Gangliosidoses clinical trials

The registry lists 11 studies for Gangliosidoses across 7 countries. 5 are recruiting or about to start. 3 of them are mainly about Gangliosidoses (how this is decided). Per ClinicalTrials.gov, last updated 2026-09-21. Counting its 4 narrower conditions too, such as Gangliosidoses, GM2: 50 studies, 14 open.

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Status

Recruiting: 4
Terminated: 2
Completed: 2
Not yet recruiting: 1
Status unknown: 1
Withdrawn: 1

Phase

Phase 3: 1
Phase 1: 1
Phase 2: 1
Phase 4: 1

Where

United States: 7
Germany: 2
China: 1
Sri Lanka: 1
France: 1
Egypt: 1

Who runs them

University of Minnesota (3) · Children's Hospital of Philadelphia (2) · SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt) (1) · Sun Yat-sen University (1) · National Human Genome Research Institute (NHGRI) (1) · Assistance Publique - Hôpitaux de Paris (1) · Lysosomal and Rare Disorders Research and Treatment Center, Inc. (1) · CENTOGENE GmbH Rostock (1)

Coming up

0phase 3 studies under way

1study finishes main data collection within a year

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

The study

Mar 2027A Natural History Study of the Gangliosidoses · University of Minnesota

Who these studies take

Of the 4 Gangliosidoses studies recruiting now, 3 (75%) set no upper age limit and 1 (25%) stop at 75 or younger. 4 (100%) take children under 18. 0 (0%) are for women only and 0 (0%) for men only; 0 (0%) take healthy volunteers.

Recruiting studies that take each age, of 4
Age	Women	Men
10	4 (100%)	4 (100%)
18	3 (75%)	3 (75%)
30	3 (75%)	3 (75%)
40	3 (75%)	3 (75%)
50	3 (75%)	3 (75%)
65	3 (75%)	3 (75%)
75	3 (75%)	3 (75%)
85	3 (75%)	3 (75%)

Across all 11 studies, recruiting or not: 36% stop at 75 or younger and 27% at 65; 91% take children; 0% are for women only and 0% for men only; 9% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

Studies

Recruiting first, then most recently updated. Showing 11 of 11. search them.