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RecruitingNCT02991469SKYPSUpdated Sep 23, 2026

A Repeated Dose-finding Study of Sarilumab in Children and Adolescents With Systemic Juvenile Idiopathic Arthritis (SKYPS)

A Phase 2 interventional study of Sarilumab SAR153191 (REGN88) in Juvenile Idiopathic Arthritis, sponsored by Sanofi. Recruiting at 37 sites in 14 countries. Open to participants aged 1 Year to 17 Years. Per ClinicalTrials.gov, last updated 2026-09-23.

Sponsored by Sanofi · Phase 2, Interventional, and Treatment

Phase
Phase 2
Study type
Interventional
Enrollment
51
Allocation
Not applicable
Ages
1 Year to 17 Years
Sex
All
01

Study summary

Primary Objective:

To describe the pharmacokinetic (PK) profile of sarilumab in patients aged 1-17 years with Systemic Juvenile Idiopathic Arthritis (sJIA) in order to identify the dose and regimen for adequate treatment of this population.

Secondary Objective:

To describe the pharmacodynamics (PD) profile, the efficacy, and the long term safety of sarilumab in patients with sJIA.

Read the detailed description

The total study duration per patient will be 166 weeks that will consist of a 4- week screening, a 12-week core treatment phase, a 144-week extension phase, and a 6-week post-treatment follow-up.

02

Conditions studied

  • Juvenile Idiopathic Arthritis

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03

Who can participate

Ages eligible
1 Year to 17 Years
Sexes eligible
All
Accepts healthy volunteers
No

Eligibility criteria

Inclusion criteria :

  • Male and female patients aged ≥1 and ≤17 years (or country specified age requirement, ≥6 to ≤17 years for Russia) at the time of the screening visit.
  • Diagnosis of systemic JIA subtype according to the International Associations against Rheumatism (ILAR) 2001 Juvenile Idiopathic Arthritis (JIA) Classification Criteria OR According to 2024 EULAR/PReS recommendation at Screening.
  • Patient with an inadequate response to current treatment and considered as a candidate for a biologic disease modifying anti rheumatic drug (DMARD) as per investigator's judgment.

Exclusion criteria:

  • Body weight \<10 kg or >60 kg for patients enrolled in the ascending dose cohorts, then body weight \<10 kg for patients subsequently enrolled at the selected dose.
  • Uncontrolled severe systemic symptoms and/or Macrophage Activation Syndrome (MAS) within 6 months prior to screening.
  • History of or ongoing interstitial lung disease, pulmonary hypertension, pulmonary alveolar proteinosis.
  • If nonsteroidal anti-inflammatory drugs (NSAIDs) (including cyclo oxygenase-2 inhibitors [COX-2]) taken, dose stable for less than 2 weeks prior to the baseline visit and/or dosing prescribed outside of approved label.
  • If non-biologic DMARD taken, dose stable for less than 6 weeks prior to the baseline visit or at a dose exceeding the recommended dose as per local labeling.
  • If oral glucocorticoid taken, dose exceeding equivalent prednisone dose 1 mg/kg/day (or 60 mg/day) within 3 days prior to baseline.
  • Use of parenteral or intra-articular glucocorticoid injection within 4 weeks prior to baseline.
  • Prior treatment with anti-interleukin 6 (IL-6) or IL-6 receptor (IL-6R) antagonist therapies, including but not limited to tocilizumab or sarilumab.
  • Treatment with any biologic treatment for sJIA within 5 half-lives prior to the first dose of sarilumab (the required off treatment periods and procedures may vary according to local requirements).
  • Treatment with a Janus kinase inhibitor within 4 weeks prior to the first dose of sarilumab; and treatment with growth hormone within 4 weeks prior to the first dose of sarilumab (the required off treatment periods and procedures may vary according to local requirements).
  • Treatment with any investigational biologic or non-biologic product within 8 weeks or 5 half-lives prior to baseline, whichever is longer.
  • Exclusion related to tuberculosis.
  • Exclusion criteria related to past or current infection other than tuberculosis.
  • Any live, attenuated vaccine within 4 weeks prior to the baseline visit, such as varicella-zoster, oral polio, rubella vaccines. Killed or inactive vaccine may be permitted based on the Investigator's judgment.
  • Exclusion related to history of a systemic hypersensitivity reaction to any biologic drug and known hypersensitivity to any constituent of the product.
  • Laboratory abnormalities at the screening visit (identified by the central laboratory).
  • Severe cardiac disease due to sJIA.
  • Pregnant or breast-feeding female adolescent patients.

The above information is not intended to contain all considerations relevant to a patient's potential participation in a clinical trial.

04

Study design

Phase
Phase 2
Primary purpose
Treatment
Allocation
Not applicable
Intervention model
Single group
Masking
None (open label)
Enrollment
51 participants (estimated)

Study arms

  • Experimental
    Sarilumab

    Participants will receive one of two ascending doses (or an additional intermediate dose based on available data) of sarilumab by subcutaneous (SC) injection based on body weight. All the participants will receive the selected dose once the selected dose is identified. Sarilumab will be given during 12-week core treatment phase followed by a 144- week extension treatment phase.

    Drug: Sarilumab SAR153191 (REGN88)

Interventions

  • DrugSarilumab SAR153191 (REGN88)

    Pharmaceutical form: Solution Route of administration: Subcutaneous

05

What researchers measure

Primary outcomes

  1. Assessment of PK parameter: maximum serum concentration observed (Cmax)

    Time frame: Up to Week 12

  2. Assessment of PK parameter: Area under the serum concentration versus time curve calculated using the trapezoidal method during a dose interval (AUC0-t)

    Time frame: Up to Week 12

  3. Assessment of PK parameter: Concentration observed before treatment administration during repeated dosing (Ctrough)

    Time frame: Up to Week 12

Secondary outcomes

  1. Number of patients with adverse events

    Time frame: Core treatment phase: Up to Week 12. Extension phase: Up to Week 162

  2. Proportion of participants with local reactions after injection

    Time frame: Core treatment phase: Up to Week 12. Extension phase: Up to Week 156

  3. Proportion of participants with Investigator Global Assessment (IGA) of disease activity below a defined value on 1-100 VAS scale

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  4. Proportion of participants with Parent / patient Global Assessment (PGA) of well-being below a defined value on 1-100 VAS scale

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  5. Proportion of participants with clinically inactive disease (CID)

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  6. Changes in glucocorticoid use

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  7. Juvenile Idiopathic Arthritis ACR30/50/70/90/100 (in the absence of fever) response rate

    Population according to the 2001 ILAR classification

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  8. Change from baseline in individual JIA ACR components

    Population according to the 2001 ILAR classification

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  9. Change from baseline in Systemic Juvenile Arthritis Disease Activity Score-10 (sJADAS-10)

    Population according to the 2001 ILAR classification

    Time frame: Core treatment phase: Up to Week 12. Extension phase: At weeks 24, 48, and every 24 weeks up to Week 156

  10. Assessment of participants with disease-related symptoms

    Population according to the 2024 EULAR / PReS

    Time frame: At Week 4

  11. Changes in IL-6 associated biomarkers

    Population according to the 2001 ILAR classification and the 2024 EULAR / PReS

    Time frame: Up to Week 12

06

Study locations

30 of 37 sites recruiting
  • Investigational Site Number : 0320004
    San Miguel de Tucumán, Tucumán Province T4000, Argentina
    Recruiting
  • Investigational Site Number : 0320005
    Buenos Aires, 1023, Argentina
    Recruiting
  • Investigational Site Number : 1240110
    Calgary, Alberta T3B 6A9, Canada
    Recruiting
  • Investigational Site Number : 2460040
    Helsinki, 00029, Finland
    Recruiting
  • Investigational Site Number : 2500041
    Bron, 69500, France
    Recruiting
  • Investigational Site Number : 2500042
    Montpellier, 34295, France
    Recruiting
  • Investigational Site Number : 2500040
    Paris, 75015, France
    Recruiting
  • Investigational Site Number : 2760064
    Berlin, 13125, Germany
    Recruiting
  • Investigational Site Number : 2760065
    Berlin, 13353, Germany
    Recruiting
  • Investigational Site Number : 2760062
    Hamburg, 22081, Germany
    Recruiting
  • Investigational Site Number : 2760060
    Sankt Augustin, 53757, Germany
    Recruiting
  • Investigational Site Number : 2760063
    Sendenhorst, 48324, Germany
    Completed
  • Investigational Site Number : 3000001
    Athens, 115 27, Greece
    Recruiting
  • Investigational Site Number : 3000004
    Athens, 115 27, Greece
    Recruiting
  • Investigational Site Number : 3000002
    Thessaloniki, 546 42, Greece
    Recruiting
  • Investigational Site Number : 3480001
    Budapest, 1085, Hungary
    Recruiting
  • Investigational Site Number : 3720001
    Crumlin, Dublin D12 N512, Ireland
    Recruiting
  • Investigational Site Number : 3800051
    Genoa, Genova 16147, Italy
    Recruiting
  • Investigational Site Number : 3800054
    Milan, Milano 20122, Italy
    Recruiting
  • Investigational Site Number : 3800052
    Rome, Roma 00165, Italy
    Recruiting
  • Investigational Site Number : 4840004
    Mérida, Yucatán 97070, Mexico
    Recruiting
  • Investigational Site Number : 4840001
    Mexico City, 06700, Mexico
    Recruiting
  • Investigational Site Number : 6200003
    Lisbon, 1150-199, Portugal
    Recruiting
  • Investigational Site Number : 6200005
    Lisbon, 1500-650, Portugal
    Recruiting
  • Investigational Site Number : 6200001
    Lisbon, 1649-035, Portugal
    Recruiting
  • Investigational Site Number : 6430001
    Moscow, 115522, Russia
    Completed
  • Investigational Site Number : 6430062
    Moscow, 117997, Russia
    Completed
  • Investigational Site Number : 6430063
    Moscow, 119991, Russia
    Completed
  • Investigational Site Number : 6430065
    Ufa, 450083, Russia
    Completed
  • Investigational Site Number : 7240050
    Esplugues de Llobregat, Barcelona [Barcelona] 08950, Spain
    Recruiting
  • Investigational Site Number : 7240055
    Barcelona, Catalunya [Cataluña] 08035, Spain
    Recruiting
  • Investigational Site Number : 7240056
    Madrid, 28010, Spain
    Recruiting
  • Investigational Site Number : 7240054
    Málaga, 29010, Spain
    Recruiting
  • Investigational Site Number : 7240051
    Valencia, 46026, Spain
    Recruiting
  • Investigational Site Number : 8260031
    London, London, City of WC1N 3JH, United Kingdom
    Completed
  • Investigational Site Number : 8260034
    Leeds, LS1 3EX, United Kingdom
    Recruiting
  • Investigational Site Number : 8260033
    Liverpool, L12 2AP, United Kingdom
    Completed
07

References and documents

08

Registry details

Key details

Study ID
NCT02991469
Lead sponsor
Sanofi
Collaborators
Regeneron Pharmaceuticals
Responsible party
Sponsor
First posted
Dec 13, 2016
Start date
Aug 9, 2018
Primary completion
Mar 1, 2028 (estimated)
Completion
Jan 17, 2031 (estimated)
Last update
Sep 23, 2026

Study contacts

Trial Transparency email recommended (Toll free for US & Canada)
Contact
Contact-Us@sanofi.com
800-633-1610 ext. option 6
Clinical Sciences & Operations
study director · Sanofi

Oversight

Data monitoring committee
Yes
FDA-regulated drug
Yes
FDA-regulated device
No
View the source record on ClinicalTrials.gov ↗

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