National Institute of Neurological Disorders and Stroke (NINDS): Fabry Disease trials

The registry lists 11 Fabry Disease studies with National Institute of Neurological Disorders and Stroke (NINDS) as lead sponsor. 0 are open to participants now and 0 have results posted.

Phase 1 1Phase 2 3Phase 4 1No phase 6(a study in two phases counts in both)

Studies

Open to participants first, then studies with results posted, then the rest; newest registration first within each.

• An Open-Label Maintenance Study of the Enzyme Replacement Therapy Replagal in Patients With Fabry DiseaseCompletedNCT00357786Phase 1
• Study to Collect Data on Fabry Disease Patients With Enhanceable Alpha-Galactosidase A ActivityCompletedNCT00106912
• Replagal Enzyme Replacement Therapy for Adults With Fabry DiseaseCompletedNCT00097890Phase 4
• Alternative Dosing and Regimen of Replagal to Treat Fabry DiseaseCompletedNCT00075244Phase 2
• An Open-Label Clinical Trial of Replagal Enzyme Therapy in Children Ages 7-17 Years With Fabry DiseaseCompletedNCT00071877Phase 2
• Registry of Fabry Disease - A Multicenter Observational StudyCompletedNCT00055016
• Alpha-Galactosidase A Replacement Therapy for Fabry DiseaseCompletedNCT00048906Phase 2
• Data Collection in Women With Fabry DiseaseCompletedNCT00030134
• PET Scans in Normal Volunteers and Patients With Fabry DiseaseCompletedNCT00005111
• Vasodilation in Patients With Fabry's DiseaseCompletedNCT00001774
• Analysis of the Nervous System in Patients With Fabry's DiseaseCompletedNCT00001491