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Sarepta Therapeutics, Inc. clinical trials
Also known as AVI BioPharma.
The registry lists 52 studies whose lead sponsor is Sarepta Therapeutics, Inc.. 8 are recruiting or about to start. Per ClinicalTrials.gov, last updated Oct 23, 2026.
Keep track of what changes. Save the Sarepta Therapeutics, Inc. studies recruiting or about to start, and get an email each week — studies that open, close, add sites or post results.
Watch these studiesRegistry sponsor names on this page
Each name exactly as ClinicalTrials.gov lists it, and how it relates to Sarepta Therapeutics, Inc..
- Sarepta Therapeutics, Inc.52 studiesSame company
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Focus areas
Conditions Sarepta Therapeutics, Inc. leads ten or more studies in, by study count. A broader condition is left out when almost all its studies are already in a narrower one listed here.
Studies
Recruiting first, then most recently updated. Showing 50 of 52. Browse all 52 →
- An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular DystrophyEnrolling by invitationNCT06270719
- A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's DiseaseRecruitingNCT07536061Phase 1
- Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing SettingRecruitingNCT07542314Phase 4
- Study of SRP-1003 in Participants With Type 1 Myotonic DystrophyEnrolling by invitationNCT06138743Phase 1/2
- Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular Dystrophy Type 1Enrolling by invitationNCT06131983Phase 1/2
- A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory CohortRecruitingNCT04626674Phase 1
- A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical StudyEnrolling by invitationNCT05967351Phase 3
- A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical PracticeEnrolling by invitationNCT06606340
- A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)Active, not recruitingNCT05881408Phase 3
- A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4Active, not recruitingNCT06246513Phase 3
- A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)Active, not recruitingNCT03992430Phase 3
- A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)Active, not recruitingNCT05876780Phase 1
- Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)TerminatedNCT03652259Phase 1/2
- A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Imlifidase Infusion in Participants With Duchenne Muscular Dystrophy (DMD) Determined to Have Pre-existing Antibodies to Recombinant Adeno-Associated Virus Serotype (rAAVrh74)TerminatedNCT06241950Phase 1
- Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT02500381Phase 3
- A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical PracticeActive, not recruitingNCT04475926
- Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Participants in the United StatesTerminatedNCT06747273Phase 1
- A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related)TerminatedNCT05906251Phase 1
- A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Following Therapeutic Plasma Exchange (Plasmapheresis) in Participants With Duchenne Muscular Dystrophy (DMD) and Pre-existing Antibodies to AAVrh74TerminatedNCT06597656Phase 1
- A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult ParticipantsWithdrawnNCT06952686Phase 3
- A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT05096221Phase 3
- Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping TreatmentTerminatedNCT04004065Phase 2
- A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)CompletedNCT03769116Phase 1/2
- A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)CompletedNCT03375164Phase 1/2
- An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051 (Vesleteplirsen)TerminatedNCT03675126Phase 1/2
- An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyTerminatedNCT03532542Phase 3
- A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)TerminatedNCT03985878Phase 2
- A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D)CompletedNCT01976091Phase 1/2
- A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD)CompletedNCT03375255Phase 1
- Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 SkippingCompletedNCT03218995Phase 2
- Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT02530905Phase 1
- rAAVrh74.MHCK7.DYSF.DV for Treatment of DysferlinopathiesCompletedNCT02710500Phase 1
- Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular DystrophyCompletedNCT02420379Phase 2
- Study of Eteplirsen in DMD PatientsCompletedNCT02255552Phase 3
- Phase I/II Study of SRP-4053 in DMD PatientsCompletedNCT02310906Phase 1/2
- Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy PatientsCompletedNCT01396239Phase 2
- Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular DystrophyCompletedNCT01540409Phase 2
- Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular DystrophyCompletedNCT02286947Phase 2
- Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) PatientsCompletedNCT00844597Phase 1/2
- A Study to Assess the Safety, Tolerability and Pharmacokinetics of AVI-7288 in Healthy Adult VolunteersCompletedNCT01566877Phase 1
- Safety Study of Single Administration Intravenous Treatment for InfluenzaTerminatedNCT01375985Phase 1
- A Study to Assess the Safety, Tolerability and Pharmacokinetics of AVI-7537 in Healthy Adult VolunteersWithdrawnNCT01593072Phase 1
- Safety Study of Single Administration Post-exposure Prophylaxis Treatment for Marburg VirusCompletedNCT01353040Phase 1
- Safety Study of Single Administration Post-Exposure Prophylaxis Treatment for Ebola VirusCompletedNCT01353027Phase 1
- Pharmacokinetic Study of a Single Dose of AVI-4126 (RESTEN-NG®) in Cerebral Spinal FluidCompletedNCT00343148Phase 1
- Safety and Efficacy Study of AVI-5126 When Used on Vein Grafts Before Use in Heart by-Pass Graft Surgery (CABG)TerminatedNCT00451256Phase 2
- Pharmacokinetic Study in Cerebral Spinal Fluid After a Single Dose of AVI-4020CompletedNCT00387283Phase 1
- Pharmacokinetic Study of a Single Dose of AVI-4065 in Cerebral Spinal FluidCompletedNCT00381433Phase 1
- An Exploratory Study of AVI-4020 in Patients With Possible Acute Neuroinvasive West Nile Virus (WNV) DiseaseTerminatedNCT00091845Phase 1
- Study of AVI-4065 in Healthy Volunteers and Chronic Active HCV PatientsTerminatedNCT00229749Phase 1/2