose tumor samples will be tested by NanoString and Histochemistry methods, are enrolled in this cohort group.

05

What researchers measure

Primary outcomes

  1. Overall Survival

    The observation period of outcome started with the first medical record available on site till last contact available on site or the end of the observation period (31 December 2017), whichever occurred first.

    Time frame: Follow-up for final survival period till 31 December 2017 or last available contact, whichever occurred first

Secondary outcomes

  1. Event Free Survival

    The observation period of outcome started with the first medical record available on site till last contact available on site or the end of the observation period (31 December 2017), whichever occurred first.

    Time frame: Follow-up for none-recurrence survival (metastasis/relapse) period till 31 December 2017 or last available contact, whichever occurred first.

06

Study locations

9 sites
  • The First Affiliated Hospital of Fujian Medical University
    Fuzhou, Fujian 350005, China
  • Fuzhou General Hospital of Nanjing Military Region
    Fuzhou, Fujian 350100, China
  • Sun Yat-Sen University Cancer Center
    Guangzhou, Guangdong 510060, China
  • Guangdong 999 Brain Hospital
    Guangzhou, Guangdong 510510, China
  • Xijing Hospital, Fourth Military Medical University
    Xi'an, Shaanxi 710032, China
  • Liaocheng People's Hospital
    Liaocheng, Shandong 252000, China
  • Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
    Shanghai, Shanghai 200086, China
  • Renji Hospital, Shanghai Jiaotong University School of Medicine
    Shanghai, Shanghai 200127, China
  • Shanxi Provincial People's Hospital
    Taiyuan, Shanxi 030012, China
07

References and documents

Individual participant data

Plan to share: Undecided

No publications or documents are linked to this record.

08

Registry details

Key details

Study ID
NCT03288168
Lead sponsor
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
Collaborators
Children's Neuro-Oncology Group (CNOG)
Responsible party
Jie Ma, MD, PhD (Head of Department of Pediatric Neurosurgery, Xinhua Hospital, Shanghai Jiao Tong University School of Medicine) — Principal investigator
First posted
Sep 19, 2017
Start date
Sep 1, 2017
Primary completion
Dec 31, 2020 (estimated)
Completion
Jun 30, 2021 (estimated)
Last update
Apr 17, 2020

Study contacts

Jie MA, MD, Phd
study chair · Xinhua Hospital, Shanghai Jiao Tong University School of Medicine

Oversight

Data monitoring committee
No
FDA-regulated drug
No
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

Not currently enrolling

This study is status unknown, as verified in Apr 2020. You cannot join it, but the record below documents what was studied.

Follow this study

Get an email when the registry record changes — status, dates, results — or when someone posts here.

Sign in to follow

Discussion

Questions and observations about this study, from anyone following it. Not medical advice, and not a channel to the study team — their contact details are on the registry record.

Sign in to join the discussion. Reading takes no account; posting does. You choose a display name, and a pseudonym is the default.

Nothing here yet. If you are running this trial, taking part in it, or weighing whether to, this is the place to say so.

Start the discussion