Dwarfism clinical trials

The registry lists 99 studies for Dwarfism across more than 10 countries. 12 are recruiting or about to start. 37 of them are mainly about Dwarfism (how this is decided). Per ClinicalTrials.gov, last updated 2026-11-10. Counting its 3 narrower conditions too, such as Dwarfism, Pituitary: 391 studies, 62 open.

Get an email when these change. Save the Dwarfism studies recruiting or about to start — once a week, free: studies that open, close, add sites or post results.

Watch these studies

See an example email

Example · made-up studies

Breast cancer · Recruiting: 2 came in, 3 changed

What changed in your saved searches, Oct 31 – Nov 6:

A study of drug A after surgery for early breast cancer

Came in · now Recruiting

Drug B with hormone therapy in advanced breast cancer

Changed

· Sites: 4 added, including Seoul and Busan

· Enrollment: 300 → 450 participants

Exercise during chemotherapy

Now Active, not recruiting

One email a week for all your saved searches. Stop any time.

Status

Completed: 58
Status unknown: 10
Terminated: 9
Active, not recruiting: 8
Recruiting: 7
Enrolling by invitation: 3

Phase

Phase 2: 34
Phase 3: 20
Phase 4: 7
Phase 1: 6

Where

United States: 55
Australia: 21
United Kingdom: 21
Spain: 19
France: 18
Germany: 12

Who runs them

BioMarin Pharmaceutical (10) · QED Therapeutics, a BridgeBio company (7) · Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) (7) · Nemours Children's Clinic (5) · Changchun GeneScience Pharmaceutical Co., Ltd. (4) · Istituto Auxologico Italiano (3) · Ascendis Pharma A/S (3) · Ipsen (3)

What is being tested here

Drugs under test in Dwarfism studies, those with the most open studies first. Medicines only given beside them are not counted. How drugs are counted

Drug	Open	Phase 3	All
Infigratinib	2	2	4
Vosoritide	1	3	11
Navepegritide	1	1	3
Lonapegsomatropin	1	1	1
Human Growth Hormone	0	7	15
Growth Hormone	0	0	3
Mecasermin	0	1	2
Anastrozole	0	1	2
Essential amino acid	0	0	1
Letrozole	0	0	1

Coming up

5phase 3 studies under way

6studies finish main data collection within a year1 of them phase 3

Studies recruiting or running, from their records. “Main data collection” ends at the primary completion date, the sponsor’s own estimate, which often moves.

All 6, phase 3 first

Jan 2027An Interventional Study of Infigratinib in Children With Hypochondroplasia · Phase 3 · QED Therapeutics, a BridgeBio company
Dec 2026The Dosage Exploration Study of PEG-rhGH for Treating Short Stature in Prepubertal and Pubertal Children · Second Affiliated Hospital of Wenzhou Medical University
Dec 2026A Natural History Study in Children With a Type II Collagen Disorder With Short Stature · Innoskel
Mar 2027A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment · BioMarin Pharmaceutical
Apr 2027Non-invasive Functional Assessment and Pathogenesis of Morquio A · Nemours Children's Clinic
Jul 2027Study of Skeletal Disorders · Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

Who these studies take

Of the 7 Dwarfism studies recruiting now, 1 (14%) set no upper age limit and 5 (71%) stop at 75 or younger. 7 (100%) take children under 18. 1 (14%) are for women only and 0 (0%) for men only; 1 (14%) take healthy volunteers.

Recruiting studies that take each age, of 7
Age	Women	Men
10	6 (86%)	5 (71%)
18	2 (29%)	2 (29%)
30	2 (29%)	2 (29%)
40	2 (29%)	2 (29%)
50	2 (29%)	2 (29%)
65	2 (29%)	2 (29%)
75	2 (29%)	2 (29%)
85	2 (29%)	2 (29%)

Across all 99 studies, recruiting or not: 81% stop at 75 or younger and 81% at 65; 94% take children; 6% are for women only and 6% for men only; 18% take healthy volunteers. From each study’s registry entry; the criteria on its page decide.

Studies

Recruiting first, then most recently updated. Showing 50 of 99. Browse all 99 → or search them.